Drugs for Angelman Syndrome (from DrugBank, HMDB, Dgidb, PharmGKB, IUPHAR, NovoSeek, BitterDB):
(show all 48)
# |
|
Name |
Status |
Phase |
Clinical Trials |
Cas Number |
PubChem Id |
1 |
|
Carbidopa |
Approved |
Phase 2, Phase 3 |
|
28860-95-9 |
34359 38101 |
Synonyms:
(-)-L-a-Hydrazino-3,4-dihydroxy-a-methylhydrocinnamate
(-)-L-a-Hydrazino-3,4-dihydroxy-a-methylhydrocinnamic acid
(-)-L-alpha-Hydrazino-3,4-dihydroxy-alpha-methylhydrocinnamate
(-)-L-alpha-Hydrazino-3,4-dihydroxy-alpha-methylhydrocinnamic acid
(-)-L-ALPHA-HYDRAZINO-3,4-DIHYDROXY-ALPHA-METHYLHYDROCINNAMIC ACID MONOHYDRATE
(-)-L-Α-hydrazino-3,4-dihydroxy-α-methylhydrocinnamate
(-)-L-Α-hydrazino-3,4-dihydroxy-α-methylhydrocinnamic acid
(2S)-3-(3,4-DIHYDROXYPHENYL)-2-HYDRAZINYL-2-METHYLPROPANOIC ACID HYDRATE
(2S)-3-(3,4-DIHYDROXYPHENYL)-2-HYDRAZINYL-2-METHYLPROPANOIC ACID MONOHYDRATE
(AlphaS)-a-hydrazino-3,4-dihydroxy-a-methylbenzenepropanoate
(AlphaS)-a-hydrazino-3,4-dihydroxy-a-methylbenzenepropanoic acid
(AlphaS)-alpha-hydrazino-3,4-dihydroxy-alpha-methylbenzenepropanoate
(AlphaS)-alpha-hydrazino-3,4-dihydroxy-alpha-methylbenzenepropanoic acid
(ALPHAS)-ALPHA-HYDRAZINO-3,4-DIHYDROXY-ALPHA-METHYLBENZENEPROPANOIC ACID MONOHYDRATE
(AlphaS)-α-hydrazino-3,4-dihydroxy-α-methylbenzenepropanoate
(AlphaS)-α-hydrazino-3,4-dihydroxy-α-methylbenzenepropanoic acid
(S)-(−)-carbidopa
(S)-(-)-Carbidopa
(S)-(-)-CARBIDOPA HYDRATE
(S)-(−)-CARBIDOPA HYDRATE
(S)-Carbidopa
(S)-CARBIDOPA HYDRATE
|
(αS)-α-hydrazino-3,4-dihydroxy-α-methylbenzenepropanoic acid
Carbidopa
Carbidopa (anhydrous)
CARBIDOPA ANHYDROUS
CARBIDOPA HYDRATE
CARBIDOPA MONOHYDRATE
Carbidopa, (R)-isomer
Carbidopa, (S)-isomer
Carbidopum
CARBIDOPUM MONOHYDRICUM
CDP536
Duodopa®|Lodosyn®|MK 486
L-3-(3,4-Dihydroxyphenyl)-2-methyl-2-hydrazinopropionate
L-3-(3,4-Dihydroxyphenyl)-2-methyl-2-hydrazinopropionic acid
L-ALPHA-(3,4-DIHYDROXYBENZYL)-ALPHA-HYDRAZINOPROPIONIC ACID MONOHYDRATE
L-alpha-Methyldopahydrazine
L-a-Methyldopahydrazine
Lodosin
Lodosyn
L-Α-methyldopahydrazine
Methyldopahydrazine
MK-486
|
|
2 |
|
Levodopa |
Approved |
Phase 2, Phase 3 |
|
59-92-7, 63-84-3 |
6047 |
Synonyms:
(-)-3-(3,4-Dihydroxyphenyl)-L-alanine
(−)-3-(3,4-DIHYDROXYPHENYL)-L-ALANINE
(-)-Dopa
(−)-DOPA
(+-)-3-(3,4-Dihydroxyphenyl)alanine
(+-)-Dopa
(+/-) 3-(3,4-dihydroxyphenyl)alanine
(2S)-2-Amino-3-(3,4-dihydroxyphenyl)propanoate
(2S)-2-Amino-3-(3,4-dihydroxyphenyl)propanoic acid
(R,S)-Dopa
2-amino-3-(3,4-Dihydroxyphenyl)propanoate
2-amino-3-(3,4-Dihydroxyphenyl)propanoic acid
3 Hydroxy DL tyrosine
3 Hydroxy L tyrosine
3-(3,4-Dihydroxyphenyl)-DL-alanine
3-(3,4-Dihydroxyphenyl)-L-alanine
3,4 Dihydroxyphenylalanine
3,4-Dihydroxy-DL-phenylalanine
3,4-Dihydroxy-L-phenylalanine
3,4-dihydroxy-L-phenylalanine|Inbrija® (levodopa inhalation powder)|L-DOPA|Sinemet®
3,4-Dihydroxyphenylalanine
3',4'-Dihydroxyphenylalanine
3,4-Dihydroxyphenyl-L-alanine
3-Hydroxy-DL-tyrosine
3-Hydroxy-L-tyrosine
3-Hydroxytyrosine
a-amino-3,4-Dihydroxy-benzenepropanoate
a-amino-3,4-Dihydroxy-benzenepropanoic acid
alpha-amino-3,4-Dihydroxy-benzenepropanoate
alpha-amino-3,4-Dihydroxy-benzenepropanoic acid
alpha-amino-Hydrocaffeic acid
b-(3,4-Dihydroxyphenyl)-a-alanine
b-(3,4-Dihydroxyphenyl)-a-L-alanine
b-(3,4-Dihydroxyphenyl)alanine
b-(3,4-Dihydroxyphenyl)-DL-a-alanine
b-(3,4-Dihydroxyphenyl)-L-alanine
Bendopa
beta Hydroxytyrosine
beta-(3,4-Dihydroxyphenyl)alanine
beta-(3,4-Dihydroxyphenyl)-alpha-alanine
beta-(3,4-Dihydroxyphenyl)-alpha-L-alanine
beta-(3,4-Dihydroxyphenyl)-DL-alpha-alanine
beta-(3,4-Dihydroxyphenyl)-L-alanine
beta-Hydroxytyrosine
BROCADOPA
Cidandopa
Deadopa
Dihydroxy-L-phenylalanine
Dihydroxyphenylalanine
Dihydroxyphenylalanine hydrochloride, (2:1)
DL-3,4-Dihydroxyphenylalanine
DL-3',4'-Dihydroxyphenylalanine
DL-3,4-Dopa
DL-3-Hydroxytyrosine
DL-4,5-Dihydroxyphenylalanine
DL-b-(3,4-Dihydroxyphenyl)-a-alanine
DL-b-(3,4-Dihydroxyphenyl)alanine
DL-beta-(3,4-Dihydroxyphenyl)alanine
DL-beta-(3,4-Dihydroxyphenyl)-alpha-alanine
DL-Dihydroxyphenylalanine
DL-Dioxyphenylalanine
|
DL-Β-(3,4-dihydroxyphenyl)alanine
DL-Β-(3,4-dihydroxyphenyl)-α-alanine
Dopa
Dopaflex
Dopaidan
Dopal
Dopal-Fher
Dopalina
Dopar
Doparkine
Doparl
Dopasol
Dopaston
Dopastone
Dopastral
Dopicar
Doprin
Eldopal
Eldopar
Eldopatec
Eurodopa
Helfo-dopa
INBRIJA
Insulamina
L 3,4 Dihydroxyphenylalanine
L Dopa
L-(-)-Dopa
L-3-(3,4-Dihydroxyphenyl)-alanine
L-3,4-Dihydroxyphenylalanine
L-4-5-Dihydroxyphenylalanine
Laradopa
Larodopa
L-b-(3,4-Dihydroxyphenyl)-a-alanine
L-b-(3,4-Dihydroxyphenyl)alanine
L-beta-(3,4-Dihydroxyphenyl)alanine
L-beta-(3,4-Dihydroxyphenyl)-alpha-alanine
L-Dihydroxyphenylalanine
L-DOPA
LDP540
Ledopa
Levedopa
Levodopa
Levodopum
Levopa
L-Β-(3,4-dihydroxyphenyl)alanine
Maipedopa
Medphano brand OF levodopa
NSC-118381
Parda
Pardopa
Prodopa
Roberts brand OF levodopa
Roche brand OF levodopa
SINEMET
Syndopa
V-1512
Veldopa
Weldopa
Β-(3,4-dihydroxyphenyl)alanine
Β-(3,4-dihydroxyphenyl)-DL-α-alanine
Β-(3,4-dihydroxyphenyl)-L-alanine
|
|
3 |
|
Dopamine |
Approved |
Phase 2, Phase 3 |
|
62-31-7, 51-61-6 |
681 |
Synonyms:
2-(3,4-Dihydroxyphenyl)ethylamine
3,4 Dihydroxyphenethylamine
3,4-Dihydroxyphenethylamine
3,4-Dihydroxyphenylethylamine
3-Hydroxytyramine
4-(2-Aminoethyl)-1,2-benzenediol
4-(2-Aminoethyl)benzene-1,2-diol
4-(2-Aminoethyl)catechol
4-(2-Aminoethyl)pyrocatechol
4-(2-Aminoethyl)-pyrocatechol
4-(2-AZANYLETHYL)BENZENE-1,2-DIOL
a-(3,4-Dihydroxyphenyl)-b-aminoethane
alpha-(3,4-Dihydroxyphenyl)-beta-aminoethane
ASL-279
CARBILEV
Deoxyepinephrine
Dopamin
Dopamina
DOPAMINE
DOPAMINE HCL
|
Dopamine hydrochloride
DOPAMIN-NATTERMAN
Dopaminum
Dopastat
Dophamine
DOPMIN
Dynatra
Hydrochloride, dopamine
Hydroxytyramin
Hydroxytyramine
Intropin
Medopa
NSC-169105
NSC-173182
Oxytyramine
PARCOPA
Revivan
SABAX DOPAMIN
SELECTAJET
SINEMET
|
|
4 |
|
Gaboxadol |
Investigational |
Phase 3 |
|
64603-91-4 |
3448 |
Synonyms:
4,5,6,7-tetrahydroisoxazolo(5,4-c)Pyridin-3-ol
Gaboxadol
LU-02030
LU-02-030
|
LU-02030|MK-0928|THIP
MK-0928
THIP
|
|
5 |
|
Dihydroxyphenylalanine |
|
Phase 2, Phase 3 |
|
|
|
6 |
|
Carbidopa, levodopa drug combination |
|
Phase 2, Phase 3 |
|
|
|
7 |
|
Dopamine Agents |
|
Phase 2, Phase 3 |
|
|
|
8 |
|
Antiparkinson Agents |
|
Phase 2, Phase 3 |
|
|
|
9 |
|
Neurotransmitter Agents |
|
Phase 3 |
|
|
|
10 |
|
Anticonvulsants |
|
Phase 3 |
|
|
|
11 |
|
GABA Agonists |
|
Phase 3 |
|
|
|
12 |
|
Analgesics |
|
Phase 3 |
|
|
|
13 |
|
Minocycline |
Approved, Investigational |
Phase 2 |
|
10118-90-8, 13614-98-7 |
54675783 5281021 |
Synonyms:
(4S,4AS,5ar,12as)-4,7-bis(dimethylamino)-3,10,12,12a-tetrahydroxy-1,11-dioxo-1,4,4a,5,5a,6,11,12a-octahydrotetracene-2-carboxamide
7-Dimethylamino-6-demethyl-6-deoxytetracycline
ACNAMINO
AKNEMIN
AKNEMIN 50
Alti-Minocycline
Apo-Minocycline
ARESTIN
BLEMIX 100
BLEMIX 50
CYCLOMIN
DENTOMYCIN
DYNACIN
Gen-Minocycline
KLINOMYCIN
MINO
Minociclina
Minociclina [INN-Spanish]
Minociclinum
MINOCIN
|
MINOCIN 50
MINOCIN MR
MINOCYCLIN
MINOCYCLINE
MINOCYCLINE HCL
MINOCYCLINE HYDROCHLORIDE
MINOCYCLINUM
Minocyclinum [INN-Latin]
Minocyn
MINOGAL
MINOLIRA
Minomycin
Novo-Minocycline
NSC-141993
SEBOMIN
SEBREN MR
SOLODYN
VECTRIN
XIMINO
|
|
14 |
|
Anti-Bacterial Agents |
|
Phase 2 |
|
|
|
15 |
|
Anti-Infective Agents |
|
Phase 2 |
|
|
|
16 |
|
Pharmaceutical Solutions |
|
Phase 2 |
|
|
|
17 |
|
Aromatic Amino Acid Decarboxylase Inhibitors |
|
Phase 1 |
|
|
|
18 |
|
Tetracycline |
Approved, Vet_approved, Withdrawn |
|
|
60-54-8 |
5353990 |
Synonyms:
(4S,4AS,5as,12as)-4-(dimethylamino)-1,4,4a,5,5a,6,11,12a-octahydro-3,6,10,12,12a-pentahydroxy-6-methyl-1,11-dioxo-2-naphthacenecarboxamide
Abramycin
Achromycin
ACHROMYCIN V
Anhydrotetracycline
CYCLOPAR
Deschlorobiomycin
E701
ECONOMYCIN
Liquamycin
NSC-108579
PANMYCI DONT CAREIQUAMYCIN
PANMYCIN
Sumycin
|
SUPRAMYCIN
SUSTAMYCIN
TC
TETRABID ORGANON
Tetracyclin
TETRACYCLINE
TÉTRACYCLINE
Tetracycline HCL
Tetracyclinum
TETRACYN
Tetrazyklin
Tsiklomitsin
VETQUAMYCIN
|
|
19 |
|
Estradiol |
Approved, Investigational, Vet_approved |
|
|
50-28-2 |
5757 |
Synonyms:
(+)-3,17B-ESTRADIOL
(17b)-Estra-1,3,5(10)-triene-3,17-diol
(17BETA)-ESTRA-1,3,5(10)-TRIENE-3,17-DIOL
(17Β)-ESTRA-1,3,5(10)-TRIENE-3,17-DIOL
(1S,10R,11S,14S,15S)-15-METHYLTETRACYCLO[8.7.0.0^{2,7}.0^{11,15}]HEPTADECA-2,4,6-TRIENE-5,14-DIOL
(8R,9S,13S,14S,17S)-13-METHYL-6,7,8,9,11,12,14,15,16,17-DECAHYDROCYCLOPENTA[A]PHENANTHRENE-3,17-DIOL
[<sup>3</sup>H]-estradiol|[<sup>3</sup>H]-estrogen|[<sup>3</sup>H]E2|[<sup>3</sup>H]estradiol
13B-METHYL-1,3,5(10)-GONATRIENE-3,17B-OL
17 beta Estradiol
17 beta Oestradiol
17 beta-Estradiol
17 beta-Oestradiol
17b Oestradiol
17b-Estra-1,3,5(10)-triene-3,17-diol
17B-ESTRADIOL
17BETA OESTRADIOL
17BETA-ESTRA-1,3,5(10)-TRIENE-3,17-DIOL
17BETA-ESTRADIOL
17BETA-OESTRADIOL
17B-OESTRADIOL
17Β oestradiol
17Β-ESTRA-1,3,5(10)-TRIENE-3,17-DIOL
17β-estradiol
17Β-OESTRADIOL
3,17B-DIHYDROXYESTRA-1,3,5(10)-TRIENE
3,17B-ESTRADIOL
3,17-EPIDIHYDROXYESTRATRIENE
ADGYN ESTRO
AERODIOL
AGOFOLLIN
ALFATRADIOL
ALORA
ALTRAD
AMNESTROGEN
AQUADIOL
AQUAGEN
BARDIOL
BEDOL
B-ESTRADIOL
BETA-ESTRADIOL
CIS-ESTRADIOL
CLIMADERM
CLIMARA
CLIMARA PRO
COMPUDOSE
CORPAGEN
Delestrogen
DELTA-ESTRADIOL
DELTA-OESTRADIOL
DEPO-ESTRADIOL
DERMESTRIL
DERMESTRIL 100
DERMESTRIL 25
DERMESTRIL 50
DERMESTRIL SEPTEM 25
DERMESTRIL SEPTEM 50
DERMESTRIL SEPTEM 75
DESTRADIOL
D-ESTRADIOL
DIHYDROFOLLICULAR HORMONE
DIHYDROFOLLICULIN
DIHYDROMENFORMON
DIHYDROTHEELIN
DIHYDRO-THEELIN
DIHYDROXYESTRIN
DIMENFORMON
DIOGYN
DIOGYNETS
DIVIGEL
D-OESTRADIOL
E2
E2|estrogen|oestrodiol|oestrogen
E-CYPIONATE
ELESTRIM
ELESTRIN
ELLESTE SOLO
ELLESTE SOLO MX 40
ELLESTE SOLO MX 80
ENCORE
EPIESTRIOL 50
ESCLIM
ESTRA-1,3,5(10)-TRIENE-3,17B-DIOL
ESTRACE
ESTRADERM
ESTRADERM MX 100
ESTRADERM MX 25
ESTRADERM MX 50
ESTRADERM MX 75
ESTRADERM TTS
ESTRADERM TTS 100
ESTRADERM TTS 25
ESTRADERM TTS 50
ESTRADIOL
Estradiol 17 alpha
Estradiol 17 beta
Estradiol 17beta
Estradiol anhydrous
ESTRADIOL HEMIHYDRATE
Estradiol hemihydrate, (17 alpha)-isomer
Estradiol monohydrate
Estradiol orion brand
Estradiol valerate
Estradiol valeriante
|
Estradiol, (-)-isomer
Estradiol, (+-)-isomer
Estradiol, (16 alpha,17 alpha)-isomer
Estradiol, (16 alpha,17 beta)-isomer
Estradiol, (17-alpha)-isomer
Estradiol, (8 alpha,17 beta)-(+-)-isomer
Estradiol, (8 alpha,17 beta)-isomer
Estradiol, (9 beta,17 alpha)-isomer
Estradiol, (9 beta,17 beta)-isomer
Estradiol, monosodium salt
Estradiol, sodium salt
Estradiol-17 alpha
Estradiol-17 beta
Estradiol-17b
ESTRADIOL-17BETA
ESTRADIOL-17-BETA
Estradiol-17β
ESTRADIOLUM
ESTRADOT
ESTRALDINE
ESTRASORB
ESTRING
ESTRING VAGINAL RING
ESTROCLIM
ESTROCLIM 50
ESTROGEL
ESTROGEL HBF
ESTROGEN
ESTROVITE
EVAMIST
EVOREL
EVOREL 100
EVOREL 25
EVOREL 50
EVOREL 75
FEMATRIX 40
FEMATRIX 80
FEMESTRAL
FEMOGEN
FEMPATCH
FEMSEVEN 100
FEMSEVEN 50
FEMSEVEN 75
FOLLICYCLIN
GELESTRA
GINOSEDOL
GVNODIOL
GYNERGON
GYNODIOL
GYNOESTRYL
GYNOGEN
IMVEXXY
INNOFEM
LAMDIOL
MACRODIOL
MENOREST
MENOREST 37.5
MENOREST 50
MENOREST 75
MENORING 50
MENOSTAR
MINIVELLE
NORDICOL
Novartis pharmaceuticals brand OF estradiol
NSC-20293
NSC-9895
OESCLIM
OESTERGON
OESTRA-1,3,5(10)-TRIENE-3,17B-DIOL
OESTRADIOL
OESTRODIOL
OESTROGEL
OESTROGEN
OESTROGLANDOL
Orion brand OF estradiol
OVAHORMON
OVASTEROL
OVASTEVOL
OVOCYCLIN
OVOCYLIN
PERLATANOL
PRIMOFOL
PROFOLIOL
PROFOLIOL B
PROGYNON
Progynon depot
PROGYNON DH
Progynon-depot
Progynova
PROGYNOVA TS
SANDRENA
SANDRENA 1
SYNDIOL
SYSTEN
VAGIFEM
VAGIFEM 18
VAGIFEM 8
VIVELLE
VIVELLE-DOT
WC3011
WC-3011
ZUMENON
Β-estradiol
|
|
20 |
|
Polyestradiol phosphate |
Approved |
|
|
28014-46-2 |
|
Synonyms:
(17-beta)-Estra-1,3,5(10)-triene-3,17-diol polymer with phosphoric acid
ESTRADIOL PHOSPHATE
Estradiol phosphate polymer
ESTRADURIN
Fosfato de poliestradiol
LEO-114
Oestradiol phosphate polymer
|
Phosphate de polyestradiol
Poly(estradiol phosphate)
POLYEST PHOS
POLYESTRADIOL PHOS PHOSPHATE
POLYESTRADIOL PHOSPHATE
Polyestradioli phosphas
|
|
21 |
|
Mecobalamin |
Approved, Investigational |
|
|
13422-55-4 |
|
Synonyms:
ASIMIL B-12
B-MAX
CO-METHYLCOBALAMIN
MeCbl
Mecobalamin
Mecobalamina
|
Mecobalaminum
Methyl vitamin B12
Methyl(III)cobalamin
Methylcob(III)alamin
Methylcobalamin
|
|
22 |
|
Hydroxocobalamin |
Approved |
|
|
13422-51-0 |
15589840 44475014 |
Synonyms:
a-(5,6-Dimethylbenzimidazolyl)hydroxocobamide
alpha Cobione
alpha-(5,6-Dimethylbenzimidazolyl)hydroxocobamide
ALPHAREDISOL
Axlon
Ciplamin H
Cobalex
Cobalin H
COBALIN-H
Cobinamide hydroxide phosphate 3'-ester with 5,6-dimethyl-1-a-D-ribofuranosylbenzimidazole inner salt
Cobinamide hydroxide phosphate 3'-ester with 5,6-dimethyl-1-alpha-delta-ribofuranosylbenzimidazole inner salt
Codroxomin
CYANOKIT
Docclan
Docelan
Docevita
Droxomin
Ducobee hy
Duradoce
|
Duralta-12
HEPAVIT
Hydrocobalamin
Hydrogrisevit
Hydrovit
Hydroxocobalamin
Hydroxo-cobalamin
HYDROXOCOBALAMIN ACETATE
HYDROXOCOBALAMIN ANHYDROUS
Hydroxocobalamine
HYDROXOCOBALAMINUM ANHYDROUS
HYDROXOCOBEMINE
Hydroxomin
Hydroxycobalamin
MEGAMILBEDOCE
NEO-CYTAMEN
OH-CBL
Vitamin b-12b
|
|
23 |
|
Coal tar |
Approved |
|
|
8007-45-2 |
|
Synonyms:
|
24 |
|
Folic acid |
Approved, Nutraceutical, Vet_approved |
|
|
59-30-3 |
6037 |
Synonyms:
(2S)-2-[(4-{[(2-AMINO-4-OXO-1,4-DIHYDROPTERIDIN-6-YL)METHYL]AMINO}PHENYL)FORMAMIDO]PENTANEDIOIC ACID
(2S)-2-[[[4-[(2-AMINO-4-OXO-1H-PTERIDIN-6-YL)METHYLAMINO]PHENYL]-OXO-METHYL]AMINO]PENTANEDIOIC ACID
(2S)-2-[[4-[(2-AMINO-4-OXO-1H-PTERIDIN-6-YL)METHYLAMINO]BENZOYL]AMINO]GLUTARIC ACID
(2S)-2-[[4-[(2-AMINO-4-OXO-1H-PTERIDIN-6-YL)METHYLAMINO]BENZOYL]AMINO]PENTANEDIOIC ACID
(2S)-2-[[4-[(2-AMINO-4-OXO-1H-PTERIDIN-6-YL)METHYLAMINO]PHENYL]CARBONYLAMINO]PENTANEDIOIC ACID
[<sup>3</sup>H]-folic acid
Acide folique
ácido fólico
Acidum folicum
ACIFOLIC
Apo-Folic
B03BB01
b9, Vitamin
BIO SCIENCE
CYTOFOL
DOSFOLAT B ACTIV
FOLACID
FOLACIN
FOLATE
FOLBAL
FOLCIDIN
FOLDINE
FOLETTES
FOLIAMIN
FOLIC ACID
Folic acid, (D)-isomer
Folic acid, (DL)-isomer
Folic acid, calcium salt (1:1)
Folic acid, monopotassium salt
Folic acid, monosodium salt
Folic acid, potassium salt
Folic acid, sodium salt
FOLICARE
FOLICET
FOLIPAC
|
FOLSAEURE
FOLSAN
FOLSAURE
Folsäure
FOLSAV
FOLVITE
Folvron
INCAFOLIC
LEXPEC
LIVER LACTOBACILLUS CASEI FACTOR
MILLAFOL
N-(4-{[(2-AMINO-4-OXO-3,4-DIHYDROPTERIDIN-6-YL)METHYL]AMINO}BENZOYL)-L-GLUTAMIC ACID
N-[(4-{[(2-amino-4-oxo-1,4-dihydropteridin-6-yl)methyl]amino}phenyl)carbonyl]-L-glutamate
N-[(4-{[(2-AMINO-4-OXO-1,4-DIHYDROPTERIDIN-6-YL)METHYL]AMINO}PHENYL)CARBONYL]-L-GLUTAMIC ACID
N-[4-[[(2-AMINO-3,4-DIHYDRO-4-OXO-6-PTERIDINYL)METHYL]AMINO]BENZOYL]-L-GLUTAMIC ACID
NATUR FLOW
N-Pteroyl-L-glutamate
N-PTEROYL-L-GLUTAMIC ACID
NSC-3073
PGA
PRECONCEIVE
PTEGLU
PTEROYLGLUTAMATE
PTEROYLGLUTAMIC ACID
PTEROYL-L-GLUTAMATE
PTEROYL-L-GLUTAMIC ACID
PTEROYL-L-MONOGLUTAMATE
PTEROYL-L-MONOGLUTAMIC ACID
PTEROYLMONOGLUTAMIC ACID
ROCHE
Vitamin B9
VITAMIN BC
VITAMIN BE
VITAMIN M
|
|
25 |
|
N,N,N-trimethylglycinium |
Approved, Experimental, Investigational, Nutraceutical |
|
|
6915-17-9, 107-43-7 |
248 |
Synonyms:
2-(Trimethylammonio)Acetate
2-N,N,N-trimethylammonio acetate
2-trimethylammonioacetate
Abromine
Acidin pepsin
Acidin-pepsin
AcidinPepsin
Acidol
Beaufour brand OF betaine citrate
Betaína anhidra
Betaine
Betaine hydrochloride
Betaine orphan brand
Betaine, anhydrous
Betaine, glycine
Boizot brand OF betaine aspartate
Byk brand OF betaine phosphate
C.B.B.
Citrate de bétaïne beaufour
Citrate de bétaïne upsa
Cystadane
Fournier brand OF betaine ascorbate and hydrate
Glycine betaine
Glycinebetaine
|
Glykokollbetain
Hepastyl
Hydrochloride, betaine
Logeais brand OF betaine cyclobutyrate
Lycine
N,N,N-trimethylammonioacetate
N,N,N-Trimethylglycine
Novobetaine
Orphan brand OF betaine
Oxyneurine
Scorbo bétaïne
Scorbobétaïne
Scorbo-bétaïne
Stea 16
Stea16
Stea-16
TMG
TRIMETHYL glycine
Trimethylaminoacetate
Trimethylammonioacetate
Trimethylammonioacetic acid
Trimethylglycine
Trimethylglycocoll
UPSA brand OF betaine citrate
|
|
26 |
|
Cyanocobalamin |
Approved, Nutraceutical |
|
|
68-19-9 |
24892734 16212801 44176380 |
Synonyms:
Anacobin
Bedoz
BEHEPAN
Berocca PN
Berubigen
BETALIN 12
Betalin 12 crystalline
Betaline-12
Betolvex
Bevidox
Bevidox concentrate
Biocobalamine
Byladoce
Cabadon m
CALOMIST
Cernevit-12
Cianocobalamina
Cobadoce forte
Cobalin
Cobavite
Cobex
Cobolin-M
Copharvit 5000
Covit
Crystamin
Crystamine
Crysti-12
Crystimin
Crystwel
Cyano-b12
Cyanobalamin concentrate
Cyanocob(III)alamin
CYANOCOBALAMIN
Cyanocobalamin (JP15/usp)
Cyanocobalamin Co 57 Schilling Test Kit
Cyanocobalamine
Cyanocobalaminum
Cyanocobalmin
Cyanoject
CYANOVIT-B12
Cycobemin
Cycolamin
Cykobemin
Cykobeminet
Cyomin
Cyredin
Cytacon
Cytamen
Cytobion
Depinar
Dicopac
Dicopac Kit
Dimethylbenzimidazoylcobamide
Distivit
Docemine
Docibin
Docivit
Dodecabee
Dodecavite
Dodex
Duodecibin
Embiol
Emociclina
Eritrone
|
Erycytol
Erythrotin
Euhaemon
Extrinsic factor
Factor II
Fermin
Fresmin
Hemomin
Hepagon
Hepavis
Hepcovite
Hylugel plus
Infuvite Pediatric
Lactobacillus lactis dorner factor
M.V.I. Pediatric
Macrabin
Megabion
Megalovel
Milbedoce
Millevit
Nagravon
Nascobal
Neuroforte-R
Normocytin
Novidroxin
NSC-80365
Pernaemon
Pernaevit
Pernipuron
Plecyamin
Poyamin
Primabalt
Rebramin
Redamina
Redisol
Rhodacryst
Rubesol
RUBIVITE
Rubramin
RUBRAMIN PC
Rubratope-57 Kit
Rubratope-60 Kit
Rubripca
Rubrocitol
RUVITE
Shovite
Sytobex
Vibal
Vibalt
Vibisone
Virubra
Vitabee 12
VITAMIN B 12
Vitamin b12
Vitamin b12 complex
VITAMIN B12 NOS
Vitamin b12 preparation
vitamine b12
Vitaped
Vitarubin
Vita-rubra
Vitral
VI-TWEL
|
|
27 |
|
Creatine |
Approved, Investigational, Nutraceutical |
|
|
57-00-1 |
586 |
Synonyms:
((Amino(imino)methyl)(methyl)amino)acetate
((Amino(imino)methyl)(methyl)amino)acetic acid
(alpha-Methylguanido)acetate
(alpha-Methylguanido)acetic acid
(a-Methylguanido)acetate
(a-Methylguanido)acetic acid
(N-Methylcarbamimidamido)acetate
(N-Methylcarbamimidamido)acetic acid
(Α-methylguanido)acetate
(Α-methylguanido)acetic acid
[[Amino(imino)methyl](methyl)amino]acetate
[[Amino(imino)methyl](methyl)amino]acetic acid
alpha-Methylguanidino acetate
alpha-Methylguanidino acetic acid
a-Methylguanidino acetate
a-Methylguanidino acetic acid
Cosmocair C 100
Creatin
Creatine
|
Creatine (8CI)
Creatine hydrate
Creatine, hydrate
Kreatin
Krebiozon
Methylglycocyamine
Methylguanidoacetate
Methylguanidoacetic acid
N-(Aminoiminomethyl)-N-methylglycine
N-(Aminoiminomethyl)-N-methyl-glycine
N-[(e)-AMINO(imino)methyl]-N-methylglycine
N-Amidinosarcosine
N-Carbamimidoyl-N-methylglycine
N-Methyl-N-guanylglycine
NSC-8752
Phosphagen
Pyrolysate
Α-methylguanidino acetate
Α-methylguanidino acetic acid
|
|
28 |
|
Cobalamin |
Experimental |
|
|
13408-78-1 |
6857388 |
Synonyms:
5,6-Dimethyl-1-a-D-ribofuranosyl-1H-benzimidazole
5,6-Dimethyl-1-a-D-ribofuranosylbenzimidazole
5,6-Dimethyl-1-alpha-delta-ribofuranosyl-1H-benzimidazole
5,6-Dimethyl-1-alpha-delta-ribofuranosylbenzimidazole
a-(5,6-Dimethylbenzimidazolyl)cobamide
alpha-(5,6-Dimethylbenzimidazolyl)cobamide
b 12, Vitamin
b12, Vitamin
Cbl
Cob(III)alamin
Cobalamin (III)
Cobalamin(1+)
Cobalamin(III)
Cobalamine
|
Cobalamins
Cobinamide ion(1+) dihydrogen phosphate (ester) inner salt 3'-ester
Cobinamide ion(1+) dihydrogen phosphate (ester) inner salt 3'-ester with 5,6-dimethyl-1-alpha-delta-ribofuranosyl-1H-benzimidazole
Cyanocobalamin
Eritron
Hydroxomin
Rubivite
Rubratope-57
Rubratope-60
Ruvite
Vitamin b 12
Vitamin b12
Α-(5,6-dimethylbenzimidazolyl)cobamide
|
|
29 |
|
Anti-Ulcer Agents |
|
|
|
|
|
30 |
|
Antacids |
|
|
|
|
|
31 |
|
Calcium, Dietary |
|
|
|
|
|
32 |
|
Estradiol 3-benzoate |
|
|
|
|
|
33 |
|
Estradiol 17 beta-cypionate |
|
|
|
|
|
34 |
|
Anesthetics |
|
Early Phase 1 |
|
|
|
35 |
|
Folate |
|
|
|
|
|
36 |
|
Vitamins |
|
|
|
|
|
37 |
|
Vitamin B9 |
|
|
|
|
|
38 |
|
Trace Elements |
|
|
|
|
|
39 |
|
Antimetabolites |
|
|
|
|
|
40 |
|
Vitamin B12 |
|
|
|
|
|
41 |
|
Vitamin B Complex |
|
|
|
|
|
42 |
|
Vitamin B 12 |
|
|
|
|
|
43 |
|
Hypolipidemic Agents |
|
|
|
|
|
44 |
|
Lipid Regulating Agents |
|
|
|
|
|
45 |
|
Gastrointestinal Agents |
|
|
|
|
|
46 |
|
Hematinics |
|
|
|
|
|
47 |
|
Micronutrients |
|
|
|
|
|
48 |
|
Calcium |
Nutraceutical |
|
|
7440-70-2 |
271 |
Synonyms:
Ca
Ca(2+)
Ca2+
Calcio
CALCIUM
Calcium element
|
CALCIUM ion
Calcium(2+)
Calcium, doubly charged positive ion
Calcium, elemental
Elemental calcium
Kalzium
|
|
Interventional clinical trials:
(show all 31)
# |
Name |
Status |
NCT ID |
Phase |
Drugs |
1 |
A Multicenter, Randomized, Double-Blind, Placebo-Controlled, Parallel-Group, Phase 3 Study to Evaluate the Efficacy and Safety of OV101 in Pediatric Individuals With Angelman Syndrome |
Completed |
NCT04106557 |
Phase 3 |
Gaboxadol;Placebo |
2 |
A Phase 2 Randomized Placebo-Controlled Trial of Levodopa in Angelman Syndrome |
Completed |
NCT01281475 |
Phase 2, Phase 3 |
Levodopa;Placebo Oral Capsule |
3 |
An Open-Label Study to Evaluate the Long-Term Safety, Tolerability, and Efficacy of OV101 in Individuals With Angelman Syndrome |
Terminated |
NCT03882918 |
Phase 3 |
OV101 |
4 |
Randomized Clinical Trial, Placebo Compared to Evaluate the Efficacy and Safety of Minocycline in Angelman Syndrome |
Completed |
NCT02056665 |
Phase 2 |
MINOCYCLINE;PLACEBO (for Minocycline) |
5 |
A Phase 2 Adult and Adolescent Angelman Syndrome Clinical Trial: A Randomized, Double-Blind, Safety and Efficacy Study of Gaboxadol |
Completed |
NCT02996305 |
Phase 2 |
OV101 Regimen 1;OV101 regimen 2 |
6 |
A Phase 1/2 Open-label, Multiple-dose, Dose-escalating Clinical Trial of the Safety and Tolerability of GTX-102 in Pediatric Patients With Angelman Syndrome (AS) |
Recruiting |
NCT04259281 |
Phase 1, Phase 2 |
GTX-102 |
7 |
HALOS: A Study to Evaluate the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of Intrathecally Administered ION582 in Patients With Angelman Syndrome |
Recruiting |
NCT05127226 |
Phase 1, Phase 2 |
ION582 |
8 |
An Open-Label Study of the Safety, Tolerability, and Pharmacokinetics of Oral NNZ-2591 in Angelman Syndrome |
Recruiting |
NCT05011851 |
Phase 2 |
NNZ-2591 |
9 |
A Phase IIa Multicenter, Open-Label, 12-Week Study to Investigate the Pharmacokinetics and Safety and to Provide Proof of Mechanism of Alogabat in Children and Adolescents Aged 5-17 Years With Angelman Syndrome (AS) With Deletion Genotype |
Not yet recruiting |
NCT05630066 |
Phase 2 |
60 mg QD Alogabat;40 mg QD Alogabat;7 mg QD Alogabat;Part 2 Adult Alogabat High Dose (aged 15-17);Alogabat;Aligabat |
10 |
A Dose-escalation Tolerability Study of Levodopa/Carbidopa in Angelman Syndrome |
Completed |
NCT00829439 |
Phase 1 |
Levodopa/Carbidopa (4:1) |
11 |
A Phase 1 Single Dose PK Study in Adolescent Subjects With Fragile X Syndrome or Angelman Syndrome |
Completed |
NCT03109756 |
Phase 1 |
OV101 |
12 |
A Non-Randomized, Open-Label, Adaptive, Single Center, Positron Emission Tomography (Pet) Study To Assess Distribution Of RO7248824 In The Central Nervous System Following Single Intrathecal Doses Of [89zr] Labeled RO7248824 In Healthy Male Participants |
Completed |
NCT04863794 |
Phase 1 |
RO7248824 |
13 |
An Open-Label, Multicenter Study To Investigate The Safety, Tolerability, Pharmacokinetics And Pharmacodynamics Of RO7248824 In Participants With Angelman Syndrome |
Recruiting |
NCT04428281 |
Phase 1 |
RO7248824 |
14 |
The Efficacy of Minocycline in the Treatment of Angelman Syndrome |
Unknown status |
NCT01531582 |
|
minocycline |
15 |
Sleep Abnormalities in Rare Genetic Disorders: Angelman Syndrome, Rett Syndrome, and Prader Willi |
Completed |
NCT02670694 |
|
|
16 |
Study on the Brain Network of Angelman Syndrome Based on Multi-modal Brain Image and Neural-EEG Data |
Completed |
NCT03358823 |
|
|
17 |
A Study to Explore Cerebrospinal Fluid and Blood Biomarkers in Participants With Angelman Syndrome |
Completed |
NCT04103333 |
Early Phase 1 |
|
18 |
Parent-child Interaction and Communication in Families Who Have a Child With Rett Syndrome or Angelman Syndrome |
Completed |
NCT03720028 |
|
|
19 |
Efficacy of a Therapeutic Treatment Trial in Angelman Syndrome |
Completed |
NCT00348933 |
|
Betaine;Creatine;Metafolin;Vitamin B12 |
20 |
Angelman Syndrome Natural History Study |
Completed |
NCT00296764 |
|
|
21 |
Evaluation of the Safety and Tolerability of a Nutritional Formulation in Angelman Syndrome |
Completed |
NCT03644693 |
|
|
22 |
Study of Phenotype and Genotype Correlations in Patients With Contiguous Gene Deletion Syndromes |
Completed |
NCT00004351 |
|
|
23 |
SNP-based Microdeletion and Aneuploidy RegisTry |
Completed |
NCT02381457 |
|
|
24 |
Clinical Trial of Levodopa/Carbidopa ( Sinemet) Therapy in Angel Man Syndrome |
Completed |
NCT03235037 |
|
Levodopa |
25 |
A Monocentric, Prospective, Longitudinal and Observational Natural History Study for Patients With Angelman Syndrome in the United Kingdom: Natural History - Foundation for Angelman Syndrome Therapeutics (FAST) United Kingdom (UK) |
Recruiting |
NCT05100810 |
|
|
26 |
Angelman Syndrome Video Assessment (ASVA) Source Material Study |
Recruiting |
NCT05637697 |
|
|
27 |
The Global Angelman Syndrome Registry |
Recruiting |
NCT05293184 |
|
|
28 |
Angelman Syndrome Natural History Study |
Recruiting |
NCT04507997 |
|
|
29 |
Italian Angelman Syndrome Registry Protocol |
Active, not recruiting |
NCT03650569 |
|
|
30 |
Piloting an Early Intervention Program for Infants With Rare Neurogenetic Disorders |
Enrolling by invitation |
NCT03836300 |
|
|
31 |
Circulating Levels of Ghrelin in Patients With a Rare Disease Associated With Intellectual Disability, and Hyperphagia, and / or Overweight, and / or Obesity |
Not yet recruiting |
NCT04768803 |
|
|
|