Drugs for Choroideremia (from DrugBank, HMDB, Dgidb, PharmGKB, IUPHAR, NovoSeek, BitterDB):
(show all 13)
# |
|
Name |
Status |
Phase |
Clinical Trials |
Cas Number |
PubChem Id |
1 |
|
Pharmaceutical Solutions |
|
Phase 3 |
|
|
|
2 |
|
Simvastatin |
Approved |
Phase 1, Phase 2 |
|
79902-63-9 |
54454 |
Synonyms:
(+)-Simvastatin
(1S,3R,7S,8S,8aR)-8-{2-[(2R,4R)-4-hydroxy-6-oxotetrahydro-2H-pyran-2-yl]ethyl}-3,7-dimethyl-1,2,3,7,8,8a-hexahydronaphthalen-1-yl 2,2-dimethylbutanoate
[(1S,3R,7S,8S,8aR)-8-[2-[(2R,4R)-4-hydroxy-6-oxooxan-2-yl]ethyl]-3,7-dimethyl-1,2,3,7,8,8a-hexahydronaphthalen-1-yl] 2,2-dimethylbutanoate
2,2-Dimethylbutanoic acid (1S,3R,7S,8S,8aR)-1,2,3,7,8,8a-hexahydro-3,7-dimethyl-8-[2-[(2R,4R)-tetrahydro-4-hydroxy-6-oxo-2H-pyran-2-yl]ethyl]-1-naphthalenyl ester
2,2-Dimethylbutyrate, 8-ester with (4R,6R)-6-(2-((1S,2S,6R,8S,8ar)-1,2,6,7,8,8a-hexahydro-8-hydroxy-2,6-dimethyl-1-naphthyl)ethyl)tetrahydro-4-hydroxy-2H-pyran-2-one
2,2-dimethylbutyric acid, 8-ester with (4R,6R)-6-(2-((1S,2S,6R,8S,8aR)-1,2,6,7,8,8a-hexahydro-8-hydroxy-2,6-dimethyl-1-naphthyl)ethyl)tetrahydro-4-hydroxy-2H-pyran-2-one
2,2-Dimethylbutyric acid, 8-ester with (4R,6R)-6-(2-((1S,2S,6R,8S,8ar)-1,2,6,7,8,8a-hexahydro-8-hydroxy-2,6-dimethyl-1-naphthyl)ethyl)tetrahydro-4-hydroxy-2H-pyran-2-one
2,2-Dimethylbutyric acid, 8-ester with (4R,6R)-6-(2-((1S,2S,6R,8S,8aR)-1,2,6,7,8,8a-hexahydro-8-hydroxy-2,6-dimethyl-1-naphthyl)ethyl)tetrahydro-4-hydroxy-2H-pyran-2-one
79902-63-9
AC-1530
AC1L1H1F
AKOS005111006
ARONIS24119
BCBcMAP01_000007
BIDD:GT0769
Bio-0672
BPBio1_001001
BRD-K22134346-001-05-8
BRN 4768037
BSPBio_000909
BSPBio_002337
Butanoic acid, 2,2-dimethyl-, (1S,3R,7S,8S,*aR)-1,2,3,7,8,8a-hexahydro-3,7-dimethyl-8-(2-((2R,4R)-tetrahydro-4-hydroxy-6-oxo-2H-pyran-2-yl)ethyl)-1-naphthalenyl ester
Butanoic acid, 2,2-dimethyl-, (1S,3R,7S,8S,8aR)-1,2,3,7,8,8a-hexahydro-3,7-dimethyl-8-(2-((2R,4R)-tetrahydro-4-hydroxy-6-oxo-2H-pyran-2-yl)ethyl)-1-naphthalenyl ester
Butanoic acid, 2,2-dimethyl-, (1S,3R,7S,8S,8aR)-1,2,3,7,8,8a-hexahydro-3,7-dimethyl-8-[2-[(2R,4R)-tetrahydro-4-hydroxy-6-oxo-2H-pyran-2-yl]ethyl]-1-naphthalenyl ester
butanoic acid, 2,2-dimethyl-,1,2,3,7,8,8a-hexahydro-3,7-dimethyl-8-[2-(tetrahydro-4-hydroxy-6-oxo-2H-pyran-2-yl)-ethyl]-1-naphthalenyl ester, [1S-[1 alpha,3 alpha,7 beta,8 beta(2S*,4S*),-8a beta
C25H38O5
CCRIS 7558
CHEBI:9150
CHEMBL1064
Cholestat
CID54454
Coledis
Colemin
Corolin
CPD000718785
D00434
D019821
Denan
DivK1c_006991
DRG-0320
Eucor
HMS1570N11
HMS1922H13
HMS2089D12
HMS2093E06
HSDB 7208
InChI=1/C25H38O5/c1-6-25(4,5)24(28)30-21-12-15(2)11-17-8-7-16(3)20(23(17)21)10-9-19-13-18(26)14-22(27)29-19/h7-8,11,15-16,18-21,23,26H,6,9-10,12-14H2,1-5H3/t15-,16-,18+,19+,20-,21-,23-/m0/s1
KBio1_001935
KBio2_002197
KBio2_004765
KBio2_007333
KBio3_001557
KBioGR_001244
KBioSS_002197
Kolestevan
KS-1113
L 644128-000U
Labistatin
Lipex
Lipinorm
Liponorm
Lipovas
Lodales
LS-46264
Medipo
MK 0733
MK 733
MK-0733
MK733
MK-733
|
MLS001304029
MLS001333077
MLS001333078
MLS002154038
Modutrol
MolPort-002-507-345
MolPort-002-885-862
NCGC00017324-01
NCGC00017324-02
NCGC00017324-03
nchembio790-comp16
Nivelipol
Nor-vastina
Pantok
Pepstatin
Prestwick_171
Prestwick0_000865
Prestwick1_000865
Prestwick2_000865
Prestwick3_000865
Rechol
Rendapid
S1792_Selleck
S6196_SIGMA
SAM002589969
Simcor
Simovil
Simvast CR
simvastatin
Simvastatin
Simvastatin & Primycin
Simvastatin (JAN/USP/INN)
Simvastatin [Usan:Ban:Inn]
Simvastatin [USAN:INN:BAN]
Simvastatin lactone
Simvastatin, Compactin
Simvastatina
Simvastatina [Spanish]
Simvastatine
Simvastatine [French]
Simvastatinum
Simvastatinum [Latin]
Simvotin
Sinvacor
Sinvascor
Sivastin
SMR000718785
SPBio_001881
SPBio_002830
SpecPlus_000895
Spectrum_001717
SPECTRUM1504236
Spectrum2_001671
Spectrum3_000669
Spectrum4_000632
Spectrum5_001428
Statin
STK801938
Synvinolin
TNP00259
UNII-AGG2FN16EV
Valemia
Vasotenal
Velostatin
Vytorin
ZINC03780893
Zocor
Zocor (TN)
Zocor, Simlup, Simcard, Simvacor, Simvoget, Zorced, Simvastatin
Zocord
|
|
3 |
|
Hypolipidemic Agents |
|
Phase 1, Phase 2 |
|
|
|
4 |
|
Hydroxymethylglutaryl-CoA Reductase Inhibitors |
|
Phase 1, Phase 2 |
|
|
|
5 |
|
Anticholesteremic Agents |
|
Phase 1, Phase 2 |
|
|
|
6 |
|
Lipid Regulating Agents |
|
Phase 1, Phase 2 |
|
|
|
7 |
|
Antimetabolites |
|
Phase 1, Phase 2 |
|
|
|
8 |
|
Ornithine |
Approved, Nutraceutical |
|
|
70-26-8, 3184-13-2 |
6262 |
Synonyms:
(+)-S-Ornithine
(S)-2,5-Diaminopentanoate
(S)-2,5-Diaminopentanoic acid
(S)-2,5-Diaminovalerate
(S)-2,5-diaminovaleric acid
(S)-2,5-Diaminovaleric acid
(S)-a,D-Diaminovalerate
(S)-a,D-Diaminovaleric acid
(S)-a,delta-Diaminovalerate
(S)-a,delta-Diaminovaleric acid
(S)-a,δ-diaminovalerate
(S)-a,δ-diaminovaleric acid
(S)-alpha,delta-Diaminovalerate
(S)-alpha,delta-Diaminovaleric acid
(S)-ornithine
(S)-Ornithine
(S)-α,δ-diaminovalerate
(S)-α,δ-diaminovaleric acid
2,5 Diaminopentanoic acid
2,5-Diaminopentanoic acid
|
5-amino-L-Norvaline
L-(-)-Ornithine
levo-ornithine
L-Ornithine
Ornithine
Ornithine dihydrochloride, (L)-isomer
Ornithine hydrochloride, (D)-isomer
Ornithine hydrochloride, (DL)-isomer
Ornithine hydrochloride, (L)-isomer
Ornithine monoacetate, (L)-isomer
Ornithine monohydrobromide, (L)-isomer
Ornithine monohydrochloride, (D)-isomer
Ornithine monohydrochloride, (DL)-isomer
Ornithine phosphate (1:1), (L)-isomer
Ornithine sulfate (1:1), (L)-isomer
Ornithine, (D)-isomer
Ornithine, (DL)-isomer
Ornithine, (L)-isomer
Ornithinum
Ornitina
|
|
9 |
|
Pyridoxine |
Approved, Investigational, Nutraceutical, Vet_approved |
|
|
65-23-6 |
1054 |
Synonyms:
(5-hydroxy-4,6-dimethylpyridin-3-yl)methyl phosphate
12001-78-4
2B3E07D2-E4CC-4CC5-B085-6070BA01F9F0
2-methyl-3-hydroxy-4,5-bis(hydroxy-methyl) pyridine
2-Methyl-3-hydroxy-4,5-bis(hydroxymethyl)pyridine
2-Methyl-3-hydroxy-4,5-di(hydroxymethyl)pyridine
2-Methyl-3-hydroxy-4,5-dihydroxymethyl-pyridin
2-Methyl-3-hydroxy-4,5-dihydroxymethyl-pyridin [German]
2-methyl-3-hydroxy-4,5-dihydroxymethylpyridine
2-Methyl-3-hydroxy-4,5-dihydroxymethylpyridine
2-Methyl-4,5-bis(hydroxymethyl)-3-hydroxypyridine
2-methyl-4,5-dimethylol-pyridin-3-ol
3,4-Pyridinedimethanol, 5-hydroxy-6-methyl-, hydrochloride
3-Hydroxy-2-picoline-4,5-dimethanol
3-hydroxy-4,5-bis(hydroxymethyl)-2-methylpyridine
3-Hydroxy-4,5-bis(hydroxymethyl)-2-methylpyridine
3-Hydroxy-4,5-dihydroxymethyl-2-methylpyridine hydrochloride
3-Hydroxy-4,5-dimethylol-.alpha.-picoline hydrochloride
3-Hydroxy-4,5-dimethylol-alpha-picoline
3-Hydroxy-4,5-dimethylol-alpha-picoline hydrochloride
3-Hydroxy-4,5-dimethylol-a-picoline
3-hydroxy-4,5-dimethylol-α-picoline
3-Hydroxy-4,5-dimethylol-α-picoline
4,5-Bis(hydroxymethyl)-2-methyl-3-pyridinol
4,5-bis(hydroxymethyl)-2-methyl-3-pyridinol hydrochloride
4,5-bis(hydroxymethyl)-2-methylpyridin-3-ol
4,5-Bis(hydroxymethyl)-2-methylpyridin-3-ol hydrochloride
4,5-bis(hydroxymethyl)-2-methylpyridine-3-ol
47862_SUPELCO
4-Deoxypyridoxine 5'-phosphate
58-56-0
58-56-0 (HCL)
58-56-0 (hydrochloride)
5-Hydroxy-6-methyl-3,4-pyridinedicarbinol hydrochloride
5-hydroxy-6-methyl-3,4-pyridinedimethanol
5-Hydroxy-6-methyl-3,4-pyridinedimethanol
5-Hydroxy-6-methyl-3,4-pyridinedimethanol hydrochloride
5-Hydroxy-6-methyl-3,4-pyridinedimethanol, hydrochloride
65-23-6
65-23-6 (Parent)
8059-24-3
85078-23-5
AC-12024
AC-14512
AC1L1AMH
AC1L1LMI
AC1L2XK2
AC1Q22HP
AC1Q2G66
AC1Q3F63
AC-907/25014218
Adermin hydrochloride
Adermine
Adermine hydrochloride
Aderomine hydrochloride
Aderoxin
Aderoxine
AI3-19016
AIDS006784
AIDS-006784
Alestrol
AR-1A6363
AR-1J1632
BB_NC-0050
Becilan
Beesix
Benadon
BIDD:PXR0180
bmse000288
Bonasanit
BPBio1_000646
BSPBio_000586
C00314
c1302
C8H11NO3
Campoviton 6
CAS-58-56-0
CBDivE_015627
CCRIS 1903
Cernevit-12
CHEBI:16709
CHEBI:30961
CHEMBL1200756
CHEMBL1364
CID104817
CID1054
CID6019
component of Alestrol
CPD0-1221
D02179
D025101
D08454
DB00165
EINECS 200-386-2
EINECS 200-603-0
EINECS 232-503-8
Godabion
Gravidox
Hexabetalin
Hexa-Betalin
Hexa-Betalin (R)
Hexa-betalin (TN)
Hexabione hydrochloride
|
Hexavibex
Hexermin
Hexermine
Hexobion
HMS1569N08
HMS2093L07
HSDB 1212
Hydoxin
I02-1897
I02-2297
KST-1A8556
LS-134393
LS-187072
LS-2332
MLS001074329
MLS002153915
MolPort-002-137-856
MolPort-002-319-991
MolPort-005-933-330
NCGC00016261-01
NCGC00164317-01
NCGC00180946-01
nchembio.93-comp1
Nestrex
NSC 36225
NSC36225
NSC36225 (HCL)
Oprea1_061614
P0561
P4722_SIAL
P5669_SIGMA
P6280_SIGMA
P8666_SIGMA
P9755_SIAL
Paxadon
Piridossina
Piridossina [DCIT]
Piridoxina
Piridoxina [INN-Spanish]
PN
PN HCl
Prestwick_925
Prestwick0_000623
Prestwick1_000623
Prestwick2_000623
Prestwick3_000623
Pydox
Pyridipca
Pyridox
Pyridoxin
Pyridoxin hydrochloride
pyridoxine
Pyridoxine
Pyridoxine (INN)
Pyridoxine [INN:BAN]
Pyridoxine chloride
Pyridoxine HCl
Pyridoxine hydrochloride
PYRIDOXINE HYDROCHLORIDE
Pyridoxine Hydrochloride (B6)
Pyridoxine hydrochloride (JP15/USP)
Pyridoxine hydrochloride [USAN:JAN]
PYRIDOXINE HYDROCHLORIDE, U.S.P.
Pyridoxine hydrogen chloride
Pyridoxine monohydrochloride
Pyridoxine, hydrochloride
Pyridoxine-HCl Microencapsulated
Pyridoxinium chloride
Pyridoxinum
Pyridoxinum [INN-Latin]
Pyridoxinum hydrochloricum
Pyridoxinum hydrochloricum (Hungarian)
Pyridoxol
Pyridoxol hydrochloride
Pyridoxol, hydrochloride
Pyridoxolum
Rodex
Rodex (R)
Rodex TD
SMP2_000230
SMR000674613
SPBio_002805
Spondylonal
STK177324
STOCK1N-08684
Tex Six T.R.
TimTec1_000657
UNII-68Y4CF58BV
UNII-KV2JZ1BI6Z
Vitamin B 6
vitamin B6
Vitamin b6
Vitamin B6
Vitamin B6-hydrochloride
Vitamin V6
Vitamin V6 (TN)
Vitamin-?B6
Vitamin-?B6 hydrochloride
Vitaped
WLN: T6NJ B1 CQ D1Q E1Q &GH
ZINC00049154
ZINC21983293
|
|
10 |
|
Pyridoxal Phosphate |
Approved, Investigational, Nutraceutical |
|
|
54-47-7 |
1051 |
Synonyms:
(4-Formyl-5-hydroxy-6-methyl(3-pyridyl))methyl dihydrogen phosphate
(4-formyl-5-hydroxy-6-methyl-3-pyridinyl)methyl dihydrogen phosphate
(4-formyl-5-hydroxy-6-methylpyridin-3-yl)methyl dihydrogen phosphate
2-Methyl-3-hydroxy-4-formyl-5-hydroxymethylpyridine-5-calcium phosphate
2-Methyl-3-hydroxy-4-formyl-5-hydroxymethylpyridine-5-calcium phosphate trihydrate
2-Methyl-3-hydroxy-4-formyl-5-pyridylmethylphosphoric acid
3-hydroxy-2-methyl-5-((phosphonooxy)methyl)-4-pyridinecarboxaldehyde
3-Hydroxy-2-methyl-5-((phosphonooxy)methyl)-4-pyridinecarboxaldehyde
3-hydroxy-2-methyl-5-[(phosphonooxy)methyl]-4-pyridinecarboxaldehyde
3-Hydroxy-2-methyl-5-[(phosphonooxy)methyl]-4-pyridinecarboxaldehyde
3-hydroxy-5-(hydroxymethyl)-2-methylisonicotinaldehyde 5-phosphate
3-Hydroxy-5-(hydroxymethyl)-2-methylisonicotinaldehyde 5-phosphate
3-Hydroxy-5-(hydroxymethyl)-2-methylisonicotinaldehyde 5-phosphoric acid
4-Formyl-5-hydroxy-6-methyl-pyridin-3-yl)methoxyphosphonic acid
4-Pyridinecarboxaldehyde, 3-hydroxy-2-methyl-5-[(phosphonooxy)methyl]- (9CI)
52064-48-9
52441-27-7
54-47-7
A26BDB6A-282A-4D13-A916-7B2B215B0FD6
AC1L1AM8
AC1Q2P2R
Apolon B(sub 6)
Apolon b6
Apolon B6
Biosechs
bmse000111
C00018
CHEBI:18405
CHEMBL82202
CID1051
Codecarboxylase
Coenzyme b6
Coenzyme B6
DB00114
EINECS 200-208-3
Hairoxal
Hexermin P
Hexermin-P
Hiadelon
Himitan
Hi-pyridoxin
HI-Pyridoxin
Isonicotinaldehyde, 3-hydroxy-5-(hydroxymethyl)-2-methyl-, 5-(dihydrogen phosphate)
LS-134383
MolPort-003-939-335
NCGC00166300-01
nchembio.237-comp3
nchembio.266-comp20
nchembio861-comp1
NSC 82388
NSC82388
P-5'-P
Pal-P
PAL-P
Phosphate mono-(4-formyl-5-hydroxy-6-methyl-pyridin-3-ylmethyl) ester
Phosphate, pyridoxal
Phosphopyridoxal
Phosphopyridoxal coenzyme
Phosphoric acid mono-(4-formyl-5-hydroxy-6-methyl-pyridin-3-ylmethyl) ester
|
Phosphoridoxal coenzyme
Pidopidon
Piodel
PLP
Pydoxal
Pyrido
pyridoxal 5-monophosphoric acid ester
Pyridoxal 5 phosphate
Pyridoxal 5'-(dihydrogen phosphate)
Pyridoxal 5'-(dihydrogen phosphoric acid)
Pyridoxal 5-monophosphate ester
Pyridoxal 5-monophosphoric acid ester
pyridoxal 5'-phosphate
pyridoxal 5-phosphate
Pyridoxal 5'-phosphate
Pyridoxal 5-phosphate
Pyridoxal 5'-phosphate hydrate
Pyridoxal 5'-phosphate monohydrate - Vitamin B6
Pyridoxal 5'-phosphate monohydrate, vitamin B6
Pyridoxal 5'-phosphoric acid
Pyridoxal 5-phosphoric acid
Pyridoxal monophosphate
Pyridoxal P
pyridoxal phosphate
Pyridoxal phosphate
Pyridoxal phosphate (6CI)
Pyridoxal phosphate [JAN]
Pyridoxal phosphate anhydrous
Pyridoxal phosphate treated .beta.-lactoglobulin from bovine whey
Pyridoxal phosphoric acid
Pyridoxal, 5-(dihydrogen phosphate)
Pyridoxal, 5-(dihydrogen phosphate) (8CI)
Pyridoxal, 5-(dihydrogenphosphate)
Pyridoxal-5-monophosphate
pyridoxal-5P
Pyridoxal-5P
Pyridoxal-5'-phosphate
PYRIDOXAL-5'-phosphATE
PYRIDOXAL-5-PHOSPHATE
Pyridoxal-5-Phosphate Hydrate
PYRIDOXAL-5'-phosphoric acid
Pyridoxaldehyde phosphate
pyridoxal-P
Pyridoxal-P
Pyridoxyl phosphate
Pyromijin
SBB065295
Sechvitan
Sechvitan, Vitahexin P
SGCUT00188
SRI 2392
TL8005582
to_000077
Vitahexin P
Vitahexin-P
VITAMIN B6 COMPLEX
Vitamin B6 phosphate
Vitamin B6 phosphate (ester)
Vitazechs
|
|
11 |
|
Vitamin B 6 |
|
|
|
|
|
12 |
|
Pyridoxal |
Experimental, Nutraceutical |
|
|
66-72-8 |
1050 |
Synonyms:
2-methyl-3-hydroxy-4-formyl-5-hydroxymethylpyridine
3-hydroxy-5-(hydroxymethyl)-2-methyl-4-pyridinecarboxaldehyde
3-hydroxy-5-(hydroxymethyl)-2-methylisonicotinaldehyde
3-HYDROXY-5-(hydroxymethyl)-2-methylisonicotinaldehyde
|
3-hydroxy-5-(hydroxymethyl)-2-methylpyridine-4-carboxaldehyde
3-Hydroxy-5-(hydroxymethyl)-2-methylpyridine-4-carboxaldehyde
Piridoxal
Pyridoxaldehyde
|
|
13 |
|
Arginine |
Investigational, Nutraceutical |
|
|
74-79-3 |
6322 |
Synonyms:
(2S)-2-amino-5-(carbamimidamido)Pentanoate
(2S)-2-amino-5-(carbamimidamido)pentanoic acid
(2S)-2-amino-5-(carbamimidamido)Pentanoic acid
(2S)-2-amino-5-Guanidinopentanoate
(2S)-2-amino-5-guanidinopentanoic acid
(2S)-2-amino-5-Guanidinopentanoic acid
(S)-2-amino-5-[(Aminoiminomethyl)amino]pentanoate
(S)-2-amino-5-[(Aminoiminomethyl)amino]-pentanoate
(S)-2-amino-5-[(Aminoiminomethyl)amino]pentanoic acid
(S)-2-amino-5-[(Aminoiminomethyl)amino]-pentanoic acid
(S)-2-amino-5-Guanidinopentanoate
(S)-2-amino-5-guanidinopentanoic acid
(S)-2-amino-5-Guanidinopentanoic acid
(S)-2-amino-5-Guanidinovalerate
(S)-2-amino-5-Guanidinovaleric acid
(S)-2-Amino-5-guanidinovaleric acid
2-amino-5-Guanidinovalerate
2-amino-5-Guanidinovaleric acid
5-[(Aminoiminomethyl)amino]-L-norvaline
Arg
Arginina
|
Arginine
Arginine hydrochloride
Arginine, L isomer
Arginine, L-isomer
DL Arginine acetate, monohydrate
DL-Arginine acetate, monohydrate
Hydrochloride, arginine
L Arginine
L-(+)-Arginine
L-a-amino-D-Guanidinovalerate
L-a-amino-D-Guanidinovaleric acid
L-alpha-amino-delta-Guanidinovalerate
L-alpha-amino-delta-Guanidinovaleric acid
L-Arg
L-Arginin
L-arginine
L-Isomer arginine
Monohydrate DL-arginine acetate
N5-(Aminoiminomethyl)-L-ornithine
R
|
|
Interventional clinical trials:
(show all 24)
# |
Name |
Status |
NCT ID |
Phase |
Drugs |
1 |
Management of Retinitis Pigmentosa by Wharton's Jelly Derived Mesenchymal Stem Cells: Preliminary Clinical Results |
Completed |
NCT04224207 |
Phase 3 |
|
2 |
A Randomised, Open Label, Outcomes-Assessor Masked, Prospective, Parallel Controlled Group, Phase 3 Clinical Trial Of Retinal Gene Therapy For Choroideremia Using An Adeno-Associated Viral Vector (AAV2) Encoding Rab Escort Protein 1 (REP1) |
Active, not recruiting |
NCT03496012 |
Phase 3 |
|
3 |
An Open Label Clinical Trial of Retinal Gene Therapy for Choroideremia Using an Adeno-associated Viral Vector (AAV2) Encoding Rab-escort Protein-1 (REP1) |
Completed |
NCT02077361 |
Phase 1, Phase 2 |
|
4 |
An Open Label Phase 2 Clinical Trial of Retinal Gene Therapy for Choroideremia Using an Adeno-associated Viral Vector (AAV2) Encoding Rab-escort Protein 1 (REP1) |
Completed |
NCT02553135 |
Phase 2 |
|
5 |
An Open Label Dose Escalation Phase 1 Clinical Trial of Retinal Gene Therapy for Choroideraemia Using an Adeno-associated Viral Vector (AAV2) Encoding Rab-escort Protein 1 (REP1) |
Completed |
NCT01461213 |
Phase 1, Phase 2 |
rAAV2.REP1 |
6 |
A Phase II/III Study of Encapsulated Human NTC-201 Cell Implants Releasing Ciliary Neurotrophic Factor (CNTF) for Participants With Retinitis Pigmentosa Using Visual Acuity as the Primary Outcome |
Completed |
NCT00447993 |
Phase 2 |
NT-501;NT-501 |
7 |
A Phase II/III Study of Encapsulated Human NTC-201 Cell Implants Releasing Ciliary Neurotrophic Factor (CNTF) for Participants With Retinitis Pigmentosa Using Visual Field Sensitivity as the Primary Outcome |
Completed |
NCT00447980 |
Phase 2 |
NT-501;NT-501 |
8 |
A Phase 1/2 Safety Study in Subjects With CHM (Choroideremia) Gene Mutations Using an Adeno-Associated Virus Serotype 2 Vector to Deliver the Normal Human CHM Gene [AAV2-hCHM] to the Retina |
Active, not recruiting |
NCT02341807 |
Phase 1, Phase 2 |
|
9 |
An Open Label Phase 2 Clinical Trial of Retinal Gene Therapy for Choroideremia Using an Adeno-associated Viral Vector (AAV2) Encoding Rab-escort Protein 1 (REP1) |
Active, not recruiting |
NCT02407678 |
Phase 2 |
|
10 |
An Open-Label Safety Study of Retinal Gene Therapy for Choroideremia With Bilateral, Sequential Administration of Adeno-Associated Viral Vector (AAV2) Encoding Rab Escort Protein 1 (REP1) |
Active, not recruiting |
NCT03507686 |
Phase 2 |
AAV2-REP1 |
11 |
THOR - Tübingen Choroideremia Gene Therapy Trial Open Label Phase 2 Clinical Trial Using an Adeno-associated Viral Vector (AAV2) Encoding Rab-escort Protein 1 (REP1) |
Active, not recruiting |
NCT02671539 |
Phase 2 |
|
12 |
A Repeated Measures Study of Simvastatin on Choroideremia: Simvastatin Intervention and Reversal in Choroideremia Patients and Age-matched Controls. |
Terminated |
NCT01654562 |
Phase 1, Phase 2 |
Simvastatin |
13 |
Extended Pilot Study to Evaluate Pattern Recognition With a Chronic Retinal Implant System |
Unknown status |
NCT00427180 |
|
|
14 |
Restoring Vision With the Intelligent Retinal Implant System (IRIS V1)in Patients With Retinal Dystrophy (Title in France: Compensation of Vision With the Intelligent Retinal Implant System (IRIS V1) in Patients With Retinal Dystrophy) |
Completed |
NCT01864486 |
|
|
15 |
Safety and Feasibility Study of a Prototype Suprachoroidal Retinal Prosthesis for Vision Restoration |
Completed |
NCT01603576 |
|
|
16 |
Compensation for Blindness With the Intelligent Retinal Implant System (IRIS V2) in Patients With Retinal Dystrophy |
Completed |
NCT02670980 |
|
|
17 |
The Diagnosis, Pathogenesis and Treatment of Gyrate Atrophy of the Choroid and Retina |
Completed |
NCT00001166 |
|
|
18 |
Foundation Fighting Blindness Registry, My Retina Tracker |
Recruiting |
NCT02435940 |
|
|
19 |
A Multicenter Prospective Observational "Natural History" Study in Patients With Choroideremia |
Active, not recruiting |
NCT02994368 |
|
|
20 |
Natural History of the Progression of Choroideremia Study |
Active, not recruiting |
NCT03359551 |
|
|
21 |
Evaluation of a Suprachoroidal Retinal Prosthesis: A 44 Channel Fully Implantable Study |
Active, not recruiting |
NCT03406416 |
|
|
22 |
A Long-term Follow-up Study to Evaluate the Safety and Efficacy of Retinal Gene Therapy in Subjects With Choroideremia Treated Previously With Adeno-Associated Viral Vector Encoding Rab Escort Protein-1 (AAV2-REP1) in an Antecedent Study |
Enrolling by invitation |
NCT03584165 |
|
|
23 |
High Resolution Retinal Imaging |
Suspended |
NCT01866371 |
|
|
24 |
Impact on Daily Life of Patients Using the Subretinal Implant RETINA IMPLANT Alpha AMS |
Terminated |
NCT03561922 |
|
|
Cochrane evidence based reviews: choroideremia
|