Drugs for Chronic Progressive External Ophthalmoplegia (from DrugBank, HMDB, Dgidb, PharmGKB, IUPHAR, NovoSeek, BitterDB):
(show all 19)
# |
|
Name |
Status |
Phase |
Clinical Trials |
Cas Number |
PubChem Id |
1 |
|
Cysteamine |
Approved, Investigational |
Phase 2 |
|
60-23-1 |
6058 |
Synonyms:
(2-Mercaptoethyl)amine
(Mercaptoethyl)ammonium toluene-p-sulphonate
.beta.-Mercaptoethylamine
139720-70-0
156-57-0 (hydrochloride)
16904-32-8 (di-hydrochloride)
1-Amino-2-mercaptoethylamine
2 Aminoethanethiol
27761-19-9 (tartrate (1:1))
2-amino-1-ethanethiol
2-amino-1-Ethanethiol
2-Amino-1-ethanethiol
2-aminoethanethiol
2-amino-ethanethiol
2-amino-ETHANETHIOL
2-Aminoethanethiol
2-AMINO-ETHANETHIOL
2-Aminoethyl mercaptan
2DFDA1F8-7010-4225-8280-AB1C4C43F546
2-Mercaptoethanamine
2-Mercaptoethylamine
2-Mercaptoethylamine, polymer-bound
30070_FLUKA
30070_SIGMA
3037-04-5
3037-04-5 (tosylate)
35S-Labeled cysteamine
42954-15-4 (hydrobromide)
60-23-1
60-23-1 (Parent)
641022_ALDRICH
93965-19-6 (maleate (1:1))
A0648
AC1L1LPL
AC1Q54NL
AKOS003793343
Aminoethyl mercaptan
b-Aminoethanethiol
b-Aminoethylthiol
Becaptan
beta Mercaptoethylamine
beta-aminoethanethiol
beta-Aminoethanethiol
beta-Aminoethylthiol
beta-MEA
beta-Mercaptoethylamine
Bitartrate, cysteamine
b-MEA
b-Mercaptoethylamine
bmse000388
C01678
C2H7NS
C-9500
CASH
CCRIS 3083
CHEBI:17141
CHEMBL602
CID6058
Cisteamina
Cisteamina [Italian]
Cystagon
Cystavision
Cysteamide
Cysteamin
Cysteamine
CYSTEAMINE
Cysteamine (USAN)
Cysteamine [USAN:BAN]
Cysteamine bitartate
cysteamine bitartrate
Cysteamine bitartrate
Cysteamine dihydrochloride
|
Cysteamine hydrobromide
Cysteamine hydrochloride
Cysteamine maleate (1:1)
Cysteamine tartrate
Cysteamine tartrate (1:1)
Cysteamine tosylate
Cysteamine, 35S labeled
Cysteamine, 35S-labeled
Cysteaminium
Cysteinamine
D03634
DB00847
Decarboxycysteine
Dihydrochloride, cysteamine
DivK1c_006750
EINECS 200-463-0
EINECS 221-235-7
Ethanethiolamine
HSDB 7353
Hydrobromide, cysteamine
Hydrochloride, cysteamine
KBio1_001694
KBio2_002235
KBio2_004803
KBio2_007371
KBioSS_002235
L 1573
L-1573
Lambraten
Lambratene
Lopac-M-6500
LS-65761
M9768_ALDRICH
M9768_SIGMA
MEA
MEA (mercaptan)
Mecramine
Mercamin
Mercamine
Mercaptamin
Mercaptamina
Mercaptamina [INN-Spanish]
Mercaptamine
Mercaptamine (INN)
Mercaptaminum
Mercaptaminum [INN-Latin]
Mercaptoethylamine
Merkamin
MolPort-001-662-635
NCGC00015691-01
NCGC00015691-04
NCGC00162236-01
nchembio.315-comp1
nchembio.316-comp1
NCI60_002000
NSC 647528
NSC647528
Riacon
SpecPlus_000654
Spectrum_001755
STK315355
Tartrate, cysteamine
Thioethanolamine
Tosylate, cysteamine
UNII-5UX2SD1KE2
WR 347
β-aminoethanethiol
β-aminoethylthiol
β-mea
β-MEA
β-mercaptoethylamine
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2 |
|
Nicotinamide |
Approved, Investigational |
|
|
98-92-0 |
936 |
Synonyms:
.beta.-Pyridinecarboxamide
11032-50-1
123574-63-0
1yc5
3 Pyridinecarboxamide
37321-14-5
3-Carbamoylpyridine
3-pyridinecarboxamide
3-Pyridinecarboxamide
3-Pyridinecarboxylic acid amide
47865U_SUPELCO
55600-01-6
63748-44-7
72340_FLUKA
72340_SIGMA
72347_FLUKA
78731-47-2
98-92-0
A186B02E-6C70-4E54-9739-79398D439AAA
AC1L1ACZ
AC1Q4ZFV
AC-907/25014114
Acid amide
AI3-02906
Amid kyseliny nikotinove
Amid kyseliny nikotinove [Czech]
Amide PP
Aminicotin
Amixicotyn
Amnicotin
Astra brand OF niacinamide
Astra Brand of Niacinamide
Austrovit PP
b 3, Vitamin
B 3, Vitamin
b3, Vitamin
B3, Vitamin
BB_NC-2290
Benicot
beta-Pyridinecarboxamide
bmse000281
b-Pyridinecarboxamide
C00153
C6H6N2O
CCRIS 1901
CHEBI:17154
CHEMBL1140
CID936
CPD000058212
D00036
D009536
DB02701
DEA No. 1405
Delonin amide
Dipegyl
Dipigyl
EINECS 202-713-4
EINECS 234-265-0
Endobion
Enduramide
Factor pp
Factor PP
Hansamid
HMS2052M21
HMS2090B05
HMS2093H03
HSDB 1237
I02-1741
I02-2250
InChI=1/C6H6N2O/c7-6(9)5-2-1-3-8-4-5/h1-4H,(H2,7,9
Inovitan PP
Jenapharm brand OF niacinamide
Jenapharm Brand of Niacinamide
Jenapharm, Nicotinsaureamid
Jenapharm, nicotinsäureamid
LS-2051
m-(Aminocarbonyl)pyridine
Mediatric
Merck brand OF niacinamide
Merck Brand of Niacinamide
MLS000069714
MolMap_000061
MolPort-001-783-876
N0078
N0636_SIGMA
N2142_SIGMA
N3376_SIGMA
N5535_SIAL
NAM
Nandervit-N
NCGC00093354-03
NCGC00093354-04
nchembio.154-comp4
nchembio.73-comp6
Niacevit
Niacin
niacin - Vitamin B3
niacinamide
Niacinamide
Niacinamide (USP)
Niacinamide [USAN]
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Niacinamide astra brand
Niacinamide Astra Brand
Niacinamide jenapharm brand
Niacinamide Jenapharm Brand
Niacinamide merck brand
Niacinamide Merck Brand
Niacinamide pharmagenix brand
Niacinamide Pharmagenix Brand
Niacinamide, Nicotinic acid amide, Nicotinamide
Niacotinamide
Niamide
Niavit PP
Nicamide
Nicamina
Nicamindon
Nicasir
Nicobion
Nicofort
Nicogen
Nicomidol
Nicosan 2
Nicosylamide
Nicota
Nicotamide
Nicotilamide
Nicotililamido
Nicotinamid
Nicotinamida
Nicotinamida [INN-Spanish]
nicotinamide
Nicotinamide
Nicotinamide (JP15/INN)
Nicotinamide (Niacinamide)
Nicotinamide, niacin, vitamin B3
Nicotinamide-carbonyl-14C
Nicotinamidum
Nicotinamidum [INN-Latin]
Nicotinate amide
Nicotine acid amide
Nicotine amide
Nicotinic acid amide
Nicotinic amide
Nicotinsaeureamid
Nicotinsaureamid
Nicotinsaureamid [German]
Nicotinsaureamid Jenapharm
Nicotinsäureamid jenapharm
Nicotol
Nicotylamide
Nicotylamidum
Nicovel
Nicovit
Nicovitina
Nicovitol
Nicozymin
Nictoamide
Nikasan
Nikazan
niko-Tamin
Niko-tamin
Nikotinamid
Nikotinsaeureamid
Nikotinsaeureamid [German]
Niocinamide
Niozymin
NSC 13128
NSC13128
NSC27452
Papulex
Pelmin
Pelmine
Pelonin amide
Pharmagenix brand OF niacinamide
Pharmagenix Brand of Niacinamide
PP-Faktor
Propamine a
pyridine-3-carboxamide
Pyridine-3-carboxylic acid amide
S1899_Selleck
SAM001246860
Savacotyl
SGCUT00176
SMR000058212
to_000073
UNII-25X51I8RD4
Vi-nicotyl
Vi-Nicotyl
Vi-noctyl
Vitamin B
Vitamin B (VAN)
Vitamin b 3
Vitamin B 3
Vitamin b3
Vitamin H1
vitamin PP
Vitamin PP
Witamina PP
WLN: T6NJ CVZ
ZINC00005878
β-pyridinecarboxamide
|
|
3 |
|
Coenzyme Q10 |
Approved, Investigational, Nutraceutical |
|
|
303-98-0 |
5281915 |
Synonyms:
(all-e)-2-(3,7,11,15,19,23,27,31,35,39-Decamethyl-2,6,10,14,18,22,26,30,34,38-tetracontadecaenyl)-5,6-dimethoxy-3-methyl-2,5-cyclohexadiene-1,4-dione
(all-e)-2,3-Dimethoxy-5-methyl-6-(3,7,11,15,19,23,27,31-octamethyl-2,6,10,14,18,22,26,30-dotriacontaoctaenyl)-2,5-cyclohexadiene-1,4-dione
2-((all-e)-3,7,11,15,19,23,27,31,35,39-Decamethyl-2,6,10,14,18,22,26,30,34,38-tetracontadecaenyl)-5,6-dimethoxy-3-methyl-P-benzoquinone
2-(3,7,11,15,19,23,27,31,35,39-Decamethyl-2,6,10,14,18,22,26,30,34,38-tetracontadecaenyl)-5,6-dimethoxy-3-methyl-P-benzoquinone
2,3-Dimethoxy-5-methyl-6-decaprenylbenzoquinone
2-[(2E,6E,10E,14E,18E,22E,26E,30E,34E)-3,7,11,15,19,23,27,31,35,39-Decamethyl-2,6,10,14,18,22,26,30,34,38-tetracontadecaenyl]-5,6-dimethoxy-3-methyl- 2,5-cyclohexadiene-1,4-dione
2-[(2E,6E,10E,14E,18E,22E,26E,30E,34E)-3,7,11,15,19,23,27,31,35,39-Decamethyltetraconta-2,6,10,14,18,22,26,30,34,38-decaen-1-yl]-5,6-dimethoxy-3-methyl-1,4-benzoquinone
4-Ethyl-5-fluoropyrimidine
Adelir
all-trans-Ubiquinone
Aqua Q 10l10
Aqua Q10
bio-Quinon
bio-Quinone Q10
Coenzyme Q10
Coenzyme Q-10
CO-Enzyme Q10
Coenzyme Q10, (Z,Z,Z,Z,Z,Z,e,e,e)-isomer
Coenzyme Q10, ion (1-), (all-e)-isomer
CoQ
CoQ 10
CoQ10
Ensorb
Kaneka Q10
|
Kudesan
Li-Q-sorb
Liquid-Q
Neuquinon
Neuquinone
PureSorb Q 40
Q
Q 10AA
Q 199
Q10
Q-Gel
Q-Gel 100
Q-Ter
Ubidecarenone
Ubiquinone
Ubiquinone 10
Ubiquinone 50
Ubiquinone Q10
UBIQUINONE-10
Ubisemiquinone
Ubisemiquinone radical
Unbiquinone
Unispheres Q 10
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4 |
|
Folic acid |
Approved, Nutraceutical, Vet_approved |
|
|
59-30-3 |
6037 |
Synonyms:
(2S)-2-[[4-[(2-amino-4-oxo-1H-pteridin-6-yl)methylamino]benzoyl]amino]pentanedioic acid
01769_FLUKA
2d0k
33609-88-0
36653-55-1 (mono-potassium salt)
59-30-3
6484-89-5 (mono-hydrochloride salt)
AC-11682
AC1L1LNX
Acfol (Spain)
Acide folique
Acide folique [INN-French]
Acido folico
ácido fólico
Acido folico [INN-Spanish]
Acidum folicum
Acidum folicum [INN-Latin]
Acifolic
AI3-26387
AKOS000503224
Antianemia factor
Apo-Folic
ARONIS014410
b9, Vitamin
BIDD:ER0563
BIDD:GT0641
BIF0608
bmse000299
BPBio1_000654
BSPBio_000594
BSPBio_002338
C00504
C20H20N6O6
CAS-59-30-3
CCRIS 666
CHEBI:27470
CHEMBL1622
CID6037
CPD000471860
Cytofol
D00070
DB00158
DivK1c_000494
Dosfolat b activ
Dosfolat B activ
EINECS 200-419-0
F0043
F7876_SIAL
F7876_SIGMA
F8758_SIGMA
F8798_SIAL
F8890_SIGMA
Facid
Factor U
FOL
Folacid
Folacin
Folaemin
Folaemin [Netherlands]
Folan
Folasic (Australia)
Folate
Folbal
Folcidin
Folcidin (VAN)
Folcysteine
Foldine
Foldine [France]
Folettes
Foliamin
Folic
folic acid
Folic acid
Folic acid (JP15/USP/INN)
Folic acid (TN)
Folic acid [BAN:INN:JAN]
Folic acid [INN:BAN:JAN]
Folic acid dihydrate
Folic acid, (D)-isomer
Folic acid, (DL)-isomer
Folic acid, calcium salt (1:1)
Folic acid, monopotassium salt
Folic acid, monosodium salt
Folic acid, potassium salt
Folic acid, sodium salt
Folicet
Folicet (TN)
Folico
Folico (Italy)
Folina
Folina (Italy)
|
Folipac
Folsaeure
Folsan
Folsaure
Folsäure
Folsav
Folvite
Folvron
Glutamic acid, N-(p-(((2-amino-4-hydroxypyrimido(4,5-b)pyrazin-6-yl)methyl)amino)benzoyl)-, L
HMS1921D20
HMS2092N17
HMS501I16
HSDB 2002
IDI1_000494
Incafolic
InChI=1/C19H19N7O6/c20-19-25-15-14(17(30)26-19)23-11(8-22-15)7-21-10-3-1-9(2-4-10)16(29)24-12(18(31)32)5-6-13(27)28/h1-4,8,12,21H,5-7H2,(H,24,29)(H,27,28)(H,31,32)(H3,20,22,25,26,30)/t12-/m0/s
KBio1_000494
KBio2_001861
KBio2_004429
KBio2_006997
KBio3_001558
KBioGR_002222
KBioSS_001861
Kyselina listova
Kyselina listova [Czech]
Liver lactobacillus casei factor
Liver Lactobacillus casei factor
LS-2157
Millafol
Mission prenatal
Mittafol
MLS001304016
MLS001335861
MolPort-004-285-551
N-(4-(((2-Amino-1,4-dihydro-4-oxo-6-pteridinyl)methyl)amino)benzo- yl)-L-glutamic acid
N-(4-((2-Amino-1,4-dihydro-4-oxo-6-pteridinyl)methyl)amino)benzoyl)-L-glutamic acid
N-(4-{[(2-amino-4-oxo-1,4-dihydropteridin-6-yl)methyl]amino}benzoyl)-L-glutamic acid
N-(4-{[(2-amino-4-oxo-3,4-dihydropteridin-6-yl)methyl]amino}benzoyl)-L-glutamic acid
N-(p-(((2-Amino-4-hydroxy-6-pteridinyl)methyl)amino)benzoyl)-L-glutamic acid
N-[(4-{[(2-amino-4-oxo-1,4-dihydropteridin-6-yl)methyl]amino}phenyl)carbonyl]-L-glutamate
N-[(4-{[(2-amino-4-oxo-1,4-dihydropteridin-6-yl)methyl]amino}phenyl)carbonyl]-L-glutamic acid
N-[4-[[(2-amino-3,4-dihydro-4-oxo-6-Pteridinyl)methyl]amino]benzoyl]-L-glutamic acid
NCGC00016265-01
NCGC00142391-01
nchembio.108-comp10
Nifolin
Nifolin [Denmark]
NINDS_000494
Novofolacid
Novofolacid [Canada]
N-Pteroyl-L-glutamate
N-pteroyl-L-glutamic acid
N-Pteroyl-L-glutamic acid
NSC 3073
PGA
PGA (VAN)
Prestwick_230
Prestwick3_000627
PteGlu
Pteroylglutamate
Pteroylglutamic acid
Pteroyl-L-glutamate
Pteroyl-L-glutamic acid
Pteroyl-L-monoglutamate
Pteroyl-L-monoglutamic acid
Pteroylmonoglutamate
Pteroylmonoglutamic acid
SAM002264616
SDCCGMLS-0066738.P001
Serum Folate Level
SMP2_000137
SMR000471860
SPBio_001357
Spectrum_001381
SPECTRUM1502020
Spectrum2_001459
Spectrum3_000749
Spectrum4_001751
Spectrum5_000602
UNII-935E97BOY8
Usaf cb-13
Vitamin B11
Vitamin b9
Vitamin B9
Vitamin Bc
Vitamin BC
Vitamin be
Vitamin Be
Vitamin m
Vitamin M
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5 |
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Niacin |
Approved, Investigational, Nutraceutical |
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59-67-6 |
938 |
Synonyms:
3 Pyridinecarboxylic acid
3-Carboxylpyridine
3-carboxypyridine
3-Carboxypyridine
3-Pyridinecarboxylate
3-Pyridinecarboxylic acid
3-Pyridylcarboxylate
3-Pyridylcarboxylic acid
Acide nicotinique
acido Nicotinico
ácido nicotínico
Acidum nicotinicum
Acidum Nicotinicum
Akotin
Aluminum salt, niacin
anti-pellagra vitamin
Anti-pellagra vitamin
Apelagrin
beta-Pyridinecarboxylate
beta-Pyridinecarboxylic acid
b-Pyridinecarboxylate
b-Pyridinecarboxylic acid
Daskil
Efacin
Enduracin
Hydrochloride, niacin
Induracin
Linic
Lithium nicotinate
m-Pyridinecarboxylate
m-pyridinecarboxylic acid
m-Pyridinecarboxylic acid
Niac
Niacin
Niacin aluminum salt
Niacin ammonium salt
Niacin calcium salt
Niacin cobalt (2+) salt
Niacin copper (2+) salt
Niacin hydrochloride
Niacin iron (2+) salt
Niacin lithium salt
Niacin lithium salt, hemihydrate
Niacin magnesium salt
Niacin manganese (2+) salt
Niacin potassium salt
Niacin sodium salt
Niacin tartrate
|
Niacin tosylate
Niacin zinc salt
Niacina
Niacine
Niacor
Nicacid
Nicamin
Nicangin
nico 400
nico-400
Nico400
Nicobid
Nicocap
Nicodelmine
Nicolar
Niconacid
Nicosan 3
nico-Span
Nicotinate
Nicotinate, lithium
Nicotinic acid
Nicotinipca
Nicyl
Nikotinsaeure
Nikotinsäure
Nyclin
P.P. factor
Pellagra preventive factor
Pellagrin
Pelonin
Potassium salt, niacin
PP Factor
Pyridine-b-carboxylate
Pyridine-b-carboxylic acid
Pyridine-beta-carboxylate
Pyridine-beta-carboxylic acid
Pyridine-β-carboxylate
pyridine-β-carboxylic acid
Pyridine-β-carboxylic acid
slo-Niacin
Sodium salt, niacin
Tartrate, niacin
Tosylate, niacin
Vitamin b3
Wampocap
β-pyridinecarboxylate
β-pyridinecarboxylic acid
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6 |
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Ubiquinone |
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7 |
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Trace Elements |
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8 |
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Micronutrients |
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9 |
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Vitamins |
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10 |
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Vitamin B Complex |
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11 |
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Nicotinic Acids |
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12 |
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Vitamin B3 |
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13 |
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Vasodilator Agents |
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14 |
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Folate |
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15 |
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Lipid Regulating Agents |
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16 |
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Nutrients |
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17 |
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Hypolipidemic Agents |
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18 |
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Vitamin B9 |
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19 |
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Antimetabolites |
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Interventional clinical trials:
# |
Name |
Status |
NCT ID |
Phase |
Drugs |
1 |
A Long-Term Open-Label Extension Study of RP103-MITO-001 to Assess the Safety, Tolerability and Efficacy of Cysteamine Bitartrate Delayed-release Capsules (RP103) for Treatment of Children With Inherited Mitochondrial Disease |
Terminated |
NCT02473445 |
Phase 2 |
Cysteamine Bitartrate |
2 |
A Phase Ia/Ib, Multiple-site Study to Assess the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of KL1333 After a Single and Multiple Ascending Oral Doses in Healthy Subjects and Patients With Primary Mitochondrial Disease |
Recruiting |
NCT03888716 |
Phase 1 |
KL1333;Placebo Oral Tablet |
3 |
Clinical Characteristics and Prognostic Factors of Mitochondrial nt3243 A>G Mutation in Taiwan |
Unknown status |
NCT02114554 |
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4 |
Magnetic Resonance Imaging Study of Patients With Chronic Progressive External Ophthalmoplegia |
Completed |
NCT02161848 |
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5 |
Can Metagenomic and Metadata be Combined Using Bioinformatics and Computational Biology Methods to Personalise Patient Treatment. |
Completed |
NCT03213067 |
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6 |
The Effect of Niacin Supplementation on Systemic Nicotinamide Adenine Dinucleotide (NAD+) Metabolism, Physiology and Muscle Performance in Healthy Controls and Mitochondrial Myopathy Patients |
Completed |
NCT03973203 |
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7 |
North American Mitochondrial Disease Consortium Patient Registry and Biorepository (NAMDC) |
Recruiting |
NCT01694940 |
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8 |
The Role of Nicotinamide Riboside in Mitochondrial Biogenesis |
Recruiting |
NCT03432871 |
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9 |
Rare Disease Clinical Research Network Natural History of Pearson Syndrome North American Mitochondrial Disease Consortium (NAMDC) |
Enrolling by invitation |
NCT02327364 |
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