Drugs for Muscular Dystrophy (from DrugBank, HMDB, Dgidb, PharmGKB, IUPHAR, NovoSeek, BitterDB):
(show top 50)
(show all 230)
# |
|
Name |
Status |
Phase |
Clinical Trials |
Cas Number |
PubChem Id |
1 |
|
Carvedilol |
Approved, Investigational |
Phase 4 |
|
72956-09-3 |
2585 |
Synonyms:
(+-)-1-(Carbazol-4-yloxy)-3-((2-(O-methoxyphenoxy)ethyl)amino)-2-propanol
14C-Labeled carvedilol
Artist
BM 14.190
BM-14.190
BM-14190
BM-14-190
C07AG02
CARVEDILOL
Carvédilol
Carvedilol hydrochloride
Carvedilol, (-)
Carvedilol, (-)-isomer
Carvedilol, (+)
Carvedilol, (+)-isomer
Carvedilol, (+-)-isomer
Carvedilol, (R)-isomer
Carvedilol, (S)-isomer
Carvedilol, 14C labeled
|
Carvedilol, 14C-labeled
Carvedilolum
Carvedilolum [Latin]
Coreg
COREG CR
Coreg®|DQ 2466|Eucardic®|SKF 105517
Coropres
Dilatrend
DQ 2466
DQ-2466
Eucardic
EUCARDIC 12.5
EUCARDIC 25
EUCARDIC 3.125
EUCARDIC 6.25
Kredex
Querto
SKF 105517
SKF-105517
|
|
2 |
|
Ramipril |
Approved |
Phase 4 |
|
87333-19-5 |
5362129 |
Synonyms:
(2S-(1(R*(r*)),2a,3abeta,6abeta))-1-(2-((1-(ethoxycarbonyl)-3-phenylpropyl)amino)-1-oxopropyl)octahydrocyclopenta(b)pyrrole-2-carboxylate
(2S-(1(R*(r*)),2a,3abeta,6abeta))-1-(2-((1-(ethoxycarbonyl)-3-phenylpropyl)amino)-1-oxopropyl)octahydrocyclopenta(b)pyrrole-2-carboxylic acid
(2S-(1(R*(r*)),2alpha,3abeta,6abeta))-1-(2-((1-(ethoxycarbonyl)-3-phenylpropyl)amino)-1-oxopropyl)octahydrocyclopenta(b)pyrrole-2-carboxylate
(2S-(1(R*(r*)),2alpha,3abeta,6abeta))-1-(2-((1-(ethoxycarbonyl)-3-phenylpropyl)amino)-1-oxopropyl)octahydrocyclopenta(b)pyrrole-2-carboxylic acid
(2S-(1(R*(r*)),2α,3abeta,6abeta))-1-(2-((1-(ethoxycarbonyl)-3-phenylpropyl)amino)-1-oxopropyl)octahydrocyclopenta(b)pyrrole-2-carboxylate
(2S-(1(R*(r*)),2α,3abeta,6abeta))-1-(2-((1-(ethoxycarbonyl)-3-phenylpropyl)amino)-1-oxopropyl)octahydrocyclopenta(b)pyrrole-2-carboxylic acid
Acovil
Almirall brand OF ramipril
Altace
ALTACE (TN)
Altace®|HOE-498|Tritace®
Astra brand OF ramipril
AstraZeneca brand OF ramipril
Aventis brand OF ramipril
Aventis pharma brand OF ramipril
C09AA05
Carasel
Cardace
Delix
HOE 498
HOE-498
|
Hoechst brand OF ramipril
Hypren
Hytren
LOPACE
Lostapres
Monarch brand OF ramipril
Pramace
Promed brand OF ramipril
Quark
Ramace
RAMICOR
RAMIPRIL
Ramiprilum
Ramiprilum [Latin]
RANACE
Triatec
Tritace
Unipril
Vesdil
Zabien
|
|
3 |
|
Tadalafil |
Approved, Investigational |
Phase 4 |
|
171596-29-5 |
110635 |
Synonyms:
(6R,12AR)-2,3,6,7,12,12a-hexahydro-2-methyl-6-(3,4-(methylenedioxy)phenyl) pyrazino(1',2':1,6)pyrido(3,4-b)indole-1,4-dione
(6R-trans)-6-(1,3-Benzodioxol-5-yl)-2,3,6,7,12,12a-hexahydro-2-methyl-pyrazino(1',2':1,6)pyrido(3,4-b)indole-1,4-dione
351, IC
6-BENZO[1,3]dioxol-5-yl-2-methyl-2,3,6,7,12,12a-hexahydro-pyrazino[1',2':1,6]pyrido[3,4-b]indole-1,4-dione
Adcirca
Adcirca®|Cialis®|IC-351|IC351
Cialis
|
IC351
IC-351
ICOS 351
Tadalafil
Tadalafilo
Tadanafil
Zalutia
|
|
4 |
|
Risedronic acid |
Approved, Investigational |
Phase 4 |
|
105462-24-6 |
5245 |
Synonyms:
1-Hydroxy-2-(3-pyridyl)ethylidene diphosphonate
2-(3-Pyridinyl)-1-hydroxyethylidenebisphosphonate
2-(3-Pyridinyl)-1-hydroxyethylidene-bisphosphonate
Acid, risedronic
Acide risédroniqe
Acido risedronico
Acidum risedronicum
Actonel
Actonel 150
Actonel®|Atelvia®|NE-58095|risedronate sodium
Atelvia
Benet
Bisphosphate risedronate sodium
Bisphosphonate risedronate sodium
|
M05BA07
NE-58095
Ridron
Risedronate
Risedronate sodium
Risedronate sodium, bisphosphate
Risedronate sodium, bisphosphonate
Risedronic acid
Risedronic acid, monosodium salt
Risedronsäure
Sodium, bisphosphate risedronate
Sodium, bisphosphonate risedronate
Sodium, risedronate
|
|
5 |
|
Alendronic acid |
Approved |
Phase 4 |
|
121268-17-5, 66376-36-1 |
2088 |
Synonyms:
(4-amino-1-hydroxybutane-1,1-diyl)bis(phosphonic acid)
(4-Amino-1-hydroxybutylidene)bisphosphonate
(4-Amino-1-hydroxybutylidene)bisphosphonic acid
4 amino 1 Hydroxybutylidene 1,1 biphosphonate
4-amino-1-hydroxybutane-1,1-diphosphonic acid
4-Amino-1-hydroxybutylidene 1,1-biphosphonate
ABDP
ABDP|BPH 1|Fosamax®|MK-217
Acide alendronique
Acide Alendronique [INN-French]
Acido alendronico
Acido Alendronico [INN-Spanish]
Acidum alendronicum
Acidum Alendronicum [INN-Latin]
Adronat
Alendronate
|
Alendronate monosodium salt, trihydrate
Alendronate sodium
Alendronate sodium hydrate
Alendronic acid
Alendros
Aminohydroxybutane bisphosphonate
Arendal
BINOSTO
Bisphosphonate, aminohydroxybutane
BPH 1
Fosamax
Fosamax Plus D
G-704650
MK-217
Onclast
Sodium, alendronate
|
|
6 |
|
Prednisolone phosphate |
Approved, Vet_approved |
Phase 4 |
|
302-25-0 |
|
Synonyms:
Prednisolone 21-(dihydrogen phosphate)
Prednisolone 21-monophosphate
|
Prednisolone 21-phosphate
|
|
7 |
|
Prednisolone acetate |
Approved, Vet_approved |
Phase 4 |
|
52-21-1 |
|
Synonyms:
ECONOPRED
FLO-PRED
METICORTELONE
NSC-10966
OMNIPRED
PRED FORTE
|
PRED FTE
PRED MILD
PREDNISOLONE 21-ACETATE
PREDNISOLONE ACETATE
STERANE
ULTRACORTENOL
|
|
8 |
|
Prednisolone |
Approved, Vet_approved |
Phase 4 |
|
50-24-8 |
4894 5755 |
Synonyms:
(11b)-11,17,21-Trihydroxypregna-1,4-diene-3,20-dione
(11beta)-11,17,21-Trihydroxypregna-1,4-diene-3,20-dione
(11Β)-11,17,21-trihydroxypregna-1,4-diene-3,20-dione
1,4-Pregnadiene-11b,17a,21-triol-3,20-dione
1,4-Pregnadiene-11beta,17alpha,21-triol-3,20-dione
1,4-Pregnadiene-11β,17α,21-triol-3,20-dione
1,4-Pregnadiene-3,20-dione-11b,17a,21-triol
1,4-Pregnadiene-3,20-dione-11beta,17alpha,21-triol
1,4-Pregnadiene-3,20-dione-11β,17α,21-triol
3,20-Dioxo-11b,17a,21-trihydroxy-1,4-pregnadiene
3,20-Dioxo-11beta,17alpha,21-trihydroxy-1,4-pregnadiene
3,20-Dioxo-11β,17α,21-trihydroxy-1,4-pregnadiene
Ak-Pred
Ak-Tate
Alphadrol
Articulose-50
Codelcortone
Co-Hydeltra
Cordrol
CORTALONE
Cotogesic
Cotolone
Decaprednil
Decortin H
DEKOTIL
Delcortol
Delta F
Delta(1)-Dehydrocortisol
Delta(1)-Dehydrohydrocortisone
Delta(1)-Hydrocortisone
DELTA.1-CORTISOL
DELTA.1-Cortisol|Orapred®|Pediapred®
Delta-Cortef
Deltacortenol
DELTACORTRIL
Deltacortril Enteric
delta-dehydrocortisol
delta-dehydrohydrocortisone
delta-hydrocortisone
Deltahydrocortisone
DELTALONE
Deltasolone
Delta-Stab
Deltisilone
Depo-Medrol
Derpo Pd
DESOWEN
Dexa-Cortidelt Hostacortin H
Di adreson F
Di-Adreson F
Di-adreson-F
DiAdresonF
Dicortol
DILACORT
Donisolone
Dydeltrone
Eazolin D
Econopred
Econopred Plus
Erbacort
Erbasona
Estilsona
Fernisolone
Fernisolone P
FERNISOLONE-P
Flamasone
Hostacortin H
HYDELTRA
Hydeltrasol
HYDELTRA-TBA
Hydeltrone
Hydrodeltalone
Hydrodeltisone
Hydroretrocortin
Hydroretrocortine
IMS904
Inflamase Forte
Inflamase Mild
I-Pred
Key-Pred
Klismacort
Lentosone
Lite Pred
Medrol
|
Medrol Acetate
Metacortandralone
Methylprednisolone acetate
METICORTELONE
METI-DERM
Metreton
M-Predrol
NEO-DELTA-CORTEF
Nisolone
Nor-Pred T.B.A.
NSC-9120
NSC-9900
Ocu-Pred
Ocu-Pred Forte
Ophtho-Tate
ORAPRED
Panafcortelone
Paracortol
Paracotol
PEDIAPRED
PEVANTI
POLY-PRED
PRDL
Precortalon
Precortancyl
Precortilon
PRECORTISYL
PRECORTISYL FTE
Pred Forte
Pred Mild
Predair
Predair A
Predair Forte
Predalone 50
Predalone T.B.A.
Predate
Predate Tba
Predate-50
Predcor-25
Predcor-50
Predcor-Tba
PRED-G
Predisolone sodium phosphate
PREDL
Predne-Dome
Prednelan
Prednicen
Predni-Dome
Predniliderm
Predniretard
Prednis
Prednisolona
Prednisolona [INN-Spanish]
Prednisolone
Prednisolone acetate
Prednisolone sodium phosphate
Prednisolone tebutate
Prednisolonum
Prednisolonum [INN-Latin]
Predonin
Predonine
PRELONE
Prenolone
Rolisone
SCHERIPROCT
Scherisolon
SERVISONE
Solone
Steran
STERANE
Sterolone
Supercortisol
TRIDESILON
Ulacort
Ultra Pred
Ultracorten H
Ultracortene H
Ultracortene-H
Ultracortene-Hydrogen
VERDESO
Δ(1)-dehydrocortisol
Δ(1)-dehydrohydrocortisone
Δ(1)-hydrocortisone
Δ-cortef
|
|
9 |
|
Methylprednisolone hemisuccinate |
Approved |
Phase 4 |
|
2921-57-5 |
1875 |
Synonyms:
Methylprednisolone hemisuccinate
Methylprednisolone hemisuccinic acid
|
Methylprednisolone hydrogen succinate
Methylprednisolone succinate
|
|
10 |
|
Methylprednisolone |
Approved, Vet_approved |
Phase 4 |
|
83-43-2 |
4159 6741 |
Synonyms:
(6a,11b)-11,17,21-Trihydroxy-6-methylpregna-1,4-diene-3,20-dione
(6alpha,11beta)-11,17,21-Trihydroxy-6-methylpregna-1,4-diene-3,20-dione
(6Α,11β)-11,17,21-trihydroxy-6-methylpregna-1,4-diene-3,20-dione
1-Dehydro-6alpha-methylhydrocortisone
1-Dehydro-6a-methylhydrocortisone
1-Dehydro-6α-methylhydrocortisone
6 Methylprednisolone
6alpha-Methyl-11beta,17alpha,21-triol-1,4-pregnadiene-3,20-dione
6alpha-Methylprednisolone
6a-Methyl-11b,17a,21-triol-1,4-pregnadiene-3,20-dione
6a-Methylprednisolone
6-Methylprednisolone
6Α-methyl-11β,17α,21-triol-1,4-pregnadiene-3,20-dione
6Α-methylprednisolone
Artisone-Wyeth
Besonia
Delta(1)-6alpha-Methylhydrocortisone
delta(1)-6a-Methylhydrocortisone
Dopomedrol
Esametone
Firmacort
J3.872E
Lemod
Medesone
Medixon
Medlone 21
Medrate
Medric acid
Medrol
Medrol Adt Pak
Medrol Dosepak
Medrol®|U-67590A
Medrone
Mesopren
|
Metastab
Methyleneprednisolone
Methylprednisolon
Methylprednisolone
Methylprednisolonum
Methylprednisolonum [INN-Latin]
Metilbetasone
Metilprednisolona
Metilprednisolona [INN-Spanish]
Metilprednisolone
Metilprednisolone [Dcit]
Metipred
Metrisone
Metrocort
Metysolon
Moderin
Nirypan
Noretona
NSC-19987
Predni N Tablinen
Promacortine
Reactenol
Sieropresol
Solomet
SOLU-MEDROL
Summicort
Suprametil
U-67590A
Urbason
Urbasone
Wyacort
Δ(1)-6a-methylhydrocortisone
Δ(1)-6α-methylhydrocortisone
|
|
11 |
|
Cholecalciferol |
Approved, Nutraceutical, Vet_approved |
Phase 4 |
|
67-97-0, 1406-16-2 |
5280795 10883523 |
Synonyms:
(+)-Vitamin D3
(1S,3Z)-3-[(2E)-2-[(1R,3AR,7as)-7a-methyl-1-[(2R)-6-methylheptan-2-yl]-2,3,3a,5,6,7-hexahydro-1H-inden-4-ylidene]ethylidene]-4-methylidene-cyclohexan-1-ol
(1S,3Z)-3-[(2E)-2-[(1R,3AS,7AR)-1-[(1R)-1,5-DIMETHYLHEXYL]-7A-METHYL-2,3,3A,5,6,7-HEXAHYDRO-1H-INDEN-4-YLIDENE]ETHYLIDENE]-4-METHYLENE-1-CYCLOHEXANOL
(1S,3Z)-3-[(2E)-2-[(1R,3AS,7AR)-1-[(1R)-1,5-DIMETHYLHEXYL]-7A-METHYL-2,3,3A,5,6,7-HEXAHYDRO-1H-INDEN-4-YLIDENE]ETHYLIDENE]-4-METHYLENE-CYCLOHEXAN-1-OL
(1S,3Z)-3-[(2E)-2-[(1R,3AS,7AR)-7A-METHYL-1-[(2R)-6-METHYLHEPTAN-2-YL]-2,3,3A,5,6,7-HEXAHYDRO-1H-INDEN-4-YLIDENE]ETHYLIDENE]-4-METHYLIDENECYCLOHEXAN-1-OL
(1S,3Z)-3-[(2E)-2-[(1R,3AS,7AR)-7A-METHYL-1-[(2R)-6-METHYLHEPTAN-2-YL]-2,3,3A,5,6,7-HEXAHYDRO-1H-INDEN-4-YLIDENE]ETHYLIDENE]-4-METHYLIDENE-CYCLOHEXAN-1-OL
(1S,3Z)-3-{2-[(1R,4E,7AR)-7A-METHYL-1-[(2R)-6-METHYLHEPTAN-2-YL]-OCTAHYDRO-1H-INDEN-4-YLIDENE]ETHYLIDENE}-4-METHYLIDENECYCLOHEXAN-1-OL
(3 beta,5Z,7E)-9,10-Secocholesta-5,7,10(19)-trien-3-ol
(3b,5Z,7E)-9,10-Secocholesta-5,7,10(19)-trien-3-ol
(3beta,5Z,7E)-9,10-Secocholesta-5,7,10(19)-trien-3-ol
(3BETA,Z,7E)-9,10-SECOCHOLESTA-5,7,10(19)-TRIEN-3-OL
(3Β,5Z,7E)-9,10-secocholesta-5,7,10(19)-trien-3-ol
(5E,7E)-9,10-SECOCHOLESTA-5,7,10-TRIEN-3-OL
(5Z,7E)-(3S)-9,10-Secocholesta-5,7,10(19)-trien-3-ol
3-BETA,Z,7E-9,10-SECOCHOLESTR-5,7,10(19)-TRIEN-3-OL
7-DEHYDROCHOLESTEROL
9,10-SECOCHOLESTA-5,7,10(19)-TRIEN-3BETA-OL
9,10-SECOCHOLESTA-5,7,10(19)-TRIEN-3-BETA-OL
9,10-SECOCHOLESTA-5,7,10(19)-TRIEN-3-OL
9,10-SECOCHOLESTA-5,7,10-TRIEN-3-OL
ACCRETE D3
ACIFEROL D3
ACTIVATED
Activated 7-dehydrocholesterol
ADCAL-D3
ARACHITOL
AVITICOL
BIOLIFE VITAMIN D3
BIO-VITAMIN D3
CACIT D3
CALCEOS
CALCICHEW D3
CALCICHEW D3 FTE
CALCICHEW D3 ONCE DAILY
CALCI-D
Calciferol
Calciol
CALDRINK D3
CALFOVIT D3
CC
Cholecalciferol
CHOLECALCIFEROL D3
Cholecalciferols
Cholecalciferolum
COLECAL D3
Colecalciferol
Colecalciferolum
COLEKAL-D3
COLEVIT D3
CUBICOLE D3
D3 LEMON MELTS
D3-50
D3-VIGANTOL
DEKRISTOL
DELSTEROL
Delta-D
DEPARAL
DESUNIN
DEVARON
Dihydrocholesterol
DLUX 400
D-MAX
D-TRACETTEN
|
D-VIT3
EBIVIT
E-D3
EVACAL D3
FERACOL
FULTIUM DAILY D3
FULTIUM-D3
GRANUVIT D3
HUX D3
INVITA D3
ISO D3
KORA LIQUID
MICRO-DEE
NATECAL D3
NATURE'S REMEDY VITAMIN D3
NEO-D
NPHD3
NSC-375571
Oleovitamin D3
OSTEOCAPS D3
PLENACHOL
PRO D3
PRO D3 FOLIC
PRO D3 FORTE
PROVITINA
QUINTOX
RICKETON
ROYALVIT D3
STEXEROL-D3
STIVIT-D3
SUNVIT-D3 1,000
SUNVIT-D3 10,000
SUNVIT-D3 2,000
SUNVIT-D3 20,000
SUNVIT-D3 3,000
SUNVIT-D3 400
SUNVIT-D3 5,000
SUNVIT-D3 50,000
SUNVIT-D3 800
SYNERVIT-D3
THEICAL D-3
THORENS
TRIVITAN
VIDDE-3-HYDROSOL
VI-DE3
VIDEKHOL
VIGANTOL
VIGANTOLETTEN
VIGANTOLETTEN 500
VIGORSAN
VIT D3 STREULI
VITA-D3
VITAMIN D
Vitamin D 3
VITAMIN D ASSAY SYSTEM SUITABILITY
Vitamin D NOS
Vitamin D, unspecified form
Vitamin D3
Vitamin D-3
VITINC DAN-DEE-3
ZYMAD
δ-D
|
|
12 |
|
Prednisolone hemisuccinate |
Experimental |
Phase 4 |
|
2920-86-7 |
4897 |
Synonyms:
(+)-prednisolone hemisuccinate
4-(2-{14,17-dihydroxy-2,15-dimethyl-5-oxotetracyclo[8.7.0.0,.0,]heptadeca-3,6-dien-14-yl}-2-oxoethoxy)-4-oxobutanoate
Prednisolonbisuccinat
Prednisolone 21-hemisuccinate
Prednisolone 21-succinate
|
Prednisolone bisuccinate
PREDNISOLONE HEMISUCCINATE
Prednisolone hemisuccinic acid
Prednisolone hydrogen succinate
PREDNISOLONE SUCCINATE
|
|
13 |
|
Adrenergic beta-Antagonists |
|
Phase 4 |
|
|
|
14 |
|
Adrenergic Antagonists |
|
Phase 4 |
|
|
|
15 |
|
Adrenergic alpha-Antagonists |
|
Phase 4 |
|
|
|
16 |
|
Adrenergic alpha-1 Receptor Antagonists |
|
Phase 4 |
|
|
|
17 |
|
Vitamins |
|
Phase 4 |
|
|
|
18 |
|
Phosphodiesterase Inhibitors |
|
Phase 4 |
|
|
|
19 |
|
Phosphodiesterase 5 Inhibitors |
|
Phase 4 |
|
|
|
20 |
|
Vasodilator Agents |
|
Phase 4 |
|
|
|
21 |
|
Calcium, Dietary |
|
Phase 4 |
|
|
|
22 |
|
calcium channel blockers |
|
Phase 4 |
|
|
|
23 |
|
Anti-Bacterial Agents |
|
Phase 4 |
|
|
|
24 |
|
Vaccines |
|
Phase 4 |
|
|
|
25 |
|
Calciferol |
|
Phase 4 |
|
|
|
26 |
|
Diphosphonates |
|
Phase 4 |
|
|
|
27 |
|
Antibiotics, Antitubercular |
|
Phase 4 |
|
|
|
28 |
|
Anti-Inflammatory Agents |
|
Phase 4 |
|
|
|
29 |
|
Hormones |
|
Phase 4 |
|
|
|
30 |
|
Antineoplastic Agents, Hormonal |
|
Phase 4 |
|
|
|
31 |
|
Hormone Antagonists |
|
Phase 4 |
|
|
|
32 |
|
glucocorticoids |
|
Phase 4 |
|
|
|
33 |
|
Methylprednisolone Acetate |
|
Phase 4 |
|
|
584547 |
Synonyms:
Acetyl methylprednisolone
Acetyl-methylprednisolone
DEPMEDALONE
Depo medrol
Depo medrone
Depo-medrol
Depo-medrone
|
MEDROL ACETATE
Methylprednisolone 21 acetate
METHYLPREDNISOLONE ACETATE
Methylprednisolone acetate, (11beta,16alpha)-isomer
Methylprednisolone acetate, (11beta,16beta)-isomer
Methylprednisolone acetic acid
Methylprednisolone-21-acetate
|
|
34 |
|
Calcium |
Nutraceutical |
Phase 4 |
|
7440-70-2 |
271 |
Synonyms:
Ca
Ca(2+)
Ca2+
Calcio
CALCIUM
Calcium element
|
CALCIUM ion
Calcium(2+)
Calcium, doubly charged positive ion
Calcium, elemental
Elemental calcium
Kalzium
|
|
35 |
|
Lisinopril |
Approved, Investigational |
Phase 2, Phase 3 |
|
83915-83-7, 76547-98-3 |
5362119 |
Synonyms:
(S)-1-(N(2)-(1-Carboxy-3-phenylpropyl)-L-lysyl)-L-proline
[N2-[(S)-1-CARBOXY-3-phenylpropyl]-L-lysyl-L-proline
Acerbon
Acercomp
Alapril
Carace
Cipral
Cipril
Coric
Inhibril
Inopril
Linopril
Linvas
Lipril
Lisinal
LISINOPRIL
Lisinopril anhydrous
LISINOPRIL DIHYDRATE
LISINOPRIL HYDRATE
Lisinopril maleate (1:1)
Lisinopril sulfate (1:2)
Lisinoprilum
Lisipril
|
Lisoril
Lispril
Loril
LPR
Lysinopril
MK-521
Noperten
Novatec
Presiten
Prinil
Prinivil
Prinivil®|Zestril®
Prinzide
Renacor
Sinopril
Sinopryl
Tensopril
Tensyn
Tersif
Vivatec
Zestoretic
Zestril
|
|
36 |
|
Metformin |
Approved |
Phase 3 |
|
1115-70-4, 657-24-9 |
4091 |
Synonyms:
[<sup>14</sup>C]-metformin
1,1-Dimethyl biguanide
1,1-Dimethylbiguanide
1-CARBAMIMIDAMIDO-N,N-DIMETHYLMETHANIMIDAMIDE
Apo-Metformin
BOLAMYN SR
Diabefagos
Diabex
Diaformin
DIAGEMET XL
Dianben
Dimethylbiguanid
Dimethylbiguanide
Dimethylbiguanidine
Dimethyldiguanide
Dimethylguanylguanidine
DMBG
Fortamet
Gen-Metformin
GLUCAMET 500
GLUCAMET 850
GLUCIENT SR
Glucophage
GLUCOPHAGE SR
GLUCOPHAGE XR
Glumetza
Glycon
GLYFORMIN
HCL, Metformin
Hydrochloride, metformin
JANUMET
LA 6023
LA-6023
|
LEDERMETIN
Meguan
METABET SR
Metformin
Metformin HCL
Metformin hydrochloride
Metformina
Metformine
Metforminum
Metiguanide
METSOL
MILFORM
Mylan-Metformin
N(1),N(1)-Dimethylbiguanide
N,N-Dimethylbiguanide
N,N-Dimethyldiguanide
N,N-Dimethylguanylguanidine
N,N-Dimethylimidodicarbonimidic diamide
N1,N1-Dimethylbiguanide
Novo-Metformin
NSC-91485
Nu-Metformin
Obimet
ORABET
PMS-Metformin
Ran-Metformin
Ratio-Metformin
Riomet
Sandoz Metformin
SUKKARTO SR
Teva-Metformin
XLA399
|
|
37 |
|
Nebivolol |
Approved, Investigational |
Phase 3 |
|
152520-56-4, 99200-09-6, 118457-14-0 |
71301 |
Synonyms:
1,1'-[Bis(6-fluoro-3,4-dihydro-2H-1-benzopyran-2-yl)]-2,2'-iminodiethanol
1,1'-Bis(6-fluoro-3,4-dihydro-2H-1-benzopyran-2-yl)-2,2'-iminodiethanol
a,Alpha'-(iminobismethylene)bis-(6-fluoro-3,4-dihydro-2H-1-benzopyran-2-methanol)
alpha,Alpha'-(iminobis(methylene))bis(6-fluoro-3,4-dihydro)-2H-1-benzopyran-2-methanol
alpha,Alpha'-(iminobismethylene)bis-(6-fluoro-3,4-dihydro-2H-1-benzopyran-2-methanol)
ALPHA,ALPHA'-(IMINODIMETHYLENE)BIS-(6-FLUORO-2-CHROMANMETHANOL)
Bystolic
Bystolic®|R-65824|Ro-67555
Hydrochloride, nebivolol
HYPOLOC
Lobivon
NARBIVOLOL
Nebicard-5
Nebilet
|
Nebilong
Nebipill
NEBIVOLOL
Nebivolol hydrochloride
NEBIVOLOLUM
nebivololum [latin]
Nodon
Nubeta
PI-21858
R-65824
RO-67555
Silostar
Α,alpha'-(iminobismethylene)bis-(6-fluoro-3,4-dihydro-2H-1-benzopyran-2-methanol)
|
|
38 |
|
Enalaprilat |
Approved |
Phase 3 |
|
76420-72-9 |
6917719 5462501 |
Synonyms:
1-(N-((S)-1-Carboxy-3-phenylpropyl)-L-alanyl)-L-proline dihydrate
Anhydrous enalaprilat citrate
Anhydrous, enalaprilat
Biovail brand OF enalaprilat anhydrous
Boehringer ingelheim brand OF enalaprilat anhydrous
Dihydrate, enalaprilat
Enalapril acid
Enalapril diacid
Enalapril teva
ENALAPRILAT
Enalaprilat anhydrous
Enalaprilat citrate, anhydrous
Enalaprilat dihydrate
Enalaprilat, (R)-isomer, anhydrous
|
Enalaprilate
Enalaprilatum
Enalaprilic acid
Enalapril-teva
EnalaprilTEVA
Merck frosst brand OF enalaprilat anhydrous
MK-421
MK-422
MSD Brand OF enalaprilat
N-[(1S)-1-Carboxy-3-phenylpropyl]-L-alanyl-L-proline
Pres IV
Teva brand OF enalaprilat
Vasotec
Xanef
|
|
39 |
|
Enalapril |
Approved, Vet_approved |
Phase 3 |
|
75847-73-3 |
40466924 5388962 5362032 |
Synonyms:
(S)-1-(N-(1-(Ethoxycarbonyl)-3-phenylpropyl)-L-alanyl)-L-proline
(S)-1-{(S)-2-[1-((S)-ethoxycarbonyl)-3-phenyl-propylamino]-propionyl}-pyrrolidine-2-carboxylate
(S)-1-{(S)-2-[1-((S)-ethoxycarbonyl)-3-phenyl-propylamino]-propionyl}-pyrrolidine-2-carboxylic acid
1-(N-((S)-1-Carboxy-3-phenylpropyl)-L-alanyl)-L-proline 1'-ethyl ester
Analapril
ánalapril
Bonuten
C09AA02
ENALADEX
Enaladex®|Vasotec®
Enalapril
Enalapril Bp
Enalapril maleate
Enalapril Richet
Enalaprila
|
Enalaprila [INN-Spanish]
Enalaprilat
Enalaprilum
Enalaprilum [INN-Latin]
EPL753
Gadopril
Kinfil
LEXXEL
Maleate, enalapril
Renitec
Renitek
VASERETIC
VASOTEC
Vasotec IV
|
|
40 |
|
Eplerenone |
Approved |
Phase 3 |
|
107724-20-9 |
443872 |
Synonyms:
9,11-Epoxy-7-(methoxycarbonyl)-3-oxo-17-pregn-4-ene-21,17-carbolactone
Eplerenon
Eplerenona
EPLERENONE
Epoxymexrenone
|
Inspra
Inspra®|SC-66110
SC-66110
SC-6611O
|
|
41 |
|
Metoprolol |
Approved, Investigational |
Phase 3 |
|
37350-58-6, 51384-51-1 |
4171 |
Synonyms:
(+/-)-metoprolol
(RS)-Metoprolol
1-(Isopropylamino)-3-[4-(2-methoxyethyl)phenoxy]propan-2-ol
Beatrolol
Beloc
Beloc duriles
Beloc-duriles
BelocDuriles
Betaloc
Betaloc astra
Betaloc-astra
BetalocAstra
Betalok
CGP-2175
CGP-2175C
CGP-2175C|GP-2175E|H-93/26|Lopressor®|Toprol®
CR-XL, Metoprolol
DL-Metoprolol
GP-2175E
H-93/26
Lopresor
Lopresoretic
LOPRESSIDONE
Lopressor
Lopressor HCT
|
Meijoprolol
Metohexal
METOPROLOL
Metoprolol CR XL
Metoprolol CR-XL
Metoprolol succinate
Metoprolol tartrate
Metoprololum
Metroprolol
Preblok
Prelis
Presolol
Seloken
Selopral
Selo-Zok
Seroken
Spesicor
Spesikor
Succinate, metoprolol
Tartrate, metoprolol
Toprol
Toprol XL
ToprolXL
Toprol-XL
|
|
42 |
|
Bisoprolol |
Approved |
Phase 2, Phase 3 |
|
66722-44-9 |
2405 |
Synonyms:
(+-)-1-((a-(2-Isopropoxyethoxy)-p-tolyl)oxy)-3-(isopropylamino)-2-propanol
(+-)-1-((alpha-(2-Isopropoxyethoxy)-p-tolyl)oxy)-3-(isopropylamino)-2-propanol
(+-)-1-((Α-(2-isopropoxyethoxy)-p-tolyl)oxy)-3-(isopropylamino)-2-propanol
(RS)-1-(4-(2-Isopropoxyethoxymethyl)phenoxy)-3-(isopropylamino)-2-propanol
Bisoprolol
Bisoprolol fumarate
Bisoprolol fumarate (1:1) salt, (+-)-isomer
Bisoprolol fumarate (2:1) salt, (+-)-isomer
Bisoprolol fumerate
Bisoprolol hemifumarate
Bisoprolol hydrochloride
Bisoprolol methanesulfonate salt
Bisoprolol, (-)-isomer
Bisoprolol, (+-)-isomer
Bisoprolol, fumarate (1:1) salt
Bisoprolol, fumarate (2:1) salt
Bisoprololum
Cardicor
CL-297939
|
Concor
Condyline
Condylox
CONGESCOR
Detensiel
Emconcor
Emcor
EMD-33512
EMD-33-512
Euradal
Fumarate, bisoprolol
Hydrochloride, bisoprolol
Isoten
Merck brand OF bisoprolol fumarate
Monocor
Soloc
Soprol
ZEBETA
ZIAC
|
|
43 |
|
Tamoxifen |
Approved |
Phase 3 |
|
10540-29-1, 54965-24-1 |
2733526 |
Synonyms:
(Z)-2-(4-(1,2-Diphenyl-1-butenyl)phenoxy)-N,N-dimethylethanamine
(Z)-2-(Para-(1,2-diphenyl-1-butenyl)phenoxy)-N,N-dimethylamine
1-Para-b-dimethylaminoethoxyphenyl-trans-1,2-diphenylbut-1-ene
1-Para-beta-dimethylaminoethoxyphenyl-trans-1,2-diphenylbut-1-ene
1-Para-β-dimethylaminoethoxyphenyl-trans-1,2-diphenylbut-1-ene
1-p-b-Dimethylaminoethoxyphenyl-trans-1,2-diphenylbut-1-ene
1-p-beta-Dimethylaminoethoxyphenyl-trans-1,2-diphenylbut-1-ene
1-p-Β-dimethylaminoethoxyphenyl-trans-1,2-diphenylbut-1-ene
Apo-tamox
Citofen
Citrate, tamoxifen
Crisafeno
Diemon
EMBLON
FENTAMOX 10
FENTAMOX 20
Gen-tamoxifen
I.C.I.46474 CITRATE
ICI-46474
ICI-46474|Nolvadex®|Soltamox®
ICI-47699
Istubol
KENTADEX
KESSAR
KESSAR 10
KESSAR 20
Noltam
Nolvadex
NOLVADEX D
NOLVADEX FTE
Nolvadex-D
Nourytam
|
Novaldex
Novo-Tamoxifen
OESTRIFEN-10
OESTRIFEN-20
OESTRIFEN-40
Oncomox
PMS-Tamoxifen
Retaxim
Savient brand OF tamoxifen citrate
Soltamox
Tamizam
Tamofen
Tamone
Tamoplex
Tamoxasta
Tamoxen
TAMOXIFEN
Tamoxifen citrate
Tamoxifene
TAMOXIFÈNE
Tamoxifene [INN-French]
Tamoxifeno
Tamoxifeno [INN-Spanish]
Tamoxifenum
Tamoxifenum [INN-Latin]
Tomaxithen
trans-Tamoxifen
Valodex
ZD6157
Zemide
Zitazonium
ZYNOPLEX
|
|
44 |
|
Prednisone |
Approved, Vet_approved |
Phase 3 |
|
53-03-2 |
5865 |
Synonyms:
1,2-Dehydrocortisone
1,4-Pregnadiene-17a,21-diol-3,11,20-trione
1,4-Pregnadiene-17alpha,21-diol-3,11,20-trione
1,4-Pregnadiene-17α,21-diol-3,11,20-trione
17,21-Dihydroxypregna-1,4-diene-3,11,20-trione
Acis brand OF prednisone
Acsis, prednison
Adasone
Ancortone
Apo-prednisone
Apotex brand OF prednisone
Aventis brand OF prednisone
Betapar
Bicortone
Cartancyl
Colisone
Cortan
Cortancyl
Cortidelt
Cotone
Cutason
Dacorten
Dacortin
Decortancyl
Decortin
Decortisyl
Dehydrocortisone
Dekortin
Delcortin
Dellacort
Dellacort A
Delta Cortelan
Delta E
Delta-cortelan
Deltacortene
delta-Cortisone
Deltacortisone
Deltacortone
Delta-cortone
DELTA-DOME
Deltasone
Deltison
Deltisona
Deltisone
Deltra
Diadreson
Di-Adreson
Diba brand OF prednisone
Econosone
Encorton
Encortone
Enkortolon
Enkorton
Fawns and mcallan brand OF prednisone
FERNISONE
Ferring brand OF prednisone
Fiasone
GALENpharma brand OF prednisone
Halsey drug brand OF prednisone
Hexal brand OF prednisone
Hoechst brand OF prednisone
Hostacortin
ICN brand OF prednisone
Incocortyl
In-Sone
Juvason
Kortancyl
Lichtenstein brand OF prednisone
|
Liquid pred
Lisacort
LODOTRA
Lodotra®|Sterapred®
Me-Korti
Merck brand OF prednisone
Merz brand OF prednisone
Metacortandracin
Meticorten
Mibe brand OF prednisone
Nisona
Nizon
Novoprednisone
NSC-10023
Nurison
Orasone
Origen Prednisone
Panafcort
Panasol
PARACORT
Parmenison
Pehacort
Pharmacia brand OF prednisone
PRD
Precort
Predeltin
PREDN
Predni tablinen
PREDNICEN-M
Prednicorm
Prednicort
Prednicot
Prednidib
Prednilonga
Predniment
Prednison
Prednison acsis
Prednison galen
Prednison hexal
Prednisona
Prednisona [INN-Spanish]
Prednisone
PREDNISONE INTENSOL
PREDNISONE TABLETS
Prednisonum
Prednisonum [INN-Latin]
Prednitone
Prednizon
Prednovister
Presone
Pronison
Pronisone
RAYOS
Rectodelt
Retrocortine
Schering-plough brand OF prednisone
Seatrace brand OF prednisone
SERVISONE
Solvay brand OF prednisone
Sone
Sterapred
Supercortil
Trommsdorff brand OF prednisone
Ultracorten
Ultracortene
Winpred
Wojtab
Zenadrid
|
|
45 |
|
Idebenone |
Approved, Investigational |
Phase 3 |
|
58186-27-9 |
3686 |
Synonyms:
2-(10-hydroxydecyl)-5,6-dimethoxy-3-methyl-1,4-benzoquinone
2-(10-HYDROXYDECYL)-5,6-DIMETHOXY-3-METHYLCYCLOHEXA-2,5-DIENE-1,4-DIONE
2-(10-HYDROXYDECYL)-5,6-DIMETHOXY-3-METHYL-P-BENZOQUINONE
2,3-DIMETHOXY-5-METHYL-6-(10'-HYDROXYDECYL)-1,4-BENZOQUINONE
6-(10-HYDROXYDECYL)-2,3-DIMETHOXY-5-METHYL-1,4-BENZOQUINONE
6-(10-HYDROXYDECYL)-2,3-DIMETHOXY-5-METHYL-P-BENZOQUINONE
|
BRN 2001459
CV 2619
idebenona
IDEBENONE
idébénone
RAXONE
|
|
46 |
|
L-Glutamine |
Approved, Investigational, Nutraceutical |
Phase 2, Phase 3 |
|
56-85-9 |
5961 |
Synonyms:
(2S)-2,5-Diamino-5-oxopentanoate
(2S)-2,5-DIAMINO-5-OXOPENTANOIC ACID
(2S)-2-Amino-4-carbamoylbutanoate
(2S)-2-AMINO-4-CARBAMOYLBUTANOIC ACID
(S)-2,5-Diamino-5-oxopentanoate
(S)-2,5-DIAMINO-5-OXOPENTANOIC ACID
[<sup>14</sup>C]-glutamine
[<sup>3</sup>H]-glutamine
2-Aminoglutaramic acid
Cebrogen
D Glutamine
D-Glutamine
ENDARI
FEMA NO. 3684
gamma-Glutamine
Glavamin
GLN
Glumin
Glutamate 5-amide
Glutamate amide
GLUTAMIC ACID 5-AMIDE
GLUTAMIC ACID AMIDE
Glutamina
GLUTAMINE
L Glutamine
L-(+)-GLUTAMINE
|
L-2-Aminoglutaramate
L-2-AMINOGLUTARAMIC ACID
L-2-Aminoglutaramidic acid
Levoglutamid
Levoglutamida
LEVOGLUTAMIDE
Levoglutamidum
Levoglutamina
L-Glutamate g-amide
L-Glutamate gamma-amide
L-Glutamate γ-amide
L-Glutamic acid 5-amide
L-Glutamic acid g-amide
L-GLUTAMIC ACID GAMMA-AMIDE
L-GLUTAMIC ACID Γ-AMIDE
L-Glutamid
L-Glutamide
L-GLUTAMIN
L-GLUTAMINE
L-GLUTAMINSAEURE-5-AMID
L-GLUTAMINSÄURE-5-AMID
NSC-27421
NUTRESTORE
Polyglutamine
Q
Stimulina
|
|
47 |
|
Ubidecarenone |
Approved, Investigational, Nutraceutical |
Phase 3 |
|
303-98-0 |
5281915 |
Synonyms:
(all-e)-2-(3,7,11,15,19,23,27,31,35,39-Decamethyl-2,6,10,14,18,22,26,30,34,38-tetracontadecaenyl)-5,6-dimethoxy-3-methyl-2,5-cyclohexadiene-1,4-dione
(all-e)-2,3-Dimethoxy-5-methyl-6-(3,7,11,15,19,23,27,31-octamethyl-2,6,10,14,18,22,26,30-dotriacontaoctaenyl)-2,5-cyclohexadiene-1,4-dione
2-((all-e)-3,7,11,15,19,23,27,31,35,39-Decamethyl-2,6,10,14,18,22,26,30,34,38-tetracontadecaenyl)-5,6-dimethoxy-3-methyl-p-benzoquinone
2-(3,7,11,15,19,23,27,31,35,39-Decamethyl-2,6,10,14,18,22,26,30,34,38-tetracontadecaenyl)-5,6-dimethoxy-3-methyl-p-benzoquinone
2,3-Dimethoxy-5-methyl-6-decaprenylbenzoquinone
2-[(2E,6E,10E,14E,18E,22E,26E,30E,34E)-3,7,11,15,19,23,27,31,35,39-Decamethyl-2,6,10,14,18,22,26,30,34,38-tetracontadecaenyl]-5,6-dimethoxy-3-methyl- 2,5-cyclohexadiene-1,4-dione
2-[(2E,6E,10E,14E,18E,22E,26E,30E,34E)-3,7,11,15,19,23,27,31,35,39-Decamethyltetraconta-2,6,10,14,18,22,26,30,34,38-decaen-1-yl]-5,6-dimethoxy-3-methyl-1,4-benzoquinone
4-Ethyl-5-fluoropyrimidine
Adelir
all-trans-Ubiquinone
API 31510
API-31510
Aqua Q 10l10
Aqua Q10
Bio-quinon
Bio-quinone Q10
Coenzyme Q10
Coenzyme Q-10
CO-Enzyme Q10
CoQ
CoQ 10
CoQ10
Ensorb
Kaneka Q10
|
Kudesan
Li-Q-sorb
Liquid-Q
Neuquinon
Neuquinone
NSC-140665
NSC-140865
PureSorb Q 40
Q
Q 10AA
Q 199
Q10
Q-Gel
Q-Gel 100
Q-Ter
Ubidecarenone
UBIDECARENONE FOR SYSTEM SUITABILITY
Ubiquinone
Ubiquinone 10
Ubiquinone 50
Ubiquinone Q10
UBIQUINONE-10
Unbiquinone
Unispheres Q 10
|
|
48 |
|
Epigallocatechin gallate |
Investigational |
Phase 2, Phase 3 |
|
989-51-5 |
65064 |
Synonyms:
(-)-Epigallocatechin gallat
(-)-EPIGALLOCATECHIN GALLATE
(-)-EPIGALLOCATECHIN-3-O-GALLATE
(-)-Epigallocatechin-3-O-gallic acid
(-)-Epigallocatechol gallate
(-)-Epigallocatehin gallate
[(2R,3R)-5,7-DIHYDROXY-2-(3,4,5-TRIHYDROXYPHENYL)-3,4-DIHYDRO-2H-CHROMEN-3-YL] 3,4,5-TRIHYDROXYBENZOATE
[(2R,3R)-5,7-Dihydroxy-2-(3,4,5-trihydroxyphenyl)-3,4-dihydro-2H-chromen-3-yl] 3,4,5-trihydroxybenzoic acid
Catechin deriv.
egcg
EGCG CPD
EGCG|epigallocatechin gallate
Epigallocatcchin gallate
Epigallocate
|
Epigallocatechin 3-gallate
Epigallocatechin 3-gallic acid
Epigallo-catechin gallate
EPIGALLOCATECHIN GALLATE
EPIGALLOCATECHIN GALLATE,EGCG
Epigallocatechin gallic acid
Epigallocatechin-3-gallate
Epigallocatechin-3-O-gallate
Epigallocic acid
EPIGALOCATECHIN GALLATE
Galloyl-L-epigallocatechol
Sunphenon
Tea catechin
|
|
49 |
|
Epigallocatechin |
Experimental, Investigational |
Phase 2, Phase 3 |
|
970-74-1 |
72277 |
Synonyms:
(-)-3,3',4',5,5',7-Flavanhexol
(-)-3,3’,4’,5,5’,7-Flavanhexol
(-)-cis-3,3',4',5,5',7-Hexahydroxyflavan
(-)-cis-3,3',4',5,5',7-Hexahydroxyflavane
(−)-epigallocatechin
(-)-epi-Gallocatechin
(-)-Epigallocatechin
(-)-Epigallocatechol
(2R,3R)-2-(3,4,5-Trihydroxyphenyl)-3,4-dihydro-2H-chromene-3,5,7-triol
(2R,3R)-2-(3,4,5-Trihydroxyphenyl)-3,5,7-trihydroxychroman
(2R,3R)-3,4-Dihydro-2-(3,4,5-trihydroxyphenyl)-2H-1-benzopyran-3,5,7-triol
1-epi-3',4',5',5,7-Pentahydroxy-3-flavanol
1-epi-3’,4’,5’,5,7-Pentahydroxy-3-flavanol
2,3-cis-Epigallocatechin
|
3,3',4',5,5',7-Flavanhexol
3,3’,4’,5,5’,7-Flavanhexol
Antiscurvy factor C2
EGC
epi-Gallocatechin
Epigallocatechin
Epigallocatechol
Gallocatechin
Gallocatechol
Gallocatechol, (2R-cis)-isomer
Gallocatechol, (2R-trans)-isomer
Galloepicatechin
L-Epigallocatechin
l-Epigallocatechol
|
|
50 |
|
Cardiotonic Agents |
|
Phase 2, Phase 3 |
|
|
|
Interventional clinical trials:
(show top 50)
(show all 519)
# |
Name |
Status |
NCT ID |
Phase |
Drugs |
1 |
Effects of Cardioprotective Therapy, Carvedilol vs Ramipril, in Patients Affected by Duchenne and Becker Muscular Dystrophy. Clinical Significance and Prognostic Value of Cardiac Magnetic Resonance Study. |
Unknown status |
NCT00819845 |
Phase 4 |
carvedilol;ramipril |
2 |
Carvedilol for the Prevention of Minor Cardiac Damage and Cardiac Function in Duchenne Muscular Dystrophy |
Unknown status |
NCT00606775 |
Phase 4 |
Carvedilol |
3 |
Comparison of the Immunogenicity of Intramuscular Versus Subcutaneous Administration of Trivalent Inactivated Influenza Vaccine in Individuals With Neuromuscular Diseases |
Completed |
NCT01422200 |
Phase 4 |
|
4 |
Functional Muscle Ischemia and PDE5A Inhibition in Becker Muscular Dystrophy |
Completed |
NCT01070511 |
Phase 4 |
Tadalafil;Placebo |
5 |
Évaluation Multidimensionnelle de la réponse au Traitement de l'ostéoporose spontanée et Induite Par Les corticostéroïdes à l'Aide d'un Bisphosphonate à Administration Orale Chez Des Malades Porteurs d'Une Dystrophie Musculaire sévère. |
Completed |
NCT01882400 |
Phase 4 |
Bisphosphonate treatment |
6 |
Stacking Exercises Attenuate the Decline in Forced Vital Capacity and Sick Time (STEADFAST) |
Completed |
NCT01999075 |
Phase 4 |
|
7 |
Phase-2 Trial of 5mg/kg/Week Prednisolone in Young Boys With DMD |
Recruiting |
NCT05412394 |
Phase 4 |
Prednisolone |
8 |
Long-term Use of Viltolarsen in Boys With Duchenne Muscular Dystrophy in Clinical Practice (VILT-502) |
Active, not recruiting |
NCT04687020 |
Phase 4 |
Viltolarsen |
9 |
An Open-Label Study to Evaluate the Safety of Golodirsen in Non-Ambulant Patients With Duchenne Muscular Dystrophy |
Terminated |
NCT04708314 |
Phase 4 |
Golodirsen 50 MG/1 ML Intravenous Solution [VYONDYS 53] |
10 |
PITT0908: Clinical Trial of Coenzyme Q10 and Lisinopril in Muscular Dystrophies |
Completed |
NCT01126697 |
Phase 2, Phase 3 |
Coenzyme Q10 and Lisinopril |
11 |
An Open-Label Study for Previously Treated Ataluren (PTC124®) Patients With Nonsense Mutation Dystrophinopathy |
Completed |
NCT01557400 |
Phase 3 |
Ataluren |
12 |
A Randomized, Double-Blind, Placebo-Controlled, Global Phase 3 Study of Edasalonexent in Pediatric Patients With Duchenne Muscular Dystrophy |
Completed |
NCT03703882 |
Phase 3 |
Edasalonexent;Placebo |
13 |
Effects of Sodium Nitrate on Blood Flow in Becker Muscular Dystrophy |
Completed |
NCT02147639 |
Phase 2, Phase 3 |
|
14 |
An Open-Label, Multi-Center, Study With a Concurrent Untreated Control Arm to Evaluate the Efficacy and Safety of Eteplirsen in Duchenne Muscular Dystrophy |
Completed |
NCT02255552 |
Phase 3 |
eteplirsen |
15 |
"A Double Blind Randomised Placebo Controlled Efficacy and Safety Study of L-citrulline and Metformin in Ambulant Children Aged Between 7 and 10 Years With Duchenne's Muscular Dystrophy" |
Completed |
NCT01995032 |
Phase 3 |
750 mg metformin and 7.5 g L-citrulline daily p.o.;Placebo |
16 |
A Randomized, Double Blind, Placebo-Controlled, Study to Assess the Efficacy, Safety, and Tolerability of RO7239361 in Ambulatory Boys With Duchenne Muscular Dystrophy |
Completed |
NCT03039686 |
Phase 2, Phase 3 |
RO7239361;Placebo for RO7239361 |
17 |
A Multicenter Randomized Placebo-controlled Double-blind Study to Assess Efficacy and Safety of Glutamine and Creatine Monohydrate in Duchenne Muscular Dystrophy |
Completed |
NCT00016653 |
Phase 2, Phase 3 |
Creatine Monohydrate;Glutamine |
18 |
A Randomized, Double-Blind, Placebo-Controlled, Multi-center Study to Examine the Effect of Nebivolol, a Beta-Blockade Drug, for the Prevention of Ventricular Systolic Dysfunction in Patients With Duchenne Muscular Dystrophy |
Completed |
NCT01648634 |
Phase 3 |
Nebivolol;Placebo |
19 |
Myocardial Fibrosis Progression in Duchenne and Becker Muscular Dystrophy - Angiotensin-Converting-Enzyme (ACE) Inhibitor Therapy |
Completed |
NCT02432885 |
Phase 3 |
Enalapril |
20 |
A Randomized Study of Daily vs. High-dose Weekly Prednisone Therapy in Duchenne Muscular Dystrophy |
Completed |
NCT00110669 |
Phase 3 |
Prednisone |
21 |
A Phase III Double-Blind, Randomised, Placebo-Controlled Study of the Efficacy, Safety and Tolerability of Idebenone in 10-18 Year Old Patients With Duchenne Muscular Dystrophy |
Completed |
NCT01027884 |
Phase 3 |
Placebo;Idebenone |
22 |
Phase III Randomized, Double-Blind Study of Prednisone for Duchenne Muscular Dystrophy |
Completed |
NCT00004646 |
Phase 3 |
prednisone |
23 |
A Multicenter Randomized Placebo-Controlled Double-Blind Study to Assess Efficacy and Safety of Glutamine and Creatine Monohydrate in Duchenne Muscular Dystrophy (DMD) |
Completed |
NCT00018109 |
Phase 3 |
glutamine;creatine monohydrate |
24 |
Duchenne Muscular Dystrophy: Double-blind Randomized Trial to Find Optimum Steroid Regimen |
Completed |
NCT01603407 |
Phase 3 |
Prednisone;Deflazacort |
25 |
Therapeutic Potential for Aldosterone Inhibition in Duchenne Muscular Dystrophy |
Completed |
NCT02354352 |
Phase 3 |
Eplerenone;Spironolactone |
26 |
A Phase III, Randomized, Double Blind, Placebo-controlled Clinical Study to Assess the Efficacy and Safety of GSK2402968 in Subjects With Duchenne Muscular Dystrophy |
Completed |
NCT01254019 |
Phase 3 |
GSK2402968 6mg/kg/week |
27 |
Sunphenon Epigallocatechin-Gallate (EGCg) in Duchenne Muscular Dystrophy |
Completed |
NCT01183767 |
Phase 2, Phase 3 |
Epigallocatechin-Gallate;Placebo |
28 |
Randomised, Double Blind, Placebo Controlled, Multicentre Study to Evaluate the Efficacy and Safety of Givinostat in Ambulant Patients With Duchenne Muscular Dystrophy |
Completed |
NCT02851797 |
Phase 3 |
givinostat;placebo |
29 |
A Pivotal, Multicenter, Open-label, Randomized Withdrawal, Non-Treatment Concurrent Control Study to Assess the Safety, Tolerability, and Efficacy of Cabaletta® in OPMD Patients Who Participated in Study BBCO-001 |
Completed |
NCT02328482 |
Phase 3 |
Tehalose 30gr |
30 |
A Phase 3 Efficacy and Safety Study of Ataluren in Patients With Nonsense Mutation Dystrophinopathy |
Completed |
NCT01826487 |
Phase 3 |
Ataluren;Placebo |
31 |
Deflazacort in Dysferlinopathies (LGMD2B/MM) - a Double Blind, Placebo-controlled Clinical Study |
Completed |
NCT00527228 |
Phase 2, Phase 3 |
deflazacort;placebo |
32 |
A PHASE 3, MULTICENTER, RANDOMIZED, DOUBLE-BLIND, PLACEBO CONTROLLED STUDY TO EVALUATE THE SAFETY AND EFFICACY OF PF 06939926 FOR THE TREATMENT OF DUCHENNE MUSCULAR DYSTROPHY |
Recruiting |
NCT04281485 |
Phase 3 |
|
33 |
The Efficacy and Safety of Metoprolol as add-on Treatment to Standard of Care in Preventing Cardiomyopathy in Patients With Duchenne Muscular Dystrophy Aged 8-16 Years. A Randomized, Double-blind, Placebo-controlled Study |
Recruiting |
NCT05066633 |
Phase 3 |
Metoprolol Succinate;Placebo |
34 |
Bisoprolol for Early Cardiomyopathy in Duchenne Muscular Dystrophy: a Randomized, Controlled Trial |
Recruiting |
NCT03779646 |
Phase 2, Phase 3 |
Bisoprolol Fumarate |
35 |
A Phase 3, Randomized, Placebo-controlled, Double-blind and Open-label, Extension Study of TAS-205 in Patients With Duchenne Muscular Dystrophy |
Recruiting |
NCT04587908 |
Phase 3 |
TAS-205;Placebo |
36 |
Tadalafil as an Adjuvant to Therapy for Duchenne Muscular Dystrophy |
Recruiting |
NCT05195775 |
Phase 2, Phase 3 |
Tadalafil |
37 |
A Double-Blind, Placebo-Controlled, Multi-Center Study With an Open-Label Extension to Evaluate the Efficacy and Safety of SRP-4045 and SRP-4053 in Patients With Duchenne Muscular Dystrophy |
Recruiting |
NCT02500381 |
Phase 3 |
SRP-4045;SRP-4053;Placebo |
38 |
A Phase 3 Randomized, Double-blind, Placebo-controlled, Multi-center Study to Assess the Efficacy and Safety of Viltolarsen in Ambulant Boys With Duchenne Muscular Dystrophy (DMD) |
Recruiting |
NCT04060199 |
Phase 3 |
Viltolarsen;Placebo |
39 |
A Randomized, Double-Blind, Dose Finding and Comparison Study of the Safety and Efficacy of a High Dose of Eteplirsen, Preceded by an Open-label Dose Escalation, in Patients With Duchenne Muscular Dystrophy With Deletion Mutations Amenable to Exon 51 Skipping |
Recruiting |
NCT03992430 |
Phase 3 |
Eteplirsen |
40 |
A Phase 3, Randomized, Double-Blind, Placebo-Controlled Trial Evaluating the Efficacy and Safety of Human Allogeneic Cardiosphere-Derived Cells for the Treatment of Duchenne Muscular Dystrophy |
Recruiting |
NCT05126758 |
Phase 3 |
Placebo |
41 |
A Phase 3 Global, Randomized, Double-Blind, Placebo-Controlled, 48-Week, Parallel-Group Study of the Efficacy and Safety of Losmapimod in Treating Subjects With Facioscapulohumeral Muscular Dystrophy (FSHD) |
Recruiting |
NCT05397470 |
Phase 3 |
Losmapimod;Placebo oral tablet |
42 |
Tamoxifen in Duchenne Muscular Dystrophy: A Multicenter, Randomised, Double-blind, Placebo-controlled, Phase 3 Safety and Efficacy 48-week Trial |
Active, not recruiting |
NCT03354039 |
Phase 3 |
Tamoxifen;Matching placebo |
43 |
A Phase 3, Randomized, Double-Blind, Trial of Pamrevlumab (FG-3019) or Placebo in Combination With Systemic Corticosteroids in Ambulatory Subjects With Duchenne Muscular Dystrophy (DMD) |
Active, not recruiting |
NCT04632940 |
Phase 3 |
Pamrevlumab;Placebo |
44 |
A Phase 3, Randomized, Double-Blind, Trial of Pamrevlumab (FG-3019) or Placebo in Combination With Systemic Corticosteroids in Subjects With Non-ambulatory Duchenne Muscular Dystrophy (DMD) |
Active, not recruiting |
NCT04371666 |
Phase 3 |
Pamrevlumab;Placebo |
45 |
A Phase 3, Randomized, Double-blind, Placebo-controlled Efficacy and Safety Study of Ataluren in Patients With Nonsense Mutation Duchenne Muscular Dystrophy and Open-Label Extension |
Active, not recruiting |
NCT03179631 |
Phase 3 |
Ataluren;PLACEBO |
46 |
A Phase 3 Multinational, Randomized, Double-Blind, Placebo-Controlled Systemic Gene Delivery Study to Evaluate the Safety and Efficacy of SRP-9001 in Subjects With Duchenne Muscular Dystrophy (EMBARK) |
Active, not recruiting |
NCT05096221 |
Phase 3 |
|
47 |
A Phase 3, Multi-center, Open-label Extension Study to Assess the Safety and Efficacy of Viltolarsen in Ambulant Boys With Duchenne Muscular Dystrophy (DMD) |
Enrolling by invitation |
NCT04768062 |
Phase 3 |
Viltolarsen |
48 |
Long-term, Open-label Extension Study for Patients With Duchenne Muscular Dystrophy Enrolled in Clinical Trials Evaluating Casimersen or Golodirsen |
Enrolling by invitation |
NCT03532542 |
Phase 3 |
Casimersen;Golodirsen |
49 |
Open Label, Long-term Safety, Tolerability, and Efficacy Study of GIVINOSTAT in All DMD Patients Who Have Been Previously Treated in One of the GIVINOSTAT Studies |
Enrolling by invitation |
NCT03373968 |
Phase 2, Phase 3 |
Givinostat |
50 |
An Open-Label, Safety Study for Ataluren (PTC124) Patients With Nonsense Mutation Dystrophinopathy |
Enrolling by invitation |
NCT01247207 |
Phase 3 |
Ataluren |
|