Drugs for Tuberous Sclerosis 2 (from DrugBank, HMDB, Dgidb, PharmGKB, IUPHAR, NovoSeek, BitterDB):
(show top 50)
(show all 71)
# |
|
Name |
Status |
Phase |
Clinical Trials |
Cas Number |
PubChem Id |
1 |
|
Doxycycline |
Approved, Investigational, Vet_approved |
Phase 4 |
|
564-25-0 |
54671203 |
Synonyms:
(4S,4AR,5S,5ar,6R,12as)-4-(dimethylamino)-3,5,10,12,12a-pentahydroxy-6-methyl-1,11-dioxo-1,4,4a,5,5a,6,11,12a-octahydrotetracene-2-carboxamide
5-Hydroxy-a-6-deoxytetracycline
5-Hydroxy-alpha-6-deoxytetracycline
5-Hydroxy-α-6-deoxytetracycline
6a-Deoxy-5-oxytetracycline
6-alpha-deoxy-5-oxytetracycline
6alpha-Deoxy-5-oxytetracycline
6Α-deoxy-5-oxytetracycline
Anhydrous doxycycline
BMY-28689|Monodox®|Vibramycin®
Doxcycline anhydrous
Doxiciclina
DOXY
Doxychel
Doxycyclin
Doxycycline
|
Doxycycline (anhydrous)
DOXYCYCLINE ANHYDROUS
DOXYCYCLINE HCL
Doxycycline hyclate
Doxycycline hydrate
Doxycycline hydric acid
Doxycycline monohydrate
Doxycycline monohydric acid
Doxycyclinum
Doxytetracycline
GS-3065
Jenacyclin
Monodox
Oracea
Supracyclin
Vibramycin
|
|
2 |
|
Cannabidiol |
Approved, Investigational |
Phase 4 |
|
13956-29-1 |
521372 644019 |
Synonyms:
(−)-trans-2-p-mentha-1,8-dien-3-yl-5-pentylresorcinol
(−)-trans-cannabidiol
(1'R,2'R)-5'-methyl-4-pentyl-2'-(prop-1-en-2-yl)-1',2',3',4'-tetrahydrobiphenyl-2,6-diol
BTX-1503
CANNABIDIOL
CBD
CBD|Epidiolex®|GWP42003-P|nabiximols (CBD + THC, fixed-dose oral spray)|Sativex® (CBD + THC, fixed-dose oral spray)
|
EPIDIOLEX
GWP42003
GWP-42003
GWP42003-P
GWP-42003-P
Δ1(2)-trans-cannabidiol
|
|
3 |
|
Vigabatrin |
Approved |
Phase 4 |
|
60643-86-9, 68506-86-5 |
5665 |
Synonyms:
4-Amino-5-hexenoate
4-Amino-5-hexenoic acid
Acid, gamma-vinyl-gamma-aminobutyric
Aventis brand OF vigabatrin
CPP-109
CPP-109|Kigabeq®|MDL-71754|Sabril®
gamma Vinyl gaba
gamma Vinyl gamma aminobutyric acid
gamma-Vinyl gaba
gamma-Vinyl-gaba
gamma-Vinyl-gamma-aminobutyrate
gamma-Vinyl-gamma-aminobutyric acid
GVG
g-Vinyl gaba
g-Vinyl-g-aminobutyrate
g-Vinyl-g-aminobutyric acid
Hoechst brand OF vigabatrin
|
MDL-71754
RMI-71754
Sabril
Sabrilex
VIGABATRIN
Vigabatrin aventis brand
Vigabatrin hoechst brand
Vigabatrin yamanouchi brand
Vigabatrina
Vigabatrine
Vigabatrinum
VINYL GAMMA-AMINOBUTYRIC ACID
Yamanouchi brand OF vigabatrin
Γ-vinyl gaba
Γ-vinyl-γ-aminobutyrate
Γ-vinyl-γ-aminobutyric acid
|
|
4 |
|
Antiprotozoal Agents |
|
Phase 4 |
|
|
|
5 |
|
Antiparasitic Agents |
|
Phase 4 |
|
|
|
6 |
|
Antimalarials |
|
Phase 4 |
|
|
|
7 |
|
Pharmaceutical Solutions |
|
Phase 4 |
|
|
|
8 |
|
Liver Extracts |
|
Phase 4 |
|
|
|
9 |
|
Neurotransmitter Agents |
|
Phase 4 |
|
|
|
10 |
|
Anticonvulsants |
|
Phase 4 |
|
|
|
11 |
|
Ethanol |
Approved |
Phase 3 |
|
64-17-5 |
702 |
Synonyms:
[CH2Me(OH)]
[OEtH]
1-Hydroxyethane
ABLYSINOL
Absolute alcohol
Absolute ethanol
Absolute ethyl alcohol
Aethanol
Aethylalkohol
Alcare hand degermer
Alcohol
Alcohol (ethyl)
Alcohol anhydrous
Alcohol denatured
ALCOHOL DETERMINATION--ALCOHOL
Alcohol etilico
Alcohol etílico
Alcohol, absolute
Alcohol, Dehydrated
Alcohol, denatured
ALCOHOL, DILUTED
Alcohol, ethyl
Alcohol, grain
ALCOHOL, RUBBING
Alcohols
Alcool ethylique
Alcool éthylique
Alcool etilico
Algrain
Alkohol
Alkoholu etylowego
Aminoethanol
Anhydrol
Anhydrous alcohol
Anhydrous ethanol
Äthanol
Äthylalkohol
B3324
Beta-Aminoethanol
Beta-Aminoethyl Alcohol
Beta-Ethanolamine
Beta-Hydroxyethylamine
C2H5OH
Caswell No. 426
Colamine
Cologne spirit
Cologne spirits
Dehydrated alcohol
Dehydrated ethanol
Denatured alcohol
Denatured Alcohol Cd-10
Denatured Alcohol Cd-5
Denatured Alcohol Cd-5a
Denatured Alcohol Sd-1
Denatured Alcohol Sd-13a
Denatured Alcohol Sd-17
Denatured Alcohol Sd-23a
Denatured Alcohol Sd-28
Denatured Alcohol Sd-30
Denatured Alcohol Sd-39b
Denatured Alcohol Sd-39c
Denatured Alcohol Sd-3a
Denatured Alcohol Sd-40m
Denatured ethanol
Desinfektol el
Diluted alcohol
Distilled spirits
DRINKING ALCOHOL
E1510
Envision Conditioner Pdd 9020
ETA
Etanol
|
Etanolo
ETHANOL
éthanol
Ethanol 200 proof
Ethanol Absolute
Ethanol Absolute Bp
Ethanol Anhydrous
Ethanol Extra Pure
Ethanol solution
Ethanol, Silent Spirit
Ethicap
Ethyl alc
Ethyl alcohol
Ethyl Alcohol & Water, 10%
Ethyl Alcohol & Water, 20%
Ethyl Alcohol & Water, 30%
Ethyl Alcohol & Water, 40%
Ethyl Alcohol & Water, 5%
Ethyl Alcohol & Water, 50%
Ethyl Alcohol & Water, 60%
Ethyl Alcohol & Water, 70%
Ethyl Alcohol & Water, 80%
Ethyl Alcohol & Water, 95%
Ethyl Alcohol & Water, 96%
Ethyl alcohol anhydrous
Ethyl alcohol in alcoholic beverages
Ethyl alcohol usp
Ethyl Alcohol, Anhydrous
Ethyl Alcohol, Denatured
Ethyl hydrate
Ethyl hydroxide
Ethylol
Ethylolamine
EtOH
FEMA NO. 2419
Fermentation alcohol
Glycinol
Grain alcohol
Hinetoless
HSDB 531
Hydroxyethane
Infinity pure
Jaysol
Jaysol S
Lux
METHYLATED MINERAL
Methylated Spirit Mineralised
Methylcarbinol
Molasses alcohol
NCI-C03134
NSC-85228
PM-6193-200
Potato alcohol
Punctilious ethyl alcohol
Pyro
Reagent Alcohol
Silent spirit
SPIRIGEL
Spirit
Spirits OF wine
Spiritus vini
Spirt
SURG
Synasol
Tecsol
Tecsol C
Thanol
Thiofaco M-50
Undenatured ethanol
USAF EK-1597
VODKA
|
|
12 |
|
Strawberry |
Approved |
Phase 3 |
|
|
|
13 |
|
Carbamazepine |
Approved, Investigational |
Phase 3 |
|
298-46-4 |
2554 |
Synonyms:
5-Carbamoyl-5H-dibenz(b,F)azepine
5-Carbamoyl-5H-dibenz[b,F]azepine
5-Carbamoyl-5H-dibenzo(b,F)azepine
5-Carbamyl-5H-dibenzo(b,F)azepine
5H-Dibenz(b,F)azepine-5-carboxamide
Amizepine
Apo-Carbamazepine
ARBIL MR
Atretol
Biston
CALEPSIN
calepsin|Carnexiv®|Tegretol®
CARBAGEN SR
Carbamazepen
Carbamazepin
Carbamazepina
Carbamazepine
Carbamazépine
Carbamazepine acetate
Carbamazepine anhydrous
Carbamazepine dihydrate
Carbamazepine hydrochloride
Carbamazepine L-tartrate (4:1)
Carbamazepine phosphate
Carbamazepine sulfate (2:1)
Carbamazepinum
Carbamezepine
CARBATROL
Carbazepin
Carbazepine
Carbelan
Carnexiv
CBZ
EPIMAZ
|
EPIMAZ RET
Epitol
Equetro
Finlepsin
G-32883
GEIGY 32883
Karbamazepin
Lexin
Neurotol
Novo-Carbamaz
NSC-169864
Nu-Carbamazepine
Sirtal
SIRTAL RET
Stazepin
Stazepine
Taro-Carbamazepine
Taro-Carbamazepine Cr
TEG111
Tegretal
Tegretol
TEGRETOL CHEWTAB
Tegretol Chewtabs
Tegretol Cr
TEGRETOL PROLONGED RELEASE
TEGRETOL XR
TEGRETOL-XR
Telesmin
TERIL
TERIL RET
Timonil
TIMONIL 200 RET
TIMONIL 400 RET
|
|
14 |
|
Phenytoin |
Approved, Vet_approved |
Phase 3 |
|
57-41-0 |
1775 |
Synonyms:
5,5-Diphenylhydantoin
5,5-Diphenylimidazolidine-2,4-dione
5,5-Diphenyl-imidazolidine-2,4-dione
5,5-Diphenyltetrahydro-1H-2,4-imidazoledione
5,5-Dwufenylohydantoina
Aleviatin
Antisacer
Auranile
Causoin
Citrullamon
Citrulliamon
Comital
Comitoina
Convul
Danten
Dantinal
Dantoinal
Dantoinal klinos
Dantoine
Denyl
Didan TDC 250
Difenilhidantoina
Difenilhidantoina [Spanish]
Difenin
Difetoin
Difhydan
Dihycon
Dihydan
Di-Hydan
Dihydantoin
DILABID
Di-Lan
DILANTIN
Dilantin acid
Dilantin®|Epanutin®|Phenytex®|phenytoin sodium
DILANTIN-125
DILANTIN-30
Dilantine
Dillantin
Dintoin
Dintoina
Diphantoin
Diphedal
Diphedan
Diphenat
Diphenin
Diphenine
Diphentoin
Diphentyn
Diphenylan
Diphenylan sodium
Diphenylhydantoin
Diphenylhydantoinate, sodium
Diphenylhydantoine [French]
Diphenylhydatanoin
Di-Phetine
Ditoinate
DPH
Ekko
Elepsindon
Enkelfel
Epamin
Epanutin
Epasmir 5
Epdantoin Simple
Epdantoine simple
Epelin
Epifenyl
Epihydan
Epilan
Epilan D
Epilan-D
Epilantin
Epinat
Epised
Eptal
Eptoin
Fenantoin
Fenidantoin s
Fenitoin
Fenitoina
Fenitoina [INN-Spanish]
|
Fentoin
Fenylepsin
Fenytoin Dak
Fenytoine
Gerot-epilan-D
Hidan
Hidantal
Hidantilo
Hidantina
Hidantina senosian
Hidantina vitoria
Hidantomin
Hindatal
Hydantal
Hydantin
Hydantoin
Hydantoinal
Hydantol
Ictalis simple
Idantoil
Idantoin
Iphenylhydantoin
Kessodanten
Labopal
Lehydan
Lepitoin
Lepsin
Mesantoin
Minetoin
Neos-Hidantoina
Neosidantoina
Novantoina
Novophenytoin
NSC-8722
Om hidantoina simple
Om-Hydantoine
Oxylan
Park davis brand OF phenytoin
Pfizer brand OF phenytoin
Phanantin
Phanatine
Phenatine
Phenatoine
Phenhydan
Phenhydanin
Phenitoin
Phentoin
PHENTYTOIN
PHENYTEK
PHENYTEX
Phenytoin
Phenytoin AWD
Phenytoin pfizer brand
Phenytoin phizer brand
Phenytoin sodium
Phenytoine
Phenytoine [INN-French]
Phenytoin-Gerot
Phenytoinum
Phenytoinum [INN-Latin]
Phizer brand OF phenytoin
Prompt Phenytoin Sodium
Ritmenal
Saceril
Sanepil
Silantin
Sinergina
SM-88 COMPONENT PHENYTOIN
Sodanthon
Sodantoin
Sodanton
Sodium diphenylhydantoinate
Solantin
Solantoin
Solantyl
Sylantoic
Tacosal
Thilophenyl
TOIN
Toin unicelles
Zentronal
Zentropil
|
|
15 |
|
Phenobarbital |
Approved, Investigational |
Phase 3 |
|
50-06-6 |
4763 |
Synonyms:
5-Ethyl-5-phenyl-2,4,6(1H,3H,5H)-pyrimidinetrione
5-Ethyl-5-phenylbarbitate
5-Ethyl-5-phenylbarbitic acid
5-Ethyl-5-phenylbarbituric acid
5-Ethyl-5-phenylpyrimidine-2,4,6(1H,3H,5H)-trione
5-Ethyl-5-phenyl-pyrimidine-2,4,6-trione
5-Phenyl-5-ethylbarbitate
5-Phenyl-5-ethylbarbitic acid
5-Phenyl-5-ethylbarbituric acid
Acid, phenylethylbarbituric
Adonal
Aephenal
Agrypnal
Amylofene
Aphenylbarbit
Aphenyletten
Barbenyl
Barbinal
Barbiphen
Barbiphenyl
Barbipil
Barbita
Barbivis
Barbonal
Barbophen
Bardorm
Bartol
Bialminal
Blu-Phen
Cabronal
Calmetten
Calminal
Cardenal
Chinoin
Codibarbita
Coronaletta
Cratecil
Damoral
Dezibarbitur
Dormina
Dormiral
Dormital
Doscalun
Duneryl
Ensobarb
Ensodorm
Epanal
Epidorm
Epilol
Episedal
Epsylone
ESKABARB
Etilfen
Euneryl
Fenbital
Fenemal
Fenobarbital
fenobarbital|Luminal®|phenobarb|phenobarbital sodium|phenobarbitone|phenylethylbarbiturate
Fenosed
Fenylettae
Gardenal
Gardepanyl
Glysoletten
Haplopan
Haplos
Helional
Hennoletten
Henotal
Hypnaletten
Hypnette
Hypnogen
Hypnolone
Hypnoltol
Hypno-Tablinetten
Hysteps
Lefebar
Leonal
Lephebar
Lepinal
Lepinaletten
Linasen
Liquital
Lixophen
Lubergal
Lubrokal
Lumen
Lumesettes
|
Lumesyn
Luminal
Lumofridetten
Luphenil
Luramin
Molinal
Monosodium salt phenobarbital
Neurobarb
Nirvonal
NOPTIL
Nova-Pheno
NSC-128143
NSC-128143-
NSC-9848
Nunol
Parkotal
Pharmetten
Phenaemal
Phen-Bar
Phenemal
Phenemalum
Phenobal
PHENOBARBITAL
PHENOBARBITAL CIV
Phenobarbital sodium
Phenobarbital, monosodium salt
Phenobarbitate
Phenobarbitic acid
Phenobarbitol
Phenobarbitone
Phenobarbituric acid
Phenobarbyl
Phenoluric
Phenolurio
Phenomet
Phenonyl
Phenoturic
Phenylaethylbarbitursaeure
Phenyläthylbarbitursäure
Phenylbarbital
Phenylethylbarbitate
Phenylethylbarbitic acid
Phenylethylbarbiturate
Phenylethylbarbituric acid
Phenylethylbarbitursaeure
Phenylethylbarbitursäure
PHENYLETHYLMALONYLUREA
Phenyletten
Phenyral
Phob
Polcominal
Promptonal
Sedabar
Seda-Tablinen
Sedicat
Sedizorin
Sedlyn
Sedofen
Sedonal
Sedonettes
Sevenal
Sinoratox
Sodium, phenobarbital
SOLFOTON
Solfoton Talpheno
Solu-Barb
Sombutol
Somnolens
Somnoletten
Somnosan
Somonal
Spasepilin
Starifen
Starilettae
Stental
Stental Extentabs
TALPHENO
Teolaxin
Teoloxin
Thenobarbital
Theoloxin
Triabarb
Tridezibarbitur
Triphenatol
Versomnal
Zadoletten
Zadonal
|
|
16 |
|
Zonisamide |
Approved, Investigational |
Phase 3 |
|
68291-97-4 |
5734 |
Synonyms:
1,2-Benzisoxazole-3-methanesulfonamide
1,2-Benzisoxazole-3-methanesulphonamide
3 Sulfamoylmethyl 1,2 benzisoxazole
3-(Sulfamoylmethyl)-1,2-benzisoxazole
3-(Sulphamoylmethyl)-1,2-benzisoxazole
3-Sulfamoylmethyl-1,2-benzisoxazole
AD-810
AD-810|CI-912|PD-110843|Zonegran®
Benzo[D]isoxazol-3-yl-methanesulfonamide
Benzo[D]isoxazol-3-yl-methanesulphonamide
CI-912
Elan brand OF zonisamide
|
Exceglan
Excegram
Excegran
PD-110843
Zonegran
Zonisamida
Zonisamida [Spanish]
Zonisamide
Zonisamide monosodium
Zonisamidum
Zonisamidum [Latin]
|
|
17 |
|
Clonazepam |
Approved, Illicit |
Phase 3 |
|
1622-61-3 |
2802 |
Synonyms:
1,3-Dihydro-7-nitro-5-(2-chlorophenyl)-2H-1,4.benzodiazepin-2-one
5-(2-Chloro-phenyl)-7-nitro-1,3-dihydro-benzo[e][1,4]diazepin-2-one
5-(2-Chlorophenyl)-7-nitro-1H-benzo[e][1,4]diazepin-2(3H)-one
5-(O-Chlorophenyl)-7-nitro-1,3-dihydro-2H-1,4-benzodiazepin-2-one
Antelepsin
Chlonazepam
CLONAZEPAM
CLONAZEPAM CIV
Clonazepam fine granules
Clonazepam tablets
|
Clonazepamum
Klonopin
KLONOPIN RAPIDLY DISINTEGRATING
Klonopin®|Ro-5-4023|Ro-54023
NSC-179913
Rivotril
RO-54023
RO-5-4023
RO-5423
|
|
18 |
|
Clobazam |
Approved, Illicit |
Phase 3 |
|
22316-47-8 |
2789 |
Synonyms:
1-Phenyl-5-methyl-8-chloro-1,2,4,5- tetrahydro-2,4-diketo-3H-1,5-benzodiazepine
1-Phenyl-5-methyl-8-chloro-1,2,4,5-tetrahydro-2,4-dioxo-3H-1,5-benzodiazepine
7-Chloro-1-methyl-5-phenyl-1,5-dihydro-benzo[b][1,4]diazepine-2,4-dione
Chlorepin
CLOBAZAM
Clobazamum
Clorepin
Frisium
H-4723
HR-376
|
LM-2717
Mystan
NSC-336279
Onfi
PERIZAM
SYMPAZAN
TAPCLOB
Urbadan
URBANOL
Urbanyl
|
|
19 |
|
Topiramate |
Approved |
Phase 3 |
|
97240-79-4 |
5284627 |
Synonyms:
[(1R,2S,6S,9R)-4,4,11,11-TETRAMETHYL-3,5,7,10,12-PENTAOXATRICYCLO[7.3.0.0^{2,6}]DODECAN-6-YL]METHYL SULFAMATE
2,3:4,5-Bis-O-(1-methylethylidene)-b-D-fructopyranose sulfamate
2,3:4,5-Bis-O-(1-methylethylidene)-b-D-fructopyranose sulfamic acid
2,3:4,5-Bis-O-(1-methylethylidene)-b-D-fructopyranose sulphamate
2,3:4,5-Bis-O-(1-methylethylidene)-b-D-fructopyranose sulphamic acid
2,3:4,5-Bis-O-(1-methylethylidene)-beta-D-fructopyranose sulfamate
2,3:4,5-Bis-O-(1-methylethylidene)-beta-D-fructopyranose sulfamic acid
2,3:4,5-Bis-O-(1-methylethylidene)-beta-D-fructopyranose sulphamate
2,3:4,5-Bis-O-(1-methylethylidene)-beta-D-fructopyranose sulphamic acid
2,3:4,5-Bis-O-(1-methylethylidene)-β-D-fructopyranose sulfamate
2,3:4,5-Bis-O-(1-methylethylidene)-β-D-fructopyranose sulfamic acid
2,3:4,5-Bis-O-(1-methylethylidene)-β-D-fructopyranose sulphamate
2,3:4,5-Bis-O-(1-methylethylidene)-β-D-fructopyranose sulphamic acid
2,3:4,5-Di-O-isopropylidene-b-D-fructopyranose sulfamate
2,3:4,5-Di-O-isopropylidene-b-D-fructopyranose sulfamic acid
2,3:4,5-Di-O-isopropylidene-b-D-fructopyranose sulphamate
2,3:4,5-Di-O-isopropylidene-b-D-fructopyranose sulphamic acid
2,3:4,5-Di-O-isopropylidene-beta-D-fructopyranose sulfamate
2,3:4,5-Di-O-isopropylidene-beta-D-fructopyranose sulfamic acid
2,3:4,5-Di-O-isopropylidene-beta-D-fructopyranose sulphamate
2,3:4,5-Di-O-isopropylidene-beta-D-fructopyranose sulphamic acid
2,3:4,5-Di-O-isopropylidene-β-D-fructopyranose sulfamate
2,3:4,5-Di-O-isopropylidene-β-D-fructopyranose sulfamic acid
2,3:4,5-Di-O-isopropylidene-β-D-fructopyranose sulphamate
2,3:4,5-Di-O-isopropylidene-β-D-fructopyranose sulphamic acid
2,3-4,5-Bis-O-(1-methylethylidene)-beta-D-fructopyranose sulfamate
|
Epitomax
epitomax|Eprontia® (liquid formulation)|MCN-4853|RWJ-17021|Topamax®
MCN-4853
QUDEXY XR
RWJ-17021
RWJ-17021-000
Tipiramate
Tipiramate [French]
Tipiramato
Tipiramato [Spanish]
Tipiramic acid
Topamax
Topamax sprinkle
TOPIRAMATE
topiramate tablet
Topiramato
Topiramato [INN-Spanish]
Topiramatum
Topiramatum [INN-Latin]
Topiramic acid
Topomax
TPM
Trokendi XR
USL255
USL-255
|
|
20 |
|
Ganaxolone |
Approved, Investigational |
Phase 3 |
|
38398-32-2 |
22023730 6918305 |
Synonyms:
CCD-1042
CCD-1042|CCD1042|Ztalmy®
|
|
|
21 |
|
Sirolimus |
Approved, Investigational |
Phase 3 |
|
53123-88-9 |
5284616 6436030 |
Synonyms:
(-)-Rapamycin
(1R,9S,12S,15R,16E,18R,19R,21R,23S,24E,26E,28E,30S,32S,35R)-1,18-Dihydroxy-12-{(2S)-1-[(1S,3R,4R)-4-hydroxy-3-methoxycyclohexyl]propan-2-yl}-19,30-dimethoxy-15,17,21,23,29,35-hexamethyl-11,36-dioxa-4-azatricyclo[30.3.1.0(4,9)]hexatriaconta-16,24,26,28-tetraene-2,3,10,14,20-pentone
Antibiotic ay 22989
AY-22989
AY-22989|Fyarro® (sirolimus albumin-bound particles)|Rapamune®|rapamycin|WY-090217
L04AA10
NSC-226080
Perceiva
RAPA
Rapammune
|
Rapamune
Rapamycin
Rapamysin
RPM
Sirolimus
Sirolimús
Sirolimusum
SM-88 COMPONENT SIROLIMUS
WY-090217
|
|
22 |
|
Miconazole |
Approved, Investigational, Vet_approved |
Phase 3 |
|
22916-47-8 |
4189 |
Synonyms:
1-(2,4-Dichloro-beta-((2,4-dichlorobenzyl)oxy)phenethyl)imidazole
1-[2-(2,4-Dichloro-benzyloxy)-2-(2,4-dichloro-phenyl)-ethyl]-1H-imidazole
Brentan
CONOFITE
Dactarin
DERMAZOLE
DUMICOAT
Esteve brand OF miconazole
florid(nitrate)|Monistat®|R-14889
Janssen cilag brand OF miconazole
Janssen-cilag brand OF miconazole
Johnston and johnston brand OF miconazole nitrate
LORAMYC
MCZ
MICATIN
|
Miconasil nitrate
Miconazol
Miconazole
Miconazole esteve brand
Miconazole janssen-cilag brand
Miconazole nitrate
Miconazolum
Monistat
MONISTAT-3
MONISTAT-DERM
Nitrate, miconasil
Nitrate, miconazole
NSC-170986
Oravig
VUSION
|
|
23 |
|
Clotrimazole |
Approved, Vet_approved |
Phase 3 |
|
23593-75-1 |
2812 |
Synonyms:
(Chlorotrityl)imidazole
1-((2-Chlorophenyl)diphenylmethyl)-1H-imidazole
1-(a-(2-Chlorophenyl)benzhydryl)imidazole
1-(alpha-(2-Chlorophenyl)benzhydryl)imidazole
1-(O-Chloro-a,a-diphenylbenzyl)imidazole
1-(O-Chloro-alpha,alpha-diphenylbenzyl)imidazole
1-(O-Chlorotrityl)imidazole
1-(O-Chloro-α,α-diphenylbenzyl)imidazole
1-(Α-(2-chlorophenyl)benzhydryl)imidazole
ABTRIM
ACTAVALL
Bay b 5097
BAY-5097
Bayer brand 1 OF clotrimazole
Bayer brand 2 OF clotrimazole
CANDIDEN
Canesten
Canesten 1-day cream combi-pak
Canesten 1-day therapy
Canesten 3-day therapy
Canesten 6-day therapy
CANESTEN AF
Canesten combi-pak 1-day therapy
Canesten combi-pak 3-day therapy
Canesten cream
CANESTEN CRM COMBI
CANESTEN INTERNAL
Canesten solution
CANESTEN VC
Canesten®|Lotrimin®
Canestine
Chlotrimazole
Clotrimaderm
Clotrimaderm cream
Clotrimazol
CLOTRIMAZOLE
Clotrimazole schering brand
Clotrimazolum
Desamix F
Empecid
FB b 5097
Fem care
FemCare
FUNGEDERM
GNF-PF-3499
Gyne lotrimin
Gyne-lotrimin
Gyne-lotrimin 3
Gyne-lotrimin 3 combination pack
Gyne-lotrimin combination pack
Gyne-lotrimin3
Gyne-lotrimin3 combination pack
|
Gynix
Kanesten
Klotrimazole
Lopac-C-6019
Lotrimax
Lotrimin
LOTRIMIN (TN)
Lotrimin af
Lotrimin af cream
Lotrimin af jock-itch cream
Lotrimin af lotion
Lotrimin af solution
Lotrimin cream
Lotrimin lotion
Lotrimin solution
Lotrisone
MASNODERM
mono-Baycuten
Monobaycuten
Mycelax
Mycelex
MYCELEX (TN)
Mycelex 7
Mycelex cream
Mycelex g
Mycelex otc
Mycelex solution
Mycelex troches
Mycelex twin pack
Mycelex: mycosporinrimazole
Mycelex-7
Mycelex-7 combination pack
Mycelex-g
MYCIL GOLD
Myclo cream
Myclo solution
Myclo spray solution
Myclo-gyne
Mycosporin
Mykosporin
Neo-zol cream
NSC-257473
Otomax
Pedisafe
Prestwick_120
PRIVACOM
Rimazole
Schering brand OF clotrimazole
Tibatin
Trimysten
Trivagizole 3
Veltrim
|
|
24 |
|
Calcitriol |
Approved, Nutraceutical |
Phase 3 |
|
32222-06-3 |
5280453 |
Synonyms:
(1a,3b,5Z,7E)-9,10-Secocholesta-5,7,10(19)-triene-1,3,25-triol
(1alpha,3beta,5Z,7E)-9,10-Secocholesta-5,7,10(19)-triene-1,3,25-triol
(1R,3S,5Z)-5-{2-[(1R,3AS,4E,7AR)-1-[(2R)-6-HYDROXY-6-METHYLHEPTAN-2-YL]-7A-METHYL-OCTAHYDRO-1H-INDEN-4-YLIDENE]ETHYLIDENE}-4-METHYLIDENECYCLOHEXANE-1,3-DIOL
(1S,3R,5Z,7E)-9,10-Seco-5,7,10(19)-cholestatriene-1,3,25-triol
(1S,3R,5Z,7E)-9,10-Secocholesta-5,7,10-triene-1,3,25-triol
(1Α,3β,5Z,7E)-9,10-secocholesta-5,7,10(19)-triene-1,3,25-triol
(3b,5Z,7E)-9,10-Secocholesta-5,7,10(19)-trienetriol
(5Z,7E)-(1S,3R)-9,10-Secocholesta-5,7,10(19)-triene-1,3,25-triol
1 alpha, 25 Dihydroxy 20 epi vitamin D3
1 alpha, 25-Dihydroxy-20-epi-vitamin D3
1 alpha,25 Dihydroxycholecalciferol
1 alpha,25 Dihydroxyvitamin D3
1 alpha,25-Dihydroxycholecalciferol
1 alpha,25-Dihydroxyvitamin D3
1,25 Dihydroxy 20 epi vitamin D3
1,25 Dihydroxycholecalciferol
1,25 Dihydroxyvitamin D3
1,25(OH)2-20EPi-D3
1,25-DHCC
1,25-Dihydroxy-20-epi-vitamin D3
1,25-Dihydroxycholecalciferol
1,25-Dihydroxyvitamin D
1,25-Dihydroxyvitamin D3
1a,25(OH)2D3
1a,25-(OH)2D3
1a,25-Dihydroxycholecalciferol
1a,25-Dihydroxyvitamin D3
1a,25-Dihydroxyvitamin D3 / 1a,25-dihydroxycholecalciferol / calcitriol
1-a-25-Dihydroxyvitamin D3
1alpha,25(OH)2D3
1alpha,25-Dihydroxycholecalciferol
1alpha,25-Dihydroxyvitamin D3
1-alpha,25-Dihydroxyvitamin D3
1-alpha-25-Dihydroxyvitamin D3
1Α,25(OH)2D3
1Α,25-dihydroxycholecalciferol
1Α,25-dihydroxyvitamin D3
1Α,25-dihydroxyvitamin D3 / 1α,25-dihydroxycholecalciferol / calcitriol
1-Α-25-dihydroxyvitamin D3
20 Epi 1alpha,25 dihydroxycholecaliferol
20-Epi-1alpha,25-dihydroxycholecaliferol
25-Dihydroxycholecalciferol
5-{2-[1-(5-hydroxy-1,5-dimethyl-hexyl)-7a-methyl-octahydro-inden-4-ylidene]-ethylidene}-4-methylene-cyclohexane-1,3-diol
Abbott brand OF calcitriol
alpha,25-Dihydroxyvitamin D3, 1
Alphapharm brand OF calcitriol
Bocatriol
Calcijex
Calcijex®|calcitriol|Rocaltrol®
|
Calcitriol
Calcitriol abbott brand
Calcitriol alphapharm brand
Calcitriol cryopharma brand
Calcitriol galderma brand
Calcitriol gry brand
Calcitriol jenapharm brand
Calcitriol kyramed
Calcitriol kyramed brand
Calcitriol leo brand
Calcitriol medice brand
Calcitriol nefro
Calcitriol renacare brand
Calcitriol roche brand
Calcitriol-nefro
CalcitriolNefro
Calcitriolum
Cryopharma brand OF calcitriol
D3, 1 alpha,25-Dihydroxyvitamin
D3, 1,25-Dihydroxy-20-epi-vitamin
D3, 1,25-Dihydroxyvitamin
Decostriol
DIHYDROXYCHOLECALCIFEROL
DIHYDROXYVITAMIN D 3
Dihydroxyvitamin D3
Galderma brand OF calcitriol
Gry brand OF calcitriol
Hoffmann la roche brand OF calcitriol
Hoffmann-la roche brand OF calcitriol
Jenapharm brand OF calcitriol
KyraMed brand OF calcitriol
KyraMed, calcitriol
Leo brand OF calcitriol
Medice brand OF calcitriol
Osteotriol
RenaCare brand OF calcitriol
Renatriol
Ro 21-5535
RO-215535
RO-21-5535
Rocaltrol
Roche brand OF calcitriol
Silkis
Sitriol
Soltriol
Tirocal
Topitriol
Toptriol
VECTICAL
|
|
25 |
|
Vitamins |
|
Phase 3 |
|
|
|
26 |
|
Hormones |
|
Phase 3 |
|
|
|
27 |
|
Trace Elements |
|
Phase 3 |
|
|
|
28 |
|
Vasoconstrictor Agents |
|
Phase 3 |
|
|
|
29 |
|
Calcium, Dietary |
|
Phase 3 |
|
|
|
30 |
|
Micronutrients |
|
Phase 3 |
|
|
|
31 |
|
Neurosteroids |
|
Phase 3 |
|
|
|
32 |
|
GABA Modulators |
|
Phase 3 |
|
|
|
33 |
|
Antifungal Agents |
|
Phase 3 |
|
|
|
34 |
|
Antibiotics, Antitubercular |
|
Phase 3 |
|
|
|
35 |
|
Calcium |
Nutraceutical |
Phase 3 |
|
7440-70-2 |
271 |
Synonyms:
Ca
Ca(2+)
Ca2+
Calcio
CALCIUM
Calcium element
|
CALCIUM ion
Calcium(2+)
Calcium, doubly charged positive ion
Calcium, elemental
Elemental calcium
Kalzium
|
|
36 |
|
Acetylsalicylic acid |
Approved, Vet_approved |
Phase 2 |
|
50-78-2 |
2244 |
Synonyms:
2-(ACETYLOXY)BENZOATE
2-(ACETYLOXY)benzoIC ACID
2-Acetoxybenzenecarboxylate
2-ACETOXYBENZENECARBOXYLIC ACID
2-ACETOXYBENZOATE
2-ACETOXYBENZOIC ACID
2-CARBOXYPHENYL ACETATE
8-HOUR BAYER
A.S.A.
A.S.A. Empirin
ACARD
ACENTERINE
Acesal
Acetal
ACETARD
ACETICYL
Acetilsalicilico
Acetilum acidulatum
Acetisal
ACETOL
ACETONYL
ACETOPHEN
Acetophen®|acetylsalicylic acid|Aspirin®
ACETOSAL
ACETOSALIC ACID
ACETOSALIN
Acetoxybenzoic acid
ACETYLIN
Acetylsal
ACETYLSALIC ACID
ACETYLSALICYLATE
ACETYLSALICYLIC ACID
Acetylsalicylsaeure
Acetylsalicylsaure
ACETYLSALICYLSÄURE
ACETYONYL
ACETYSAL
ACETYSALICYLIC ACID
Acid, acetylsalicylic
Acide 2-(acetyloxy)benzoique
ACIDE 2-(ACÉTYLOXY)BENZOÏQUE
Acide acetylsalicylique
ACIDE ACÉTYLSALICYLIQUE
Acido acetilsalicilico
ÁCIDO ACETILSALICÍLICO
Acido O-acetil-benzoico
ACIDUM ACETYLSALICYLICUM
Acimetten
Acisal
ACYLPYRIN
Adiro
ALKA RAPID
Aloxiprimum
ANADIN ALL NIGHT
ANGETTES 75
ASA
Asagran
ASATARD
Ascoden-30
Aspalon
Aspec
ASPERGUM
ASPIRDROPS
ASPIRIN
Aspirina
Aspirine
Aspro
ASPRO CLR
Asteric
Azetylsalizylsaeure
AZETYLSALIZYLSÄURE
BAY1019036
BAYER EXTRA STRENGTH
Bayer Extra Strength Aspirin For Migraine Pain
BENASPIR
Bialpirina
BIALPIRINIA
Bi-prin
BUFFERIN
CAPRIN
CARDIOASPIRINA
Cemirit
Claradin
Clariprin
Colfarit
Contrheuma retard
Coricidin
Crystar
DANAMEP
Decaten
Delgesic
Dispril
DISPRIN CV
|
DISPRIN DIRECT
Dolean pH 8
Duramax
DURLAZA
EASPRIN
ECM
ECOLEN
ECOTRIN
EMPIRIN
ENDOSPRIN
ENDYDOL
ENPRIN
Entericin
Enterophen
Enterosarein
Enterosarine
Entrophen
EQUI-PRIN
Extren
GENCARDIA
Globentyl
Globoid
Helicon
Idragin
Kyselina 2-acetoxybenzoova
Kyselina acetylsalicylova
LEVIUS
Magnecyl
MAX STRGH ASPRO CLR
MEASURIN
Micristin
MICROPIRIN EC
Neuronika
Novid
NSC-27223
NSC-406186
Nu-seals
NU-SEALS 300
NU-SEALS 600
NU-SEALS 75
Nu-seals aspirin
NU-SEALS CARDIO 75
O-(ACETYLOXY)BENZOATE
O-(ACETYLOXY)BENZOIC ACID
O-accetylsalicylic acid
O-ACETOXYBENZOATE
O-ACETOXYBENZOIC ACID
O-Acetylsalicylate
O-ACETYLSALICYLIC ACID
O-CARBOXYPHENYL ACETATE
O-Carboxyphenyl acetic acid
PAYNOCIL
PERSISTIN
PHARMACIN
Pirseal
PLATET
PLATET 300
Polopirin
POLOPIRYNA
POSTMI 300
POSTMI 75
PREMASPIN
RHEUMINTABLETTEN
RHODINE
Rhonal
Salacetin
SALCETOGEN
SALETIN
Salicylate acetate
SALICYLIC ACID ACETATE
Salicylic acid acetic acid
Salicylic acid, acetate
SALOSPIR
Solfrin
SOLPRIN
SOLPRIN ACID
SOLPYRON
Solupsan
Spira-Dine
St. Joseph
St. Joseph Aspirin for Adults
Supac
TASPRIN
TEMPERAL
TOLDEX
TRIAMINICIN
Triple-sal
Vanquish
VAZALORE
Xaxa
Yasta
Zorprin
|
|
37 |
|
Propranolol |
Approved, Investigational |
Phase 2 |
|
318-98-9, 525-66-6 |
62882 4946 |
Synonyms:
(+-)-1-(ISOPROPYLAMINO)-3-(1-NAPHTHYLOXY)-2-PROPANOL HYDROCHLORIDE
1-((1-Methylethyl)amino)-3-(1-naphthalenyloxy)-2-propanol
1-(1-NAPHTHYLOXY)-2-HYDROXY-3-ISOPROPYLAMINOPROPANE HYDROCHLORIDE
1-(ISOPROPYLAMINO)-3-(1-NAPHTHOXY)-PROPAN-2-OL HYDROCHLORIDE
1-(ISOPROPYLAMINO)-3-(1-NAPHTHYLOXY)-2-PROPANOL HYDROCHLORIDE
1-(Isopropylamino)-3-(1-naphthyloxy)propan-2-ol
1-ISOPROPYLAMINO-3-(1-NAPHTHOXY)-PROPAN-2-OL-HYDROCHLORIDE
Anaprilin
Anapriline
ANGILOL
APSOLOL
Avlocardyl
AY-64043
AY-64043-
BEDRANOL
BEDRANOL S.R.
Bedranol®|Hemangiol®|Inderal®|propranolol hydrochloride
Beprane
BERKOLOL
Betachron
Betadren
BETADUR CR
Betalong
Beta-Neg
BETA-PROGRANE MR
beta-Propranolol
Beta-Tablinen
Beta-Timelets
b-Propranolol
CARDINOL
Caridolol
Corpendol
Deralin
Dexpropranolol
Dl-Propranolol Hydrochloride
Dociton
DUPROMEX
Duranol
Efektolol
Elbrol
Etalong
Euprovasin
Frekven
HALF BETA-PROGRANE MR
HALF PROPANIX LA
HALF PROPATARD LA
HALF-BEPRANE CR
HALF-BETADUR CR
HALF-INDERAL LA
HEMANGEOL
Hydrochloride, propranolol
ICI-45520
Inderal
INDERAL LA
|
Inderide
INDERIDE-40/25
INDERIDE-80/25
Indobloc
INNOPRAN
INNOPRAN XL
Intermigran
Kemi S
LEDERPRONOL
LOPRANOL LA
Migrastat
NSC-91523
Obsidan
Obzidan
Oposim
Prano-Puren
PROBETA LA
Propanalol
Propanix
PROPANIX LA
PROPANIX-10
PROPANIX-160
PROPANIX-160 SR
PROPANIX-40
PROPANIX-80
Propanolol
PROPATARD LA
Prophylux
Propranalol
PROPRANOLOL
PROPRANOLOL HCL
Propranolol Hcl Intensol
Propranolol hydrochloride
PROPRANOLOL HYDROCHLORIDE INTENSOL
Propranololo
Propranololum
Propranur
Proprasylyt
Pylapron
R,S-Propranolol Hydrochloride
RAPRANOL SR
Rapynogen
Reducor
Reducor Line
Rexigen
SAGITTOL
Servanolol
SLO-BLOK
SLO-PRO
SLOPROLOL
Sumial
SYPROL
TESNOL
Î’-propranolol
|
|
38 |
|
Simvastatin |
Approved |
Phase 1, Phase 2 |
|
79902-63-9 |
54454 |
Synonyms:
(+)-Simvastatin
(1S,3R,7S,8S,8AR)-8-{2-[(2R,4R)-4-HYDROXY-6-OXOOXAN-2-YL]ETHYL}-3,7-DIMETHYL-1,2,3,7,8,8A-HEXAHYDRONAPHTHALEN-1-YL 2,2-DIMETHYLBUTANOATE
2,2-Dimethylbutyrate, 8-ester with (4R,6R)-6-(2-((1S,2S,6R,8S,8ar)-1,2,6,7,8,8a-hexahydro-8-hydroxy-2,6-dimethyl-1-naphthyl)ethyl)tetrahydro-4-hydroxy-2H-pyran-2-one
2,2-Dimethylbutyric acid, 8-ester with (4R,6R)-6-(2-((1S,2S,6R,8S,8ar)-1,2,6,7,8,8a-hexahydro-8-hydroxy-2,6-dimethyl-1-naphthyl)ethyl)tetrahydro-4-hydroxy-2H-pyran-2-one
C10AA01
Cholestat
Coledis
Colemin
Corolin
Denan
Eucor
FLOLIPID
Kolestevan
Labistatin
LACERSA
Lipex
Lipinorm
Liponorm
Lipovas
Lodales
Medipo
MK-0733
MK-733
MK-733|Zocor®
Modutrol
Nivelipol
Nor-vastina
Pantok
Pepstatin
RANZOLONT
|
Rechol
Rendapid
Simcor
Simovil
SIMVADOR
SIMVASTATIN
Simvastatin [Usan:Ban:Inn]
SIMVASTATIN HYDROXY ACID
Simvastatin lactone
Simvastatina
Simvastatina [Spanish]
Simvastatine
Simvastatine [French]
Simvastatinum
Simvastatinum [Latin]
Simvotin
Sinvacor
Sinvascor
SIV691
Sivastin
Statin
Synvinolin
Valemia
Vasotenal
Velostatin
Vytorin
Zocor
ZOCOR HEART-PRO
Zocord
|
|
39 |
|
Benzocaine |
Approved, Investigational |
Phase 2 |
|
1994-09-7, 94-09-7 |
2337 |
Synonyms:
(P-(Ethoxycarbonyl)phenylamine
4-(Ethoxycarbonyl)aniline
4-(Ethoxycarbonyl)phenylamine
4-Aminobenzoate
4-Aminobenzoate ethyl ester
4-Aminobenzoic acid
4-Aminobenzoic acid ethyl ester
4-Carbethoxyaniline
Acetate, benzocaine
Aethoform
AEZODENT
Amben ethyl ester
Americaine
Anaesthan-syngala
Anaesthesin
Anaesthin
Anestezin
Anesthesin
Anesthesine
Anesthone
ANTHISAN PLUS
AR01
AR-01
Baby anbesol
Bensokain
Benzoak
Benzocaina
BENZOCAINE
Benzocaine acetate
Benzocaine formate
Benzocaine hydrobromide
Benzocaine hydrochloride
Benzocaine methanesulfonate
Benzocainum
BURNEZE
CHILDREN'S CHLORASEPTIC
DEQUACAINE
Dermoplast
Diet ayds
Ethoform
Ethyl 4-aminobenzoate
|
Ethyl 4-aminobenzoic acid
Ethyl aminobenzoate
Ethyl aminobenzoic acid
Ethyl P-aminobenzenecarboxylate
Ethyl p-aminobenzoate
Ethyl p-aminobenzoic acid
Ethyl p-aminophenylcarboxylate
Ethyl p-aminophenylcarboxylic acid
Ethylester kyseliny P-aminobenzoove
Formate, benzocaine
Hurricaine
Hydrobromide, benzocaine
Hydrochloride, benzocaine
Identhesin
Keloform
LANACANE
MEDILAVE
Methanesulfonate, benzocaine
NESTOSYL
Norcain
Norcaine
NSC-41531
NSC-4688
Orabase-b
Ora-jel
ORAJEL
Orthesin
p-(Ethoxycarbonyl)aniline
P-Aminobenzoate
P-Aminobenzoic acid
P-Aminobenzoic acid ethyl ester
Parathesin
Parathesine
p-Carbethoxyaniline
p-Ethoxycarboxylic aniline
Slim mint gum
Solarcaine
Solu H
Topcaine
TYROSOLVEN
TYROZETS
|
|
40 |
|
Tannic acid |
Approved |
Phase 2 |
|
1401-55-4 |
16129878 16129778 |
Synonyms:
Acid, tannic
ácido tánico
Acids, tannic
E181
FEMA NO. 3042
Gallotannic acid
|
Gallotannin
NSC-656273
TANNIC ACID
Tannic acids
Tannins
|
|
41 |
|
Coal tar |
Approved |
Phase 1, Phase 2 |
|
8007-45-2 |
|
Synonyms:
|
42 |
|
Analgesics |
|
Phase 2 |
|
|
|
43 |
|
Antirheumatic Agents |
|
Phase 2 |
|
|
|
44 |
|
Fibrinolytic Agents |
|
Phase 2 |
|
|
|
45 |
|
Antipyretics |
|
Phase 2 |
|
|
|
46 |
|
Cyclooxygenase Inhibitors |
|
Phase 2 |
|
|
|
47 |
|
Platelet Aggregation Inhibitors |
|
Phase 2 |
|
|
|
48 |
|
Anti-Inflammatory Agents, Non-Steroidal |
|
Phase 2 |
|
|
|
49 |
|
Analgesics, Non-Narcotic |
|
Phase 2 |
|
|
|
50 |
|
Anti-Inflammatory Agents |
|
Phase 2 |
|
|
|
Interventional clinical trials:
(show top 50)
(show all 84)
# |
Name |
Status |
NCT ID |
Phase |
Drugs |
1 |
Phase IV, Single Arm Study of Safety and Efficacy of Everolimus in Chinese Adults With Tuberous Sclerosis Complex Who Have Renal Angiomyolipoma Not Requiring Immediate Surgery |
Completed |
NCT03525834 |
Phase 4 |
Everolimus |
2 |
CLINICAL TRIAL TO DETERMINE THE EFFICACY AND SAFETY OF RAPAMYCIN IN ANGIOMYOLIPOMAS IN PATIENTS WITH TUBEROUS SCLEROSIS |
Completed |
NCT01217125 |
Phase 4 |
Sirolimus |
3 |
A Randomised, Double Blind, Placebo Controlled Trial of Doxycycline in Lymphangioleiomyomatosis. |
Completed |
NCT00989742 |
Phase 4 |
Doxycycline;Placebo |
4 |
A Long-term Safety Study to Assess the Potential for Chronic Liver Injury in Participants Treated With Epidiolex (Cannabidiol) Oral Solution |
Recruiting |
NCT05044819 |
Phase 4 |
Cannabidiol |
5 |
Phase IV, Prospective Single Arm Study of Safety and Efficacy of Votubia (Everolimus) in Taiwanese Adults With Tuberous Sclerosis Complex Who Have Renal Angiomyolipoma |
Not yet recruiting |
NCT05252585 |
Phase 4 |
Everolimus |
6 |
Sabril for Treatment of Adult Refractory Partial Seizures Symptomatic of Tuberous Sclerosis: An Open Label, Phase IV Prospective Safety and Tolerability Study |
Terminated |
NCT01266291 |
Phase 4 |
vigabatrin |
7 |
Efficacy of RAD001/Everolimus in Autism and NeuroPsychological Deficits in Children With Tuberous Sclerosis Complex |
Unknown status |
NCT01730209 |
Phase 2, Phase 3 |
Everolimus;Placebo |
8 |
A Double-blind, Randomized, Placebo-controlled Phase III Trial to Investigate the Efficacy and Safety of NPC-12G Gel (Topical Formulation of Sirolimus) to Angiofibroma and Other Skin Lesions in Patients With Tuberous Sclerosis Complex |
Completed |
NCT02635789 |
Phase 3 |
NPC-12G gel;Placebo gel |
9 |
A Phase 2/3, Multi-Center, Double-Blind, Placebo-Controlled, Randomized, Parallel-Group, Dose-Response Comparison of the Efficacy and Safety of a Topical Rapamycin Cream for the Treatment of Facial Angiofibromas (FA) Associated With Tuberous Sclerosis Complex (TSC) in Patients 6 Years of Age and Over |
Completed |
NCT03826628 |
Phase 2, Phase 3 |
rapamycin;placebo |
10 |
A Randomized, Double-blind, Placebo-controlled Study of Everolimus in the Treatment of Patients With Subependymal Giant Cell Astrocytomas (SEGA) Associated With Tuberous Sclerosis Complex (TSC) |
Completed |
NCT00789828 |
Phase 3 |
Everolimus;Placebo |
11 |
A Long-term, Single-arm, Open-label Trial of NPC-12G (Topical Formulation of Sirolimus) to Angiofibroma and Other Skin Lesions in Patients With Tuberous Sclerosis Complex |
Completed |
NCT02634931 |
Phase 3 |
NPC-12G gel |
12 |
A Randomized, Double-blind, Placebo-controlled Study of RAD0001 in the Treatment of Angiomyolipoma in Patients With Either Tuberous Sclerosis Complex (TSC) or Sporadic Lymphangioleiomyomatosis (LAM) |
Completed |
NCT00790400 |
Phase 3 |
Everolimus (RAD001);Everolimus Placebo |
13 |
A Double-blind, Randomized, Placebo-controlled Study to Investigate the Efficacy and Safety of Cannabidiol (GWP42003-P, CBD) as Add-on Therapy in Patients With Tuberous Sclerosis Complex Who Experience Inadequately-controlled Seizures |
Completed |
NCT02544763 |
Phase 3 |
GWP42003-P;Placebo |
14 |
A Double-blind, Randomized, Placebo-controlled Study to Investigate the Efficacy and Safety of Cannabidiol (GWP42003-P, CBD) as Add-on Therapy in Patients With Tuberous Sclerosis Complex Who Experience Inadequately-controlled Seizures |
Completed |
NCT02544750 |
Phase 3 |
GWP42003-P |
15 |
Study of Combination Therapy With Topical Rapamycin and Calcitriol for Cutaneous Lesions of Tuberous Sclerosis: A Double-blind Randomized Controlled Trial |
Completed |
NCT03140449 |
Phase 3 |
Rapamycin;Calcitriol;Rapamycin-calcitriol combination |
16 |
A Three-arm, Randomized, Double-blind, Placebo-controlled Study of the Efficacy and Safety of Two Trough-ranges of Everolimus as Adjunctive Therapy in Patients With Tuberous Sclerosis Complex (TSC) Who Have Refractory Partial-onset Seizures |
Completed |
NCT01713946 |
Phase 3 |
RAD001;Placebo;Antiepileptic drug (1 to 3 only);open label RAD001 (only used for post-extension phase) |
17 |
An Open-label, Randomized Trial to Assess the Safety, Pharmacokinetics, and Exploratory Efficacy of Adjunctive Cannabidiol Oral Solution (GWP42003-P) Compared With Standard of Care Antiseizure Medication, in Patients Age 1 Month to Less Than 12 Months of Age With Tuberous Sclerosis Complex Who Experience Inadequately-controlled Seizures |
Recruiting |
NCT04485104 |
Phase 3 |
GWP42003-P;SOC |
18 |
A Phase 3, Double-blind, Randomized, Placebo-controlled Trial of Adjunctive Ganaxolone (GNX) Treatment in Children and Adults With Tuberous Sclerosis Complex (TSC)-Related Epilepsy |
Recruiting |
NCT05323734 |
Phase 3 |
GNX oral suspension, TID;Placebo |
19 |
Randomized, Placebo-controlled, Double-blind and Double-dummy Clinical Trial Comparing the Safety, Tolerability, and Efficacy of Vigabatrin and Rapamycin in a Preventive Treatment of Infants With Tuberous Sclerosis Complex |
Recruiting |
NCT04987463 |
Phase 2, Phase 3 |
Vigabatrin;Rapamycin;Placebo |
20 |
Placebo-controlled Comparative Study of NPC-12Y Gel in Patients With Skin Lesions Associated With Tuberous Sclerosis Complex |
Recruiting |
NCT05495425 |
Phase 3 |
NPC-12Y gel;NPC-12Y placebo gel |
21 |
An Open-label, Multi-center Long-term Safety Roll-over Study in Patients With Tuberous Sclerosis Complex (TSC) and Refractory Seizures Who Are Judged by the Investigator to Benefit From Continued Treatment With Everolimus After Completion of Study CRAD001M2304. |
Active, not recruiting |
NCT02962414 |
Phase 3 |
everolimus |
22 |
A Phase 3, Open-label Study of Adjunctive Ganaxolone (GNX) Treatment in Children and Adults With Tuberous Sclerosis Complex (TSC)-Related Epilepsy (TrustTSC OLE) |
Enrolling by invitation |
NCT05604170 |
Phase 3 |
GNX oral suspension, TID |
23 |
Multicenter, Randomized, Double-blind, Placebo Controlled Study to Assess the Efficacy and Safety of Rapamycin in Drug Resistant Epilepsy Associated With TSC |
Not yet recruiting |
NCT05534672 |
Phase 3 |
|
24 |
Topical Everolimus Versus Placebo for the Treatment of Facial Angiofibromas in Patients With Tuberous Sclerosis Complex. A Phase II/III, Multicentre, Randomized, Double-blind, Placebo-controlled Study of 3 Doses of Topical Everolimus. |
Withdrawn |
NCT02860494 |
Phase 2, Phase 3 |
Everolimus;Placebo |
25 |
A Trial of the Efficacy and Safety of Sirolimus(Rapamycin)Therapy for Renal Angiomyolipmoas in Patients With Tuberous Sclerosis Complex and Sporadic Lymphangioleiomyomatosis |
Unknown status |
NCT00490789 |
Phase 2 |
sirolimus |
26 |
TRON: A Randomised, Double Blind, Placebo-controlled Study of RAD001 (Everolimus) in the Treatment of Neurocognitive Problems in Tuberous Sclerosis |
Unknown status |
NCT01954693 |
Phase 2 |
Placebo;Everolimus (RAD001) |
27 |
A Placebo-controlled Study of Efficacy & Safety of Aspirin as an add-on Treatment in Patients With Tuberous Sclerosis Complex (TSC) & Refractory Seizures |
Unknown status |
NCT03356769 |
Phase 2 |
Aspirin;AED;Placebo |
28 |
Rapamycin Therapy of Angiomyolipomas in Patients With Tuberous Sclerosis Complex and Sporadic Lymphangioleiomyomatosis |
Completed |
NCT00457808 |
Phase 2 |
Rapamycin, sirolimus |
29 |
RAD001 Therapy of Angiomyolipomata in Patients With Tuberous Sclerosis Complex and Sporadic Lymphangioleiomyomatosis |
Completed |
NCT00457964 |
Phase 1, Phase 2 |
RAD001 |
30 |
Everolimus (RAD001)Therapy of Giant Cell Astrocytomas in Patients With Tuberous Sclerosis Complex |
Completed |
NCT00411619 |
Phase 1, Phase 2 |
Everolimus |
31 |
Treatment of Renal Angiomyolipomas in Tuberous Sclerosis by Beta-blockers: Pilot Trial |
Completed |
NCT02104011 |
Phase 2 |
Propranolol |
32 |
The Safety of Simvastatin (SOS) in Patients With Pulmonary Lymphangioleiomyomatosis (LAM) and With Tuberous Sclerosis Complex (TSC) |
Completed |
NCT02061397 |
Phase 1, Phase 2 |
Simvastatin;Sirolimus Oral Product;Everolimus Oral Product |
33 |
Long Term Follow Up for RAD001 Therapy of Angiomyolipomata in Patients With Tuberous Sclerosis Complex and Sporadic Lymphangioleiomyomatosis |
Completed |
NCT00792766 |
Phase 1, Phase 2 |
everolimus (RAD001) |
34 |
A Phase 2 Open-label 12-Week Trial of Adjunctive Ganaxolone Treatment (Part A) in Tuberous Sclerosis Complex-related Epilepsy Followed by Long-term Treatment (Part B) |
Completed |
NCT04285346 |
Phase 2 |
Ganaxolone |
35 |
Everolimus (RAD001) Therapy for Epilepsy in Patients With Tuberous Sclerosis Complex |
Completed |
NCT01070316 |
Phase 1, Phase 2 |
Everolimus |
36 |
Randomized Double-Blind Phase 2 Trial Of RAD001 For Neurocognition In Individuals With Tuberous Sclerosis Complex |
Completed |
NCT01289912 |
Phase 2 |
RAD001;Placebo |
37 |
Rapalogues for Autism Phenotype in TSC: A Feasibility Study |
Completed |
NCT01929642 |
Phase 2 |
Sirolimus;Everolimus |
38 |
A Pilot Study To Evaluate The Effects of Everolimus on Brain mTOR Activity and Cortical Hyperexcitability in TSC and FCD |
Completed |
NCT02451696 |
Phase 2 |
Everolimus |
39 |
A Phase II Multi-Center Study of Rapamycin for Treating Kidney Angiomyolipomas in TSC or LAM Patients |
Completed |
NCT00126672 |
Phase 2 |
Rapamycin |
40 |
Phase II Study of Topical Rapamycin to Erase Angiofibromas in TSC-Multicenter Evaluation of a Novel Therapy |
Completed |
NCT01526356 |
Phase 2 |
Placebo;Rapamycin |
41 |
A Phase II Trial of Everolimus for Cancer Patients With Inactivating Mutations in TSC1 or TSC2 or Activating MTOR Mutations |
Completed |
NCT02201212 |
Phase 2 |
Everolimus |
42 |
Phase II Study of Everolimus in Patients With Advanced Solid Malignancies With TSC1, TSC2, NF1, NF2, or STK11 Mutations |
Completed |
NCT02352844 |
Phase 2 |
Everolimus |
43 |
A Phase 2B, Multicenter, 30-week, Prospective, Cross-over, Double-blind, Randomized, Placebo-controlled Study Followed by a 52-Week Open-label Extension Study to Evaluate the Efficacy and Safety of Basimglurant Adjunctive to Ongoing Anticonvulsive Therapy in Children, Adolescents, and Young Adults With Uncontrolled Seizures Associated With Tuberous Sclerosis Complex |
Recruiting |
NCT05059327 |
Phase 2 |
Basimglurant with crossover to Placebo;Placebo with crossover to Basimglurant |
44 |
Phase 2 Multi Center Prospective Rand. Double Blind Placebo Cont. Parallel Design Study to Evaluate Safety & Efficacy of Topical Sirolimus for Cutaneous Angiofibromas in Subjects W/ Tuberous Sclerosis Complex Followed by Opt. Open Label |
Recruiting |
NCT03363763 |
Phase 2 |
Sirolimus 0.2%;Sirolimus 0.4%;Placebo ointment |
45 |
Stopping TSC Onset and Progression 2B: Sirolimus TSC Epilepsy Prevention Study |
Recruiting |
NCT05104983 |
Phase 2 |
Sirolimus;Placebo |
46 |
Feasibility Study of [11C]Acetate Positron Emission Tomography (PET) as an Indicator of Early Response to Rapamycin in Lymphangioleiomyomatosis (LAM) Patients |
Recruiting |
NCT05467397 |
Phase 1, Phase 2 |
[11C]acetate |
47 |
A Phase 2 Multi-center Open-label Basket Trial of Nab-sirolimus for Adult and Adolescent Patients With Malignant Solid Tumors Harboring Pathogenic Inactivating Alterations in TSC1 or TSC2 Genes |
Recruiting |
NCT05103358 |
Phase 2 |
nab-sirolimus |
48 |
Preventing Epilepsy Using Vigabatrin In Infants With Tuberous Sclerosis Complex (PREVeNT Trial) A Randomized, Double-blind, Placebo-controlled Seizure Prevention Clinical Trial for Infants With TSC |
Active, not recruiting |
NCT02849457 |
Phase 2 |
Vigabatrin;Placebo |
49 |
Stopping TSC Onset and Progression 2: Epilepsy Prevention in TSC Infants |
Active, not recruiting |
NCT04595513 |
Phase 1, Phase 2 |
TAVT-18 (sirolimus) |
50 |
An Open Label, Multicenter, Single Arm Phase II Study to Evaluate the Activity and Tolerability of the Novel mTOR Inhibitor, MLN0128 (TAK-228), in Patients With Locally Advanced or Metastatic Transitional Cell Carcinoma of the Urothelial Tract Whose Tumors Harbor a TSC1 and/or a TSC2 Mutation |
Active, not recruiting |
NCT03047213 |
Phase 2 |
Sapanisertib |
|